Hereditary Angioedema Discovery is First Step Toward Gene Therapy
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Hereditary Angioedema Discovery is First Step Toward Gene Therapy

Hereditary Angioedemia (HAE) results when the blood is missing the C1-inhibitor protein. It causes unpredictable and sudden attacks of swelling on various parts of the body. It can affect practically…

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Experimental Treatment Shuts Down Hereditary Angioedema Attacks Quickly in Trials
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Experimental Treatment Shuts Down Hereditary Angioedema Attacks Quickly in Trials

According to a story from Angioedema News, an investigational product from BioCryst Pharmaceuticals called BCX7353 was able to quickly subdue swelling attacks in hereditary angioedema in clinical trials. In addition,…

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New Treatment For Hereditary Angioedema Gets Approved in Canada
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New Treatment For Hereditary Angioedema Gets Approved in Canada

According to a story from pm360online.com, the global biotechnology company Shire plc recently announced its product Takhzyro (injectable lanadelumab) was approved by Health Canada after priority review. Takhzyro is indicated…

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The US FDA Has Approved Takhzyro for the Treatment of Hereditary Angioedema
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The US FDA Has Approved Takhzyro for the Treatment of Hereditary Angioedema

The US Food and Drug Administration has approved a drug called TakhzyroTM (lanadelumab-flyo) for the treatment of hereditary angioedema. This approval was based on supporting evidence from several studies, including from…

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Investigational Gene Therapy for Hereditary Angioedema Gets Orphan Drug Designation
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Investigational Gene Therapy for Hereditary Angioedema Gets Orphan Drug Designation

According to a story from globnewswire.com, the gene therapy company Adverum Biotechnologies recently announced that the US Food and Drug Administration (FDA) has granted them Orphan Drug designation for their…

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Experimental Treatment for Hereditary Angioedema Gets Fast Track Designation
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Experimental Treatment for Hereditary Angioedema Gets Fast Track Designation

According to a story from Benzinga, the pharmaceutical company BioCryst Pharmaceuticals, Inc., recently announced that its investigational product BCX7353 has been granted Fast Track Designation from the FDA for the…

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I’m Always Saying Sorry: Apologizing for My Hereditary Angioedema
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I’m Always Saying Sorry: Apologizing for My Hereditary Angioedema

As I’ve gotten older, I realize I’ve become more introspective, analyzing my relationships, emotions, spiritual well being, and mental health. While talking to others with rare diseases I’ve learned it…

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Scientists Have Identified Genes Involved in Hereditary Angioedema Acute Attacks

Researchers have carried out a study into the genetic mechanisms involved in hereditary angioedema acute attacks. They found that two genes, called uPAR and ADM, had a particularly strong influence.…

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The Rising Price of Prescription Medicine Disproportionately Affects Rare Disease Patients
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The Rising Price of Prescription Medicine Disproportionately Affects Rare Disease Patients

It may not be surprising news to find that the United States now pays more for prescription drugs than any other high-income country. This was not always the case however. Read…

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Study Testing Self-Administration of Hereditary Angioedema Treatment Shows Positive Results
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Study Testing Self-Administration of Hereditary Angioedema Treatment Shows Positive Results

According to a story from Rare Disease Report, a recent study indicates that the self-administration of Berinert, a drug used to treat hereditary angioedema, is effective and safe for patients…

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Living with Hereditary Angiodema: My Life was Changed in an Instant, Part Two
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Living with Hereditary Angiodema: My Life was Changed in an Instant, Part Two

Have you read part one of Loukisha's story? Check it out here! When I imagined life with my husband and children my plans didn’t include surgeries, walkers, canes, a wheelchair,…

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Living with Hereditary Angiodema: My Life was Changed in an Instant, Part One
Source: Loukisha Olive-McCoy

Living with Hereditary Angiodema: My Life was Changed in an Instant, Part One

From birth until my mid-thirties I was a very active person. I loved dancing West Coast Swing, doing yoga, and cooking large meals for my ‘Ohana. The word "'Ohana" describes…

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Treatment for Hereditary Angiodema Gets Marketing Approval From the EMA
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Treatment for Hereditary Angiodema Gets Marketing Approval From the EMA

According to a recent story from pm360online.com, the pharmaceutical company Shire announced that the marketing application for its drug product lanadelumab has gained approval from the European Medicines Agency (EMA).…

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