medical research – Page 3

Pre-Clinical Safety Data Available on DA-1241 Combination for Metabolic Dysfunction-Associated Steatohepatitis (MASH)

Post author:Jessica Lynn
Post published:February 9, 2024
Post category:Metabolic dysfunction-associated steatohepatitis Nonalcoholic fatty liver disease Nonalcoholic steatohepatitis

Metabolic dysfunction-associated steatohepatitis (MASH) unfortunately has no treatments to reverse the disease or its damage. MASH can be managed through weight loss, regular exercise, and blood sugar management. But identifying…

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Dupixent Label Update Reflects Safety and Efficacy Results for Moderate-to-Severe Atopic Dermatitis with Severe Hand/Foot Involvement

Post author:Jessica Lynn
Post published:February 7, 2024
Post category:Atopic dermatitis

According to reporting from Healio Psoriatic Disease, the Food and Drug Administration (FDA) recently updated the label for Dupixent (dupilumab) in the indication of moderate-to-severe atopic dermatitis with moderate-to-severe hand…

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Study Suggests that Perinatal Depression Risk is Significantly Higher in Women with Autoimmune Diseases

Post author:Jessica Lynn
Post published:January 31, 2024
Post category:Rare Disease

Type 1 diabetes (T1D), rheumatoid arthritis, lupus, and ulcerative colitis are all examples of autoimmune diseases. An autoimmune disease is a condition that occurs when the immune system mistakenly attacks…

Photo by Sangharsh Lohakare on Unsplash

Naturally Occurring SHLP2 Variant Protects Against Parkinson’s Disease

Post author:Jessica Lynn
Post published:January 29, 2024
Post category:Parkinson's Disease

Genes serve as the intricate orchestrators of our health. By better understanding our genetic makeup, we gain invaluable insights into how our genes shape and affect us. Yet the genetic…

Source: Pixabay.com

Could Low Serotonin Cause MCI and Alzheimer’s Disease?

Post author:Jessica Lynn
Post published:January 25, 2024
Post category:Alzheimer's disease

Editor's Note: Chronic conditions and rare diseases don't discriminate, Patient Worthy and its partners are interested in amplifying the voices of those from all identities and backgrounds. If you have…

source: pixabay.com

FLORetina-ICOOR Meeting: Do GLP-1 Agonists Increase Risk of Diabetic Retinopathy?

Post author:Jessica Lynn
Post published:January 25, 2024
Post category:Diabetic retinopathy

Editor's Note: Chronic conditions and rare diseases don't discriminate, Patient Worthy and its partners are interested in amplifying the voices of those from all identities and backgrounds. If you have…

source: shutterstock.com

UMass Chan Progressing on Gene Therapy Vector for Cockayne Syndrome

Post author:Jessica Lynn
Post published:January 24, 2024
Post category:Cockayne syndrome

Genes hold the key to our health. Through revolutionary gene therapy solutions, the medical field is transforming to laud the power and precision of personalized medicine. Gene therapy has the…

Source: pixabay.com

Could Omega-3 Fatty Acids Slow Pulmonary Fibrosis Progression?

Post author:Jessica Lynn
Post published:January 22, 2024
Post category:Pulmonary fibrosis

Omega-3 fatty acids like alpha-linlenic acid or docosahexaenoic acid are "healthy fats" that are found in foods like flaxseed, fish, soybeans, and canola oil; they may also be given via…

sasint / Pixabay

Hemithyroidectomy vs. Total Thyroidectomy for Thyroid Cancer: Which Choice for Better Quality-of-Life?

Post author:Jessica Lynn
Post published:January 16, 2024
Post category:Thyroid Cancer

Both a hemithyroidectomy and total thyroidectomy are surgical interventions for people with low-risk differentiated thyroid cancer. Prior studies suggest that survival rates following these surgeries are relatively equal for these…

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Is Idiopathic Hypersomnia More Prevalent Than We Believed?

