Promising data from the ongoing Phase I clinical trial Explorer has been announced by Blueprint Medicines Corporation. The trial is designed to evaluate the effects of the experimental drug avapritinib…
According to a story from businesswire.com, the company Prana Biotechnology Ltd recently announced that it is beginning the recruitment process for its Phase 1 clinical trial of its investigational product…
The U.S. Food and Drug Administration has granted the experimental drug A4250 rare paediatric disease designation for the treatment of progressive familial intrahepatic cholestasis. The full article can be found…
According to a story from pm360online.com, the speciality pharmaceutical company Chiesi USA and the biotech company Holostem Terapie Avanzate S.r.l. of Italy recently announced that the U.S. FDA recently granted orphan…
Newron Pharmaceuticals S.p.A (Newron) is a biopharmaceutical company specializing in developing inventive therapeutic options. They focus primarily on conditions related to the nervous system. According to bioportfolio.com, Newron announced on…
According to BioPortfolio, there was recently an announcement about preclinical data for SYNB1618, which is a Synthetic Biotic treatment that is being assessed right now in a Phase 1/2a clinical trial in…
According to EurekAlert!, a study at Virginia Commonwealth University has potentially pinpointed the so called "Achilles heal" of a certain type of deadly brain cancer: glioblastoma multiforme. Glioblastoma, or glioblastoma…
According to a story from med.miami.edu, a team of researchers working at the Sylvester Comprehensive Cancer Center, which is part of the University of Miami School of Medicine, made a…
According to WBUR, treatments like CAR-T and CRISPR are on the cutting edge. They’re important to keep an eye on as the future of medical technology and treatment. They’re not…
Medical Research Network (MRN) is an organisation that specialises in the conduct of clinical trial visits in the patient’s home and supporting clinical trial sites with nursing resources. MRN aims…
There are many mysteries still contained in human biology. Circadian clocks and DNA repair seem to share an interaction that may be one of them. Furthermore, based on research from…
According to Medical Xpress, scientists have pinpointed how a potentially new treatment effectively targets spinal muscular atrophy (SMA). The results from the research could lead to further development in SMA…
According to Wilts and Gloucestershire Standard, aspirin is potentially the difference maker in preventing esophageal cancer, especially among those at high risk for the cancer. Esophageal cancer originates in the…
According to a story from the National Institutes of Health, a recent study has revealed that the absence of a specific protein in the cells lining the esophagus could be…
According to a story from PLOS Medicine, most people will probably tell you that the anti-vaccine movement in the United States is a total failure. While the vast majority of…
The biotechnology company Bloom Science has found that the ketogenic diet can be an effective treatment for epilepsy due to its effects on gut bacteria. Bloom Science is planning on…
Researchers from the UK have developed a new test for oesophageal cancer. The full article can be found here, at ABC News. Oesophageal cancer is a form of cancer estimated…
Dicerna Pharmaceuticals has dosed the first patient with primary hyperoxaluria in Group B of a clinical trial of the investigational drug DCR-PHXC. Dicerna has also announced that DCR-PHXC has just…
According to The Washington Post, recent results from a study show great news for women diagnosed with early-stage breast cancer. The news is that the majority of these women will…
Researchers have found that inhibiting an enzyme called heparanase can significantly reduce the growth of mesothelioma in mouse models. The full article can be found here, at the American Technion…
A recently published study has found that a protein the in blood, called CC16, can predict lung disease progression in patients with systemic sclerosis. High levels of the protein are…
Efficiency is one of the great success of modern computers. When it comes to sifting through large quantities of data or recognizing patterns, for instance, computers are several magnitudes better…
A new clinical trial aims to be the first treatment for mitochondrial disease to be granted FDA approval. Whether or not the trial results in a landmark treatment, it is…
In a study conducted by Ph.D Ludwine Messiaen, the professor of genetics at the University of Alabama at Birmingham, says that there has been progress made to help aid those…
According to a story from abc.net.au, ever since Massimo Damiani was first diagnosed with a leukodystrophy, his parents, Sally and Stephen, have been committed to promoting research efforts and new…
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