A new study has found that a certain type of bacteria may play a significant role in the development of stomach cancer. For more information, you can view the source…
A research team led by scientists from Newcastle University believe that they may have identified a previously unknown genetic cause of childhood mitochondrial disease. For more information about this, you…
According to a story from Clinical Advisor, a recent study has found a link between McCune-Albright syndrome and gastrointestinal disease. In fact, the authors of the study recommend that patients…
According to a story from the Houston Chronicle, researchers are hoping that an immunotherapy treatment that was originally funded by an Ice Bucket Challenge grant could be a viable option…
According to a UVAToday report, researchers at UVA uncovered a new piece of the multiple sclerosis puzzle. The secret lies with what are known as lymphatic vessels. Lymphatic vessels normally…
Amicus Therapeutics has met with the United States Food and Drug Administration to discuss the investigational drug AT-GAA, which is being researched as a potential treatment for Pompe disease.…
The United States Food and Drug Administration has awarded Fast Track Designation to an experimental gene therapy for the treatment of wet age-related macular degeneration. For more detailed information, you…
An international study led by researchers at the University of Alabama Birmingham has investigated the link between a specific genetic mutation underlying neurofibromatosis type 1, and the symptoms patients with…
According to a story from Science Trends, a recent trial of an experimental treatment demonstrates that it could be a potential treatment for Pompe disease. There are very limited treatment…
According to a report by sciencealert.com, a novel form of antidepressant recently entered review by the FDA. While the new treatment is currently being examined for its effects on postpartum…
Corbus Pharmaceuticals have announced that they will go ahead with a Phase 3 study investigating the drug lenabasum as a potential treatment for dermatomyositis. For more information, you can view…
A recently published study has highlighted the role of a sub-group of astrocytes (a type of brain cell) in brain inflammation, which can be a feature of multiple serious diseases,…
According to a story from The New York Times, it didn't take long after Bertrand Might was born for his parents to realize that something was off. He had developmental…
With technologies like CRISPR, it is possible to imagine a world where genetic diseases fade into obscurity. Gene editing technologies may not have reached their potential yet, but many people…
According to a story from blogs.bmj.com, the situation has been tense recently in the halls of the Cochrane Collaboration. Cochrane is a non-profit organization that involves the work of over…
According to a story from Eye on the Cure, the biopharmaceutical company Ophthotech is hard at work researching and developing gene therapy solutions for a variety of rare retinal conditions.…
According to a story from Healio, a recent study found that irbesartan, marketed under the name Avapro, can help reduce the rate at which the aorta, the largest blood vessel…
The United States Food and Drug Administration has awarded Rare Paediatric Disease Designation to an experimental drug for the treatment of Stargardt disease. For more information, you can find the…
Bone Therapeutics, who are developing an allogeneic bone cell therapy as a treatment for delayed-union fractures of long bones, has announced the results of a Phase 1/11A study. They have…
According to a story from Hematology Times, a recent study found that genetic sequencing after the completion of a hematopoietic stem cell transplant could provide doctors with vital information about…
According to a story from Medical Xpress, three medical students at Florida International University are hoping to see if DNA collected from tampons could help detect ovarian cancer. There is…
Novartis has carried out a survey to find out what elements of a treatment are most important to patients with psoriasis. The survey found that patients value clear skin the…
According to a report by CheckOrphan, a recent study investigated the use of genome editing directly in the body. The research involved the use of these editing techniques in cases…
The United States FDA has awarded Breakthrough Therapy Designation to a drug called LOXO-292 for the treatment of RET-altered non-small cell lung cancer and thyroid cancer, in patients who meet…
The United States Food and Drug Administration has granted Breakthrough Device Designation to a medical device that is designed to screen for hyperkalaemia (high blood potassium levels) without taking a…
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