A new, joint research pact between Illumina and the National Cancer Center Japan aims to shed light onto the clinical information and genomics of nasopharyngeal carcinoma, a rare cancer. Together,…
In the United States, Orphan Drug designation is granted to drugs or biologics intended to treat, prevent, or diagnose rare diseases or conditions. A “rare” condition is one affecting under…
Nicole Burns’ great grandfather left her his house and a portion of his 100 acres. According to a recent article in STAT News, Nicole also inherited her great grandfather’s heart…
Historically, both osteosarcoma and neuroblastoma have been difficult to treat. Therefore, new treatment options are needed for these cancers, which predominantly affect children and teenagers. According to Medical XPress, a…
The question plaguing the geneticists about the Burns family was: how have they survived? In 2016, several geneticists theorized that certain people may have a good-gene bad-gene scenario taking place…
Dr. Rachel Grisham MSK ovarian cancer section head discussed clinical trials investigating PARP inhibitors for ovarian cancer patients. The event was a round table discussion and interview for Targeted Oncology.…
Over the last few years, many researchers have been utilizing organoids as a pathway to learn more about diseases and spur drug development. Organoids may be helpful, moving forward, in…
In the past, many researchers have hypothesized a link between multiple sclerosis (MS) and different viruses or viral infections. While these hypotheses are varied in nature, there has rarely been…
Tay-Sachs disease has escaped effective treatment since 1883 when an ophthalmologist names Warren Tay found small red spots in the back of the eyes of some infants. According to an…
Research is constantly being done on possible treatment strategies for different forms of cancer; there are many patient populations that face an unmet need. Currently, a team of researchers from…
On February 15, 2022, biotechnology company Zealand Pharma A/S (“Zealand”) announced that its Phase 3 1703 clinical trial evaluating dasiglucagon for congenital hyperinsulinism (CHI) had reached full enrollment. Within this…
Researchers are consistently looking for ways to deepen their understanding of various conditions, which not only helps with drug development but with patient outcomes. According to Medical XPress, a research…
Prozac (fluoxetine) is used to treat a variety of mental health conditions including major depressive disorder (MDD), obsessive-compulsive disorder (OCD), bulimia, and premenstrual dysphoric disorder (PMDD), among others. You may…
Unfortunately, a pancreatic cancer diagnosis also comes with a poor prognosis. Since many people do not receive a diagnosis until later stages of the cancer, the 5-year survival rate is…
What prognostic tools can be used to assess patients with idiopathic pulmonary fibrosis (IPF)? How can researchers use these tools to determine the efficacy of therapies during clinical trials, or…
CFTR gene mutations cause cystic fibrosis, a rare genetic condition which causes progressive digestive and respiratory system damage. Yet it can be extremely difficult to treat for those with “stop”…
An estimated 1 in every 200,000 Americans has lymphangioleiomyomatosis (LAM), a rare lung disease that disproportionately affects females. To this day, researchers are still learning new information about this condition.…
The Ebola virus is endemic in certain areas of Africa, where viral outbreaks still exist to this day. For example, there were at least three Ebola outbreaks in Africa during…
LOXO-305 is an investigational Bruton’s tyrosine kinase (BTK) inhibitor which is currently in development for the treatment of mantle cell lymphoma (MCL). The next step is to evaluate LOXO-305 in…
Have you ever heard of comorbidities? In short, comorbidities mean the presence of more than one disease or condition in someone at a time. For example, arthritis and heart disease…
Digital health company AEYE Health was founded on the desire to provide fully automated, artificial intelligence (AI) based diagnostic screening tools for retinal imaging. According to the Ophthalmology Times, the…
Renal cell carcinoma (RCC) is a highly metastatic (easily spreading) cancer. If RCC progresses, it can spread to other organs, such as the lungs. Although RCC is a rare cancer,…
According to an article recently published in Clinical Trials Arena, the Swedish pharmaceutical company Oncorena has recently initiated a Phase I/II trial for orellanine. This investigational treatment is intended for…
According to a recent article, a research team discovered that the inhibition of sphingolipid synthesis on mice models of Duchenne muscular dystrophy can counteract the certain symptoms of the disease.…
According to a recent article, a study shows that patients with epithelial ovarian cancer do present with at least one symptom the majority (72%) of the time. Ovarian Cancer Ovarian…
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