According to a story from the Derby Telegraph, four-year-old Audrina Hatton-Wright was diagnosed with a rare cancer called neuroblastoma about a year ago. This cancer mostly affects children. Doctors initially…
Sarcoidosis is a rare condition which causes inflammatory cells to build up in various organs throughout the body. For 90% of people with a sarcoidosis diagnoses, the lungs are one…
According to a story from Oral Cancer News, a class of immunotherapy drugs called immune checkpoint inhibitors can play a critical role in treating a number of common and rare…
The State of Cancer in the United States A recent report posted by the American Cancer Society has indicated that cancer rates in the United States have been continuously falling over…
According to a story from the Philly Voice, it has been nearly nine years since Dr. David Fajgenbaum was first diagnosed with idiopathic multicentric Castleman disease. This immune system disorder…
According to a story from Physician's Weekly, the pharmaceutical company AbbVie, Inc. recently announced that its cancer drug Imbruvica failed to measure up in a recent clinical trial in which…
Autoimmune hepatitis (AIH) is a rare condition which causes inflammation in the liver. It can lead to cirrhosis and ultimately, liver failure. The typical treatment for patients with the disease includes…
According to a story from Scleroderma News, a recent study found that while treatment approaches for juvenile localized scleroderma were quite consistent in the UK, there were significant disparities in…
According to a story from Science Daily, a team of scientists from the Translational Genomics Research Institute (TGen) have identified the likely cause of a recent outbreak of an unusual…
We've made a lot of progress in cancer research in recent years. Many novel therapies have been developed for illnesses previously considered untreatable. However, as new treatments have been discovered,…
According to a story from brightsurf.com, a team from the Washington University School of Medicine, based in St. Louis, has succesfully developed a gene therapy that appears to prevent damage…
According to a story from StartUp Health, the organization has recently partnered with Chiesi Farmaceutici, an Italy-based pharmaceutical company, in order to call for innovation and new advancements in the field…
According to a press release from the biopharmaceutical company Cerecor, Inc., the US Food and Drug Administration (FDA) recently agreed to accept the company's Investigational New Drug (IND) application for its…
According to a story from news-medical.net, a team of researchers have found that patients with inflammatory bowel disease display distinct changes to the makeup of bacteria that live in their…
According to a story from PR Newswire, the international drug developer Eli Lilly and Company recently announced the results of a Phase 3 clinical trial testing the company's drug LARTRUVO…
According to an article published by Washington University of Medicine in St. Louis, scientists appear to have succeeded in slowing axon destruction in mice through standard gene therapy. Though an…
A concerned Texas mom finally has answers about the cause of her son’s sensory-processing problems, thanks to a special collaboration among her patient-advocacy group and the lab of Scripps Research…
The Florey Institute of Neuroscience (FIN), one of the world’s largest and most respected brain research centers, recently announced trial results for the drug CuATSM, developed by FIN, the School…
David Radford, a 63-year-old resident of Oxford, UK, and a liver cancer survivor, said his surgeon attributes his successful liver transplant to the new normothermic perfusion machine. As reported recently…
According to a story from Medical Xpress, a recent study found that people who survived Hodgkin lymphoma during their childhood were at a greater risk of developing another type of…
Hope everyone is having a wonderful Wednesday! The weather where we are is freezing this week-- but that's a perfect excuse to sit down with a few of our top…
Danon disease is a rare condition caused by a mutated LAMP-2 gene. This gene has three different forms- LAMP-2A, 2B, and 2C. Depending in which variant is mutated, individuals with…
According to a story from BioPortfolio, the biotechnology company Vertex Pharmaceuticals recently announced that the European Commission has approved a label extension for the company's cystic fibrosis drug Orkambi. Under…
aTTP aTTP, or acquired thrombotic thrombocytopenia purpura, is an immune condition which results in severe Thrombocytopenia. Thrombocytopenia means the body doesn't have enough platelets in the blood. In aTTP, it's caused…
According to a story from news-medical.net, a recent study has a found that a hidden disease called hemochromatosis could be a major risk factor for several different joint diseases and…
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