I sofferenti cisti della fibrosi britannica stanno lottando per Orkambi: ecco come puoi aiutarti

Orkambi (ivacaftor / lumacaftor) è la seconda medicina di precisione da licenza per uso nel Regno Unito da persone con fibrosi cistica. La presa? Non è attualmente fornito dal Servizio…

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Les victimes britanniques de la fibrose kystique se battent pour Orkambi: voici comment vous pouvez vous aider

Orkambi (ivacaftor / lumacaftor) est le second médicament de précision à être autorisé à être utilisé au Royaume-Uni par des personnes atteintes de fibrose kystique. La prise? Il n'est actuellement…

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All Eyes are Open for This New Narcolepsy Drug
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All Eyes are Open for This New Narcolepsy Drug

At a recent conference, Jazz Pharmaceuticals presented positive efficacy results from the JZP-110 (TONES) studies in adult patients with sleep impairment conditions and the excessive sleepiness associated with these diseases.…

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Statins May Do More Than Lower Cholesterol: They May Give IPF Drugs a Boost
Statins May Do More Than Lower Cholesterol: They May Give IPF Drugs a Boost

Statins May Do More Than Lower Cholesterol: They May Give IPF Drugs a Boost

For people living with Idiopathic Pulmonary Fibrosis (IPF), every day is part of an ongoing battle to hold on tight to lung function as long as possible. That battle can…

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World Hemophilia Day Ignites Hemophilia Awareness and Explodes with Inspiration
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World Hemophilia Day Ignites Hemophilia Awareness and Explodes with Inspiration

I came across an interesting blog about World Hemophilia Day (WHD) which was April 17th, 2017. It’s an interesting read, and fairly simple, one every woman should know about for inspiration,…

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This Drug Would Target the Heart of Genetic Obesity
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This Drug Would Target the Heart of Genetic Obesity

Rhythm Pharmaceuticals is currently developing a melanocrotin-4 (MC4) receptor therapy called setmelanotide for the treatment of obesity and related disorders caused by genetic defects. This therapy could potentially be used to…

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Relapsed or Refractory Does Not Have to Mean Untreatable
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Relapsed or Refractory Does Not Have to Mean Untreatable

At the recent Annual American Society of Clinical Oncology (ASCO) Meeting, bluebird bio, Inc. released updated data from its Phase 1 trial of bb2121. bb2121 is a new anti-BCMA chimeric…

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This Just In! Promising Results from Ulcerative Colitis Clinical Trial!
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This Just In! Promising Results from Ulcerative Colitis Clinical Trial!

The highly-anticipated data from Pfizer's Phase 3 Octave Studies of tofacitinib in ulcerative colitis patients were published early last month in The New England Journal of Medicine. The data overall…

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