Post author:Jessica Lynn
Post published:January 11, 2024
Post category:Idiopathic Hypersomnia

In 2021, approximately 37 people per every 100,000 were diagnosed with idiopathic hypersomnia (IH), a neurological disorder characterized by excessive sleepiness and excessive daytime sleepiness. This amounts to roughly…

https://pixabay.com/en/epilepsy-seizure-stroke-headache-623346/

Researchers Identify Potential CDKL5 Treatment Target

Post author:Jessica Lynn
Post published:January 11, 2024
Post category:CDKL5

As it stands today, there are no cures for CDKL5 deficiency disorder. Treatment is symptomatic and supportive, and includes physical, occupational, and speech therapy. CDKL5 deficiency disorder causes seizures,…

Oral Arsenic Trioxide Regimen Effective for Treating APL, Study Results Suggests

Post author:Jessica Lynn
Post published:January 9, 2024
Post category:Acute Myeloid Leukemia Acute promyelocytic leukemia

The 66th American Society for Hematology (ASH) Annual Meeting and Exhibition took place from December 7-10, 2023. During the meeting, researchers and other stakeholders shared insights into clinical trends,…

PDPics / Pixabay

ICYMI: LP-284 Earns Orphan Drug Designation for High-Grade B-Cell Lymphoma with MYC/BCL2 Rearrangements

Post author:Jessica Lynn
Post published:January 4, 2024
Post category:Non-Hodgkin lymphoma Non-Hodgkin's Lymphoma

Have you ever heard of Orphan Drug designation? This designation, granted by the U.S. Food and Drug Administration (FDA), is given to drugs or biologics that are designed to treat,…

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Evobrutinib Fails in Phase 3 Trial for Multiple Sclerosis (MS)

Post author:Jessica Lynn
Post published:January 3, 2024
Post category:Multiple Sclerosis

Clinical trials are helpful tools in deepening our understanding of certain diseases and evaluating and identifying effective treatment options. Unfortunately, these trials don't always garner the necessary information. For…

[Source: Pixabay.com]

FABHALTA Now FDA-Approved for PNH

Post author:Jessica Lynn
Post published:December 25, 2023
Post category:paroxysmal nocturnal hemoglobinuria

Paroxysmal nocturnal hemoglobinuria (PNH) is a rare acquired hematopoietic stem cell disorder in which blood cells break apart prematurely. In an effort to bring more effective and targeted treatments…

PublicDomainPictures / Pixabay

Using Fruit Flies, Researchers Find Potential Genetic Link to Alzheimer’s

Post author:Jessica Lynn
Post published:December 19, 2023
Post category:Alzheimer's disease

Editor's Note: We believe that patients are a key part of developing and leading the conversation in disease communities. Patient Worthy sometimes partners with reputable agencies that wish to speak…

source: shutterstock.com

TRIAL RESULTS: How Did Mirdametinib Perform for NF1-PN?

Post author:Jessica Lynn
Post published:December 18, 2023
Post category:Neurofibroma Neurofibromatosis Neurofibromatosis Type 1

Over their lifetime, people with neurofibromatosis type 1 (NF1), a rare genetic disorder, have a 30-50% chance of developing plexiform neurofibromas. These tumors grow on peripheral nerve sheaths throughout…

slon_dot_pics / Pixabay

Phase 3 Program on Cobitolimod for UC Discontinued After Inability to Meet Primary Endpoint

Post author:Jessica Lynn
Post published:December 18, 2023
Post category:ulcerative Colitis

The risk of developing an inflammatory bowel disease (IBD) such as Crohn's disease or ulcerative colitis (UC) has been slowly but steadily increasing over time, with an estimated 0.8%…

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ICYMI: Positive Topline Data Available on Vimseltinib for TGCT

Post author:Jessica Lynn
Post published:December 14, 2023
Post category:Tenosynovial giant cell tumors

Surgical resection remains the most common treatment approach for people living with tenosynovial giant cell tumors (TGCT). Unfortunately, surgery is not always an appropriate treatment option for all people.…

source: shutterstock.com

Dosing Begins in WVE-006 Study for AATD

Post author:Jessica Lynn
Post published:December 12, 2023
Post category:Alpha-1 Antitrypsin Deficiency Alpha-1 antitrypsin deficiency

Clinical studies are critical tools in identifying and developing therapeutics for a wide variety of conditions. This research is especially important in the rare disease and chronic illness spaces,…

https://pixabay.com/en/mom-daughter-son-relationship-2208928/

Research Suggests That Maternal and Infant Antibiotic Exposure Heightens EoE Risk

