Before you read on, make sure you take a look at Pt. 1 of our interview, which goes over what PGAP3 is, Lucy's story, and the reasons behind why Zach and Geri…
The Problem: Colorectal Cancer (CRC): It is fourth on the list of life-threatening cancers in the United States and the number of incidents is rising mostly among people under fifty…
Over the last few years, the incidence of nonalcoholic fatty liver disease (NAFLD) has increased rapidly. As a result, many researchers are beginning to pay closer attention to this disease…
“My son has Costello syndrome, but he is not defined by his diagnosis,” Ryan Sheedy tells me about his son, Reynolds. To Ryan, his statement exemplifies his beliefs about needed…
The incidence of nonalcoholic fatty liver disease (NAFLD) has been rapidly rising worldwide, with many healthcare providers expressing concern. Because of this rapid growth – and simultaneous problems with underdiagnosis…
Zach and Geri Landman are devoted parents and physicians – a pain specialist and pediatrician, respectively – committed to making the world a better place for those around them. They…
According to a story from express.co.uk, the COVID-19 pandemic was a shock to the world when it first struck over two years ago, and while we have a better understanding…
Currently, there are upwards of six million people in the United States alone living with Alzheimer’s disease. As some researchers work to determine the exact cause of this neurodegenerative…
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…
Have you ever heard of machine learning? Machine learning is a form of artificial intelligence (AI) which teaches systems to learn, act, and improve an experience without explicit programming.…
According to a recent press release from Globe Newswire, Albireo Pharma announced that Lancet Gastroenterology published results of the PEDFIC 1 trial evaluating Bylvay® in the treatment of progressive…
This is Part Two of a two part story. Click here to read Part One. Joyce Sanchez, M.D., professor at Wisconsin’s Medical College, supported the women by stating that…
The Cure Mito Foundation, a Patient Worthy partner organization, and integrative Cardiovascular Metabolism and Pathophysiology Laboratory (iCaMP) at Boston University, are hosting a virtual conference titled "Empower and Inspire: Understanding…
Could a vaccine help treat cancer such as Merkel cell carcinoma (MCC)? Immunomic Therapeutics believes so. Its therapeutic plasmid DNA (pDNA) vaccine, ITI-3000, is designed for those with MCC,…
Unfortunately, doctors and scientists are still learning about Zellweger syndrome, a rare multisystem genetic disorder. But this can be incredibly difficult for families whose children are diagnosed – after all,…
Desiree Thompson recently turned three years old – and the Tulsa County Sheriff’s Office (TSCO) planned a big surprise for her. You see, Desiree, who has epilepsy and lissencephaly, absolutely…
As many people in the rare, chronic, or underserved disease community know, the journey to diagnosis can be a long and difficult one. For Texas resident Cheryl Yetz, the diagnostic…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
A recent article published in Physicians Weekly and also by the National Institute of Health stated that immunosuppressive medication and kidney biopsies may not be necessary if children with…
According to a story from Charcot-Marie-Tooth News, the Global CMT Research Convention is set to take place in Cambridge, Massachusetts on September 16-17, 2022. Organized by the CMT Research Foundation,…
Currently, there are an estimated 30 million people in the European Union (EU) who are living with a rare disease. Drug developers are incentivized to create therapies for those…
This is Part One of the two part story. Stay tuned for Part Two Imagine being told the pain you are feeling throughout your body is not real and then…
Currently, clinical-stage oncology company Sumitomo Pharma Oncology, Inc. is working to develop DSP-5336 for patients with acute myeloid leukemia (AML). The company even began recruiting for a Phase 1/2 study…
In an August 3rd, 2022 news release from Syros Pharmaceuticals (“Syros”), the company shared that its product tamibarotene had received a positive opinion for its Orphan Drug designation application.…
In a news release from biopharmaceutical and RNAi therapeutics company Alnylam Pharmaceuticals, Inc. ("Alnylam"), the company shared that positive data was available from the Phase 3 APOLLO-B clinical trial.…
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