Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.

    ABBV CLS 7262 is Being Evaluated as a Potential Treatment for Vanishing White Matter Disease in the Brain

    The safety, pharmacokinetics (absorption), and tolerability of the investigational eIF2B activator ABBV-CLS-7262 is being evaluated in a Phase 1b clinical study to treat patients with Vanishing White Matter (VWM) Disease.…

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    A Glimmer of Hope for Patients with Advanced Biliary Tract Cancer
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    A Glimmer of Hope for Patients with Advanced Biliary Tract Cancer

        For patients who were given a diagnosis of advanced, inoperable (unresectable) biliary tract cancer, an article appeared in Healio with some encouraging news. Gemcitabine and cisplatin drugs have…

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    New Cell Therapy Approved by the FDA to Reduce Risk of Infection After Transplant
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    New Cell Therapy Approved by the FDA to Reduce Risk of Infection After Transplant

      Omisirge (omidubicel) is the first allogeneic (from a donor) product for SCT that has been the recipient of FDA approval. The FDA's nod moves Omisirge into the realm of…

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    Damage from Cocaine Abuse can be Misdiagnosed as Granulomatosis with Polyangiitis
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    Damage from Cocaine Abuse can be Misdiagnosed as Granulomatosis with Polyangiitis

      The damage caused by cocaine can sometimes be misdiagnosed as a rare disease: granulomatosis with polyangiitis. Cocaine use has been increasing in America and the UK, resulting in serious…

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    Compassion Corner: Compassion Should be Reciprocal: The Rising Suicide Rate of Physicians and Nurses
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    Compassion Corner: Compassion Should be Reciprocal: The Rising Suicide Rate of Physicians and Nurses

    Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is a…

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    Non-Alcoholic Fatty Liver Disease (NAFLD) in Pregnancy has Nearly Tripled in the Past Ten Years
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    Non-Alcoholic Fatty Liver Disease (NAFLD) in Pregnancy has Nearly Tripled in the Past Ten Years

      In the last decade, NAFLD in pregnancy has nearly tripled in concert with the worldwide increase in diabetes. Mayo Clinic reports that NAFLD in general affects one-fourth of the…

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    Advanced Leukemia: Test of Oral Revumenib Brought Impressive Results
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    Advanced Leukemia: Test of Oral Revumenib Brought Impressive Results

      For patients with refractory or relapsed KMT2A rearrangement or NPM1-mutations, the AUGMENT 101 study of the investigational menin inhibitor revumenib yielded impressive results. According to an article in MedicalXpress,…

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    May is Cystic Fibrosis (CF) Month and Some Patients Are Living Past Middle Age Due to Treatment Advances
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    May is Cystic Fibrosis (CF) Month and Some Patients Are Living Past Middle Age Due to Treatment Advances

    There is no cure for cystic fibrosis. That is the reason the Cystic Fibrosis Research Institute (CFRI) is very vocal and makes it clear that cooperation is needed from the…

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    Compassion Corner: An Honest Account by an Orthopedic Surgeon Who Found the Key to Compassion
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    Compassion Corner: An Honest Account by an Orthopedic Surgeon Who Found the Key to Compassion

    Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is a…

    Continue Reading Compassion Corner: An Honest Account by an Orthopedic Surgeon Who Found the Key to Compassion