Who needs a shot of feel good today?! Young Skye Savren-McCormick was diagnosed with juvenile myelomonocytic leukemia in 2016 and required a bone marrow transplant - and Hayden Hatfield Ryals…
According to a story from govloop.com, Dr. Daniel Kastner, the Scientific Director for the Division of Intramural Research at the National Institutes of Health (NIH), has committed his career to…
Helena Baker is the Vice President of Clinical Strategy at Medical Research Network, a Nurse, and also, a rare disease patient. I had the opportunity to interview her for a…
According to a story from medicalxpress.com, early tests of a gene therapy for X-linked myotubular myopathy are showing promising results. This could represent a major breakthrough for this disease, which…
A researcher from the University of Alabama at Birmingham is working on how to improve treatment for patients with status epilepticus. The original article can be read here, at UAB…
The final results from a study of the experimental drug tegsediTM (inotersen) for the treatment of patients with hereditary ATTR amyloidosis with polyneuropathy have been published. The original article can be…
Cleveland Clinic’s first every three-way kidney transplant has taken place. It involved six people in total: three donors and three recipients. The full article can be read here, at the…
When you think of arthritis, naturally the first thing that comes to mind is an older person - and with good reason, since artists is more common in people over…
According to PRNewswire, Beverly Hills, and Frankfurt based INFUSIO donated $5000 each of their patient’s Lyme disease treatment in May. Interest in the program was high. As a result, INFUSIO…
For any John Oliver fans out there, you know his thing is deep-diving into topics of importance - from beauty pageants to international elections to failing American infrastructure - just…
The experimental drug olinciguat (IW-1701) has been granted Orphan Drug Designation by the U.S. Food and Drug Administration (FDA) for the treatment of sickle cell disease. The full article can…
The Children’s Hospital Colorado has announced that it will part in a Phase 3 clinical trial for an experimental new cystic fibrosis therapy. The full article can be found at…
Happy Independence Day Weekend! As the firework shows wind down, we want to wrap up the week with three great contributor stories, and one research update. First, we have some…
Dewayne Johnson used to work as a school groundskeeper. Now, some days, he can’t manage to speak as a result of the cancer he lives with. Now, despite professional expectations…
According to The Seattle Times, the prognosis of a certain four-drug combination is much greater for patients with pancreatic cancer than the typical single standard cancer treatment. This discovery is…
According to a story from the Washington Post, Dr. Rahul Desikan had chosen to dedicate much of his research career to the study of long term, neurodegenerative illnesses. About a…
A biotechnology company called Valneva is developing an experimental vaccine for Lyme disease. Valneva has said that it is making progress in the vaccine development. A Phase I trial has…
According to University of Wisconsin News, UW-Madison professor David Beebe and his colleague Anna Huttenlocher, fellow UW professor, were awarded a $3.7 million grant from the National Institutes of Health (NIH)…
The Orphan Drug Designation awarded to the drug dovitinib for treating adenoid cystic carcinoma has been transferred from Novartis to Oncology Venture. The full article can be found here, at…
According to a June 29th report by Business Wire, ACADIA Pharmaceuticals Inc. received a new FDA approval for a form of Parkinson’s treatment. The approval specifically allows ACADIA to produce…
A recent study has found that ‘clock’ genes that help to regulate the body’s circadian rhythm may be affected by spinal muscular atrophy. The original paper, which is published in…
According to a story from the Vancouver Sun, the College of Physicians and Surgeons of B.C. recently issued new requirements in regards to the usage of opioids for treating patients…
According to a story from Global Knock, a woman with spina bifida died after a severe bedsore on her back became infected. Chrissy Dunnington was in long term care at…
July 13th is Gastrointestinal Stromal Tumors Awareness Day! And that "13" has extra relevance. 5,000 Americans are diagnosed with Gastrointestinal Stromal Tumors (GIST) each year. That’s 13 people diagnosed each day.…
The US Food and Drug Administration (FDA) has approved an Investigational New Drug (IND) application for an experimental drug that is being researched for its use as a treatment for…
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