According to a story from abc.net.au, ever since Massimo Damiani was first diagnosed with a leukodystrophy, his parents, Sally and Stephen, have been committed to promoting research efforts and new…
According to a story from pm360online.com, the clinical stage corporation Epizyme recently released detailed results from the Phase 2 trial of its leading investigational candidate, tazemetostat. This drug is in…
The Investigational New Drug Application for the experimental drug CTX001 for treating sickle cell disease has been put on clinical hold, announced Vertex Pharmaceuticals Incorporated and CRISPR Therapeutics. This hold…
A study has discovered a mechanism involved in amyotrophic lateral sclerosis (ALS). The researchers hope that this new information could contribute to finding a treatment for the condition. The full…
According to a story from empr.com, a recent study revealed that gene therapy could allow patients with beta thalessemia to stop having to get regular blood transfusions. The gene therapy…
According to a story from Reuters, the cancer drug developer Loxo Oncology recently released the latest results from the trial testing its investigational therapy LOXO-292. Preliminary results released about a…
A recent study by researchers in the US has linked Lynch syndrome to several more forms of cancer. Previously, Lynch syndrome has mainly been associated with colorectal and endometrial cancers,…
The results of a Phase 1 clinical trial of the experimental drug ivosidenib, led by researchers at The University of Texas MD Anderson Cancer Center, have been published in the…
Researchers from the University Hospital Bonn in Berlin, Germany have successfully used artificial intelligence image scanning to diagnose patients with Glycolipid (GPI) anchor deficiencies, reports Healthcare Analytics News. They recently published…
Cancer treatment is most successful when the cancer can be detected early. The earlier the better. According to Newsweek, a new screening test may be able to detect cancer faster…
Early trial results in the United Kingdom point to a new vaccine which may extend the lives of cancer patients. The vaccine, designed to help treat glioblastoma, is being described…
A primary immunodeficiency report, published in the journal Clinical and Experimental Immunology, examines medical care for primary immunodeficiency patients in the UK. The publication of the report coincides with the…
The biopharmaceutical company Complexa, Inc., has announced that the first patient has been dosed on the Phase 2 clinical trial FIRSTx. FIRSTx is a study of the experimental drug CXA-10…
According to a story from Renal & Urology News, a recent study investigated the origins of hyperkalemia caused by certain treatments, specifically the class of drugs known as renin-angiotensin-aldosterone system inhibitors…
According to a story from cancer.nautil.us, some cancer researchers are beginning to look at the animal kingdom in order to find new answers for finding what it takes to beat…
According to Timesunion, 10 patients in New York were diagnosed with the extremely rare eye cancer called vitreoretinal lymphoma. Since all of these diagnoses happened within four years of patients…
Researchers at the Massachusetts General Hospital Research Institute and the Georgia Institute of Technology are investigating a medication currently approved to treat a type of multiple sclerosis as a possible…
According to a story from Reuters, the Danish biotech company Genmab saw its share value drop by a quarter after Johnson & Johnson, which had partnered with the company to…
Myalgic encephalomyelitis/ chronic fatigue syndrome (ME/CFS) has been a controversial condition ever since it was first diagnosed and recognized. Some uninformed doctors still believe that the syndrome is a psychological…
A new study conducted by Centers for Disease Control and Prevention found that premature babies were more susceptible to having obstructive sleep apnea (OSA), reported RadioAllen. About 1 in 10 newborns…
Researchers have carried out a study into the genetic mechanisms involved in hereditary angioedema acute attacks. They found that two genes, called uPAR and ADM, had a particularly strong influence.…
Studies show that if your father's mother, your paternal grandmother, was diagnosed with ovarian cancer, you are at a higher risk for the disease than if your grandmother on your…
Precision medicine, also known as personalized medication, is now surfacing more than ever, but could not have happened without the years of research and billions of dollars in funding to…
Research into possible facial creams containing the medicine rapamycin have found that they are effective for reducing facial tumours in people with tuberous sclerosis complex. The full article can be…
According to an article from Globe Newswire, the company Shire plc recently presented new data in relation to recombinant human parathyroid hormone (rhPTH) and its relationship to hypoparathyroidism. This information…
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
