Results from research into an experimental therapy called SL-401 for the treatment of patients with blastic plasmacytoid dendritic cell neoplasm have been shared at the Congress of the European Haematology…
According to Medical Xpress, gene therapy may become the next treatment option for those with chronic kidney disease, CKD. Researchers at Washington University School of Medicine in St. Louis have…
Kalytera Therapeutics, Inc. has announced that a meeting with the Centre for Drug Evaluation and Research of the US FDA is planned for Tuesday, 31st July this year. The purpose of…
According to a story published by STAT, a daredevil neuroscientist at Stanford University is utilizing the relatively new concept of virtual reality to solve an unsuspecting problem. Not only is…
BrainStorm Cell Therapeutics Inc. has announced that it has secured its second U.S. manufacturing location for NurOwn®, an experimental drug currently under investigation for the treatment of amyotrophic lateral sclerosis…
According to a story from the Deccan Chronicle, researchers may have discovered a new treatment for Dupuytren's contracture that could offer substantial benefits over currently available treatment options. The scientists…
According to a story from medicalresearch.com, recent research has revealed that many pancreatic cancer tumors appear to have vulnerabilities to treatments that take advantage of genetic mutations that are present…
According to an article from the Detroit News, the most recent budget proposal from the Trump administration would call for cuts to Medicare to the tune of $236 billion over…
Bruce Howell is 63 years old living with retinitis pigmentosa. He’s been legally blind since age 37. As a result, public transportation is a critical service to him. Without the…
According to a story from pm360online.com, a new study of Prader-Willi syndrome will soon be under way thanks to a recent collaboration between the biopharmaceutical company Zafgen and the Foundation…
According to a story from Psychology Today, a study from 2017 titled Cognitive behavioral therapy is effective in misophonia: An open trial concluded that cognitive behavioral therapy could play a significant role in…
Ellil Mathiyan is the sort of lively character most people can’t believe experienced a double cancer diagnosis. He describes how people usually respond with “are you sure?” or “you’re kidding”…
As I’ve gotten older, I realize I’ve become more introspective, analyzing my relationships, emotions, spiritual well being, and mental health. While talking to others with rare diseases I’ve learned it…
Organisations are planning to develop new clinical practice guidelines for the diagnosis and management of von Willebrand disease. The original article can be read here, at PR Newswire (whose source…
According to BioPortfolio, the company UniQure has recently announced that the first hemophilia B patient has been enrolled in their Phase III study of the treatment AMT-061, which is an…
According to a story from CNN, Nick Foles, who plays for the Philadelphia Eagles, helped lead the team to victory at the Super Bowl, and was awarded MVP for the…
If you look on Ed Sheeran's Instagram you will see a recent photo of him and a beautiful eleven-year-old fan. But this is not just any fan-- the picture holds…
A recently published study found that, out of the people studied, young cancer survivors were more likely to develop endocrine diseases than people who had no history of cancer. The…
Researchers investigating the symptoms of testicular cancer have published their results in the British Journal of General Practise. Their study showed that testicular enlargement from a lump or swelling is…
Duncan Avery is father to two children, Kalea, and Noah. At age six, doctors discovered Kalea had a tumor in her brain. They would successfully remove it via surgical methods.…
According to a story from Jewish Community Voice, the BRCA Founder Outreach Study, which is a national, cancer-focused research study, is offering free screenings for people of Ashkenazi Jewish descent.…
Miracle Flights help children to fly to access medical treatment. They work to support people like Shelby, who was diagnosed with alveolar soft part sarcoma at the age of seventeen.…
Most of us are familiar with Parkinson's Disease. Parkinson’s disease is a central nervous system disorder affecting movement. It is a progressive disease and develops gradually, sometimes starting with a subtle tremor in…
According to Medical Xpress, Chris Jones from the Institute of Cancer Research in the UK has delved into the complexities of the rare childhood brain tumors called diffuse intrinsic pontine…
According to a story from sciencedaily.com, recent research has revealed the mechanism that causes hypokalemic periodic paralysis, a rare condition that causes patients to experience sudden, severe muscle weakness. The…
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