uniQure Receives FDA Fast Track Designation for AMT 130 Gene Therapy for the Treatment of Huntingtons Disease

LEXINGTON, Mass. and AMSTERDAM, the Netherlands - uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing transformative therapies for patients with severe medical needs,  announced that the U.S. Food and Drug…

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Drag Queen on RuPaul’s Drag Race Television Show Talks About Ehlers-Danlos Syndrome 

Any fans of RuPaul Drag Race or the art of drag itself? Raise your manicured hand! Well, regardless of your answer - watch how the world of drag and rare…

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New Phase 1 Clinical Trial for Mastocytosis, MDS, and AML has Just Begun!

GT Biopharma has just announced that their Phase 1 clinical trial for Mastocytosis, Myelodysplastic Syndrome (MDS), and Acute Myeloid Leukemia (AML) has been authorized to begin. Although this investigation had previously…

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Experimental Treatment for Sanfilippo Syndrome Type B Gets Fast Track Designation
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Experimental Treatment for Sanfilippo Syndrome Type B Gets Fast Track Designation

According to a story from finanznachrichten.de, the biopharmaceutical company Abeona Therapeutics, Inc. recently announced that its experimental medical product ABO-101 has earned Fast Track designation from the US Food and…

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Epigenetic Test Developed in UK Could Help Diagnose Genetic Disorders

According to the publication from the London Free Press, a new technique in development at Lawson Health Research Institute uses epigenetics to more closely study genetic expression in humans. Epigenetics…

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