According to a story from the Tenterfield Star, a fundraiser was recently held for Tommy Johnston, a one year old boy who was diagnosed with the rare Niemann-Pick disease type…
Niemann-Pick Disease is a genetic lysosomal storage disease. Lipids accumulate in the lysosomes of cells, causing debilitating symptoms. There are three forms of the disease- A, B, and C. Each…
There is a great unmet medical need for patients living with metabolic disorders. There are few approved treatments for these conditions and many are fatal. These diseases include phenylketonuria, homocystinuria, tyrosinemia, and maple syrup…
A recent survey conducted by researchers at the NYU School of Medicine has indicated that oncologists know much less about the unique cancer needs of the LGBTQ population than they thought.…
Mesothelioma is a cancer which occurs in the thin layers of tissue (mesothelium) which surround most of the body's internal organs. It's often caused by asbestos exposure. However, symptoms can take…
Sickle cell disease (SCD) is a rare blood condition. It causes sickling in the red blood cells which results in the blockage of blood vessels and capillaries. The sickling process…
Ionis Pharmaceuticals and Roche have been collaborating on a drug for Huntington's Disease which will treat the root cause of the condition. Currently, there are no such approved treatments, meaning…
While juvenile idiopathic arthritis remains to be the most common rheumatic disease in children, researchers have long been stumped at its caused. The best prediction was that it originated as…
Non-tuberculous mycobacterial (NTM) infections are caused by bacteria found in the environment. In healthy individuals, these bacteria normally cause no harm. However, for those who have a compromised immune system or who…
Happy Wednesday! While it's felt like January was going to last forever, we're almost through the first month of 2019. As we gear up for February, we want to reflect…
According to a story from sectorpublishingintelligence.co.uk, the biopharmaceutical company Processa Pharmaceuticals, Inc. recently announced that the first patient had been dosed in the company's Phase 2 clinical trial. This trial…
According to a story from globenewswire.com, the biopharmaceutical company Xenon Pharmaceuticals, Inc., recently announced the latest updates on the progress of two of its experimental products. The first is called…
According to a story from pm360online.com, the drug developer Innate Pharma SA recently announced that its experimental therapy IPH4102 has been granted Fast Track designation from the US Food and…
Notable Labs Notable Labs was created after founder, Matt De Silva, felt he was left in a helpless point, following a year of research on treatment options for his father's Glioblastoma…
Systemic Sclerosis (SSc) is a rare disease that causes the skin to thicken and form into scar tissue. It can affect various parts of the body including the gastrointestinal track,…
According to a story from the Irish Mirror, 32-year-old Ben McGuire recently sued the HSE after claiming that the Cork University Hospital was unable to detect a pancreatic cancer tumor…
According to a story from statnews.com, the biotechnology company Alexion Pharmaceuticals recently announced that its product Ultomiris, which was recently approved as a treatment for paroxysmal nocturnal hemoglobinuria, was also…
Epidermolysis Bullosa Epidermolysis Bullosa (EB) refers to a group of rare conditions which are characterized by fragile skin. Basically, the disease is caused by separation between the layers of the skin.…
The History of West Nile Virus The West Nile Virus (WNV) was named for the location where it was originally found- the West Nile district in Uganda. It was discovered…
The most common treatment for someone who is discovered to have early stage kidney cancer is surgery. The patient's tumors and a part of their kidneys are removed through a…
Sarcoidosis is a rare condition which causes inflammatory cells to build up in various organs throughout the body. For 90% of people with a sarcoidosis diagnoses, the lungs are one…
The State of Cancer in the United States A recent report posted by the American Cancer Society has indicated that cancer rates in the United States have been continuously falling over…
According to a story from Physician's Weekly, the pharmaceutical company AbbVie, Inc. recently announced that its cancer drug Imbruvica failed to measure up in a recent clinical trial in which…
Autoimmune hepatitis (AIH) is a rare condition which causes inflammation in the liver. It can lead to cirrhosis and ultimately, liver failure. The typical treatment for patients with the disease includes…
According to a story from Science Daily, a team of scientists from the Translational Genomics Research Institute (TGen) have identified the likely cause of a recent outbreak of an unusual…
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