The United States Food and Drug Administration has granted the drug Lynparza® (olaparib) Orphan Drug Designation for the treatment of pancreatic cancer. Lynparza is used in the US to treat…
The United States Food and Drug Administration has granted Fast Track designation to a drug being researched as a potential treatment for progressive familial intrahepatic cholestasis, a serious liver disease…
Across the globe, countries are transitioning their healthcare systems to provide more care within the patient's home and less in a hospital setting. Why? Simply put, it's because there's beginning…
The United States Food and Drug Administration has awarded Rare Pediatric Disease Designation to a potential drug for Mucopolysaccharidosis type I. For more detailed information about this news, you can…
Multiple sclerosis is a disease that can effect every aspect of daily life. However, symptoms vary on a day to day basis and the lack of predictability makes the disease…
According to a story from finanznachrichten.de, the Korean biopharmaceutical company Biocure Technology, Inc., recently announced the results of a pre-clinical trial that tested CAR-T cell therapy as a treatment for acute…
According to a story from Healio, recent testing has found that FibroScan, a form of medical imaging, is capable of detecting nonalcoholic steatohepatitis earlier than it would be possible to…
According to a story from Market Screener, the pharmaceutical company Retrotope has recently released data that indicates that the company's experimental product RT001 is capable of halting disease progression for…
According to a story from EurekAlert!, a recent study from the University of Zurich has illuminated the connection between the gastrointestinal flora and multiple sclerosis. The discovery illuminates the potential…
The United States Food and Drug Administration has awarded Orphan Drug Designation to an investigational drug for narcolepsy, and there are plans to carry out a Phase 2 study to…
Encouraging topline results from a pivotal Phase 3 study into a drug for Charcot-Marie-Tooth type 1A disease have been shared by Pharnext. To find out about this news in more…
According to recent research, a bacteria that causes some forms of stomach cancer may also be responsible for increased risk of colon cancer. The research points to this being especially…
Of pediatric cancers, brain cancer has the highest rate of mortality and medulloblastoma is the most common of brain cancer diagnoses in children. It's a brain cancer that originates in…
Increasingly, researchers are looking into how the human microbiome – the trillions of microbes that live on and in your body – can influence various aspects of health, from nutrition…
According to a story from baledezi.wordpress.com, a recent study demonstrated that a chemotherapy agent that originates from a sea sponge was able to prolong the lives of women with metastatic…
According to a story from pm360online.com, the orphan lung disease company Savara recently announced that they had completed their enrollment target of 135 patients for a Phase 3 clinical trial…
According to a story from Roche, the pharmaceutical company recently released new data from its ongoing clinical trial, which is testing the company's investigational product risdiplam. In this study, the…
Gene editing has come a long way as a treatment option in the last several years. Rapid advances in technology continue to find more and more novel therapies. According to…
The Parkinson’s Institute and Clinical Center and Retrotope are teaming up to study a potential new therapy for patients with progressive supranuclear palsy. For more information about this collaboration, you…
What is PML? PML stands for progressive multifocal leukoencephalopathy. It’s a brain infection caused by the JC virus. The JC virus itself isn’t all that rare. In fact, its pretty…
According to a story from Bioportfolio, the biopharmaceutical company Newron Pharmaceuticals has chosen to support Rett Syndrome Awareness Month this year. Rett Syndrome Awareness Months falls on the October of…
Zealand Pharma A/S (Zealand) recently announced in a press release the start phase 3 trial for short bowel syndrome treatment. The trial investigates the use of glepaglutide as a treatment…
According to a story from OncLive, the drug development company Karyopharm Therapeutics recently announced that the US Food and Drug Administration has granted Priority Review to the company's XPO1 inhibitor…
As part of their work to support the treatment of patients with multiple sclerosis, Biogen has been investigating a potential new biomarker for the disease called serum neurofilament light (sNfL),…
The United States Food and Drug Administration has accepted an Investigational New Drug application (IND) for an investigational gene therapy designed to be a treatment for sickle cell disease. Previously,…
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