Spinal muscular atrophy is rare progressive muscular disease that over time, erodes a patient’s movement. Without early intervention, the condition erodes the young patients ability to breathe and even swallow.…
Medical professionals are still working to uncover the cause of Alzheimer's disease. While they believe that a combination of genetic and environmental factors paired with certain lifestyle choices leads to…
According to a story from Parkinson's News Today, a three-year study has determined that dancing to music weekly may help slow the progression of Parkinson's disease symptoms. This effect included…
Normally, B lymphocytes ("B cells") are a type of white blood cell that plays a role in immune function. In healthy individuals, B cells create antibodies to fight infections and…
Accessing treatments can be difficult, especially if one is impacted by a rare disease. In fact, only 5% of rare diseases have an FDA-approved treatment. Because of this, many patients…
In a news release from mid-July, 2021, biopharmaceutical company Strongbridge Biopharma plc ("Strongbridge") shared the publication of new post hoc analyses regarding KEVEYIS (dichlorphenamide) for patients with Primary Periodic Paralysis…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
Researchers at NYU Abu Dhabi (NYUAD) have discovered the code that is associated with the liver’s genome (complete set of DNA) and its ability to regenerate. According to a…
Even though a drug is sometimes developed with a certain condition in mind, it can be used to effectively treat or manage alternate conditions. For example, pembrolizumab (KEYTRUDA) is…
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