The Genomics England Research Study listed approximately two hundred rare treatable conditions of children five years old or younger. Genomics has had, and continues to have, an impact on healthcare.…
Editor's Note: The following is an excerpt from Bird’s Eye View: Stories of a Life Lived in Health Care by Sue Robins. I remember every single act of kindness I’ve encountered…
As reported on Pharmaceutical Technology, Alentis Therapeutics has expanded its efforts in claudin-1-targeted cancer therapeutics through a newly announced partnership with PinotBio, aimed at generating antibody-drug conjugates (ADCs) for multiple…
One of the most persistent hurdles in biology is the natural, age-related decline of female fertility. As women age, both the quantity and quality of their eggs (the "ovarian reserve")…
Exercise, yoga, psychological support and other approaches that do not involve medication or surgery may help people with low back pain—and may be cost-effective, according to a review of 20…
Editor's Note: Patient Worthy is honored to bring you this article, shared with us by our friends at Rareatives. Originally written by Davi Jacobs, the article can be found in…
At just two years old, Asher is already teaching us that the smallest milestones can be the biggest victories. Our son, Asher, was born on February 10, 2024. He's a…
IndoUSrare and GORD Foundation are honored to announce the 2026 Abbey Meyers Khushi Bridging RARE Award Honorees: Rare Disease is a global problem, a human problem, and the individuals below…
Editor's Note: The following article was submitted to Patient Worthy by Regina Portnoy. “Nothing hurts. I feel fine. Why would I need to see a doctor?” Throughout my career, I…
Genetic testing is now more available than ever before. For those who suspect a genetic disorder, the best route is often through a genetic counselor. They can advise you not…
Editor's Note: The following story was submitted to us by Pam Mason, Patient Speaker & Advocate. If you looked at a picture of me, you probably wouldn't see someone who…
Editor's Note: Patient Worthy is honored to present this story, shared with us by our friends at the Courageous Parents Network. Originally written by Dr. Adebimpe Adewusi, the article can…
As reported on Becker's Hospital Review, the FDA has approved a first-of-its-kind pulmonary heart valve that can be enlarged after implantation, potentially allowing the device to accommodate a child’s growth…
Patients in the United States wait an average of 34 to 50 days (roughly 1 to 1.5 months) for an initial neurology appointment, with wait times stretching up to 4…
World Lung Day 2026 puts a spotlight on lung health across the life course Lung health begins early in life and needs to remain a priority throughout life, says the…
Twenty-six Novel Therapies have been FDA-approved so far this year. Medical journals, including "The Lancet", see this as a difficult task. The Agency must maintain strict safety rules while simultaneously…
Chronic diseases perplex doctors, while leaving patients mysteriously ill Meghan O’Rourke, the author of the best-selling book Invisible Kingdom, recently released an excerpt from this compelling story to Elle Magazine.…
To start, a few words about the immune system: The immune system is comprised of cells, molecules, and biochemicals, and works to maintain human health. It can be defined as…
Editor's Note: Patient Worthy is honored to share this article, originally written by Linda Chase of Able Hire. Accessible travel planning means building a trip around a traveler’s actual mobility,…
For new caregivers supporting a parent, partner, or relative at home, the days can turn into an unbroken string of decisions, vigilance, and worry. The caregiving challenges often arrive faster…
As reported on Fierce Biotech, the U.S. Food and Drug Administration (FDA) has launched a new pilot program designed to streamline the investigational new drug (IND) application process and reduce…
Editor's Note: Patient Worthy is honored to share this article, originally written by David St. Denis, President & Director at Anteris Technologies. Transcatheter aortic valve replacement (TAVR) was originally developed…
As reported on Science Daily, researchers at the University of Michigan have identified a potential new therapeutic approach for aggressive prostate cancers that become resistant to standard hormone-targeting treatments. Preclinical…
Editor's Note: We're honored to share the following article from our friends at the Courageous Parents Network. To see this article in its original format, please click here. Parents will…
As reported in the European Medical Journal, Novartis has paused eight clinical studies evaluating its experimental CAR-T cell therapy, known as rap-cell, after three trial participants died following severe immune-related…
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