A recently published study examines the response of motor nerve cells to motor neuron disease. Researchers hope that by more completely understanding this cellular response that they may be able…
According to a story from Everyday Health, The U.S. Food and Drug Administration (FDA), has recently approved a new drug for the treatment of recently diagnosed patients with Hodgkin disease.…
According to a story from GlobeNewswire, The pharmaceutical company AveXis, Inc., a company that specializes in the development of gene therapies, recently announced that its candidate AVXS-101 was awarded SAKIGAKE…
According to a story from Innovation Toronto, a recent study has helped develop methods that could be used to create cell-based, personalized immunotherapy treatments that could be used to treat…
According to a story from healio.com, scientists have developed an easy to use testing method for Barrett's esophagus, which can be a precursor to esophageal cancer. The new device combines…
Following Rare Disease Day at the NIH Clinical Center in early March, we spoke to the NIH about remaining questions we had pertaining to rare disease research. We are impressed with…
In the beginning of March, Patient Worthy joined many other groups from the rare disease community for Rare Disease Day at the NIH Clinical Center, an event which you can…
According to a story from news-medical.net, the Genomics England company, which was founded as a subsidiary of the UK's Department of Health and Social Care in 2013, announced recently that…
Sisters Nicole and Jessica Rich, both diagnosed with Batten disease, will finally be able to receive treatment at Great Ormond Street Hospital in London. Nicole, who is six years old,…
According to a story from Financial Content, the drug company Arena Pharmaceuticals recently announced that its data results from Phase II clinical trials has been positive. The trial in question…
March is not just multiple myeloma awareness month... ...it is multiple myeloma ACTION month! Multiple myeloma is a form of cancer that develops in a type of white blood cell…
According to a story from Digital Trends, Google has recently added an option for wheelchair-accessible routes on its widely popular navigation tool, Google Maps. This option will make the app…
Erin Gard and her mother, Joanne Guthrie-Gard, already spent many years of their lives searching for an effective epilepsy medication for Erin. However, once they found it, they lost access…
According to a story from medscape.com, the 2018 budget recently signed by the president is going to feature some spending increases for health-related services. These changes have the potential to…
According to a story from the National Institutes of Health, the innovative new CRISPR gene editing technology is being used in order to identify specific genes that could play a…
According to a story from biospace.com, a research team from the National Cancer Institute was able to successfully deliver an experimental nanomedicine to mice that had rare cancers such as…
According to a story from Medical Xpress, two new treatments were able to slow down the worsening of symptoms associated with muscular dystrophy in a mouse model study. Tamoxifen and…
Vanderbilt University Medical Center researchers have discovered a new method of searching existing electronic medical records to help identify genetic diseases in larger populations, reported EurekAlert!. Many people who may…
Happy first week of spring, everybody! Spring has finally begun, at least in our hemisphere-- we're breaking out shorts, sunscreens, allergy medicines, and some new rare disease updates. This week,…
When Mac Grieb was just a one-year-old he already had two open heart surgeries and doctors said that he would need another in his teenage years, reports The Inquirer. Last…
A popular landscaping bush may be a major culprit in the spread of Lyme disease according to one story. The Japanese barberry plant (Berberis thunbergii) is a small invasive shrub that…
According to a story from webmd.com, diesel exhaust could increase the risk of developing amyotrophic lateral sclerosis, also known as Lou Gehrig disease. People who are exposed to diesel exhaust…
According to a story from People, parents Lester and Noreen Jessop from Utah recently discovered that all three of their children have a rare, life-threatening disease called pantothenate kinase-associated neurodegeneration. Their firstborn…
According to a story from pharmiweb.com, the pharmaceutical company Ovid Therapeutics announced recently that the U.S. Food and Drug Administration (FDA) has given its drug candidate OV101 Fast Track designation…
According to a story from aninews.in, mother Shashi Mishra and her daughter Anamika Mishra have staged a hunger strike in a desperate move to receive treatment for their muscular dystrophy.…
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