Post author:Jessica Lynn
Post published:December 11, 2023
Post category:Eosinophilic Esophagitis

Over the last three decades, researchers and doctors have noticed a concerning trend: increasing cases of eosinophilic esophagitis (EoE), a chronic digestive system disorder, in infants and children. In particular,…

Photo by Wengang Zhai on Unsplash

Experimental Study Highlights Potential Benefit of Zinc for Treating Vulvovaginal Candidiasis

Post author:Jessica Lynn
Post published:December 8, 2023
Post category:Vulvovaginal candidiasis

An estimated 75% of women will develop vulvovaginal candidiasis (a vaginal yeast infection) during their lifetime, with a significant number (approximately 140 million women worldwide) experiencing recurrent yeast infections.…

Source: Pixabay

Updated Phase 1/2 Data Highlights Vepdegestrant Benefits for ER+ HER2- Breast Cancer

Post author:Jessica Lynn
Post published:December 8, 2023
Post category:Breast Cancer

A Phase 1/2 clinical trial sought to evaluate the potential of vepdegestrant as a therapeutic option for heavily pretreated individuals with estrogen receptor-positive (ER+) and HER2 negative (HER2-) advanced…

Source: https://pixabay.com/en/hand-hold-care-help-elderly-old-1549132/

The Impact and Challenges of Caring for People with Tardive Dyskinesia

Post author:Jessica Lynn
Post published:December 6, 2023
Post category:Tardive Dyskinesia

When it comes to caregiving for a family member, loved one, or other individual living with any type of health issue, there is an enormous financial, emotional, and mental burden…

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14-Year-Old Rising College Senior Dives into Ovarian Cancer Research

Post author:Jessica Lynn
Post published:December 4, 2023
Post category:Ovarian Cancer

Editor's Note: We believe that patients are a key part of developing and leading the conversation in disease communities. Patient Worthy sometimes partners with reputable agencies that wish to speak…

Pre-Clinical Safety Data Available on DA-1241 Combination for Metabolic Dysfunction-Associated Steatohepatitis (MASH)

Dupixent Label Update Reflects Safety and Efficacy Results for Moderate-to-Severe Atopic Dermatitis with Severe Hand/Foot Involvement

Study Suggests that Perinatal Depression Risk is Significantly Higher in Women with Autoimmune Diseases

Naturally Occurring SHLP2 Variant Protects Against Parkinson’s Disease

Could Low Serotonin Cause MCI and Alzheimer’s Disease?

FLORetina-ICOOR Meeting: Do GLP-1 Agonists Increase Risk of Diabetic Retinopathy?

UMass Chan Progressing on Gene Therapy Vector for Cockayne Syndrome

Could Omega-3 Fatty Acids Slow Pulmonary Fibrosis Progression?

Hemithyroidectomy vs. Total Thyroidectomy for Thyroid Cancer: Which Choice for Better Quality-of-Life?

Is Idiopathic Hypersomnia More Prevalent Than We Believed?

Researchers Identify Potential CDKL5 Treatment Target

Oral Arsenic Trioxide Regimen Effective for Treating APL, Study Results Suggests

ICYMI: LP-284 Earns Orphan Drug Designation for High-Grade B-Cell Lymphoma with MYC/BCL2 Rearrangements

Evobrutinib Fails in Phase 3 Trial for Multiple Sclerosis (MS)

FABHALTA Now FDA-Approved for PNH

Using Fruit Flies, Researchers Find Potential Genetic Link to Alzheimer’s

TRIAL RESULTS: How Did Mirdametinib Perform for NF1-PN?

Phase 3 Program on Cobitolimod for UC Discontinued After Inability to Meet Primary Endpoint

ICYMI: Positive Topline Data Available on Vimseltinib for TGCT

Dosing Begins in WVE-006 Study for AATD

Research Suggests That Maternal and Infant Antibiotic Exposure Heightens EoE Risk

Experimental Study Highlights Potential Benefit of Zinc for Treating Vulvovaginal Candidiasis

Updated Phase 1/2 Data Highlights Vepdegestrant Benefits for ER+ HER2- Breast Cancer

The Impact and Challenges of Caring for People with Tardive Dyskinesia

14-Year-Old Rising College Senior Dives into Ovarian Cancer Research

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