According to a recent article, a woman dealing with chronic fatigue and multiple UTI’s was not diagnosed with ovarian cancer until she was rushed into the hospital after collapsing. Ovarian…
In October 2021, the FDA approved Susvimo (ranibizumab injection) for the treatment of wet age-related macular degeneration. Now, shares WFMZ, Dr. Chin Yee from Georgia Retina has performed the first…
As many of you know, Rare Disease Day 2022 is coming up at the end of the month. Celebrated on February 28, Rare Disease Day aims to raise awareness and…
Compassion [kuhm-pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the suffering. Compassion Corner is a…
February 1st marked the beginning of Turner Syndrome Awareness Month, which is an entire month dedicated to learning about this rare disease and raising awareness. The Turner Syndrome Foundation (TSF) has…
Orphan drug designation is granted to drugs or biologics intending to treat, diagnose, or prevent rare diseases or conditions. Within the United States, a rare condition is one affecting under…
Newborn screening is a public health program which screens infants for a variety of genetic, endocrine, and metabolic disorders following birth. For example, a newborn screening panel may test for…
The Central Mississippi Down Syndrome Society (CMDSS) is a parent-driven nonprofit organization which serves to provide support for Central Missourians with Down syndrome and their families. In addition to offering…
According to a recent article in SMA News Today, more spinal muscular atrophy (SMA) patients in the United Kingdom (UK) will have access to Zolgensma. This change comes after the…
According to an article recently published in Clinical Trials Arena, the Swedish pharmaceutical company Oncorena has recently initiated a Phase I/II trial for orellanine. This investigational treatment is intended for…
According to a recent article, a research team discovered that the inhibition of sphingolipid synthesis on mice models of Duchenne muscular dystrophy can counteract the certain symptoms of the disease.…
According to a recent article, Revolo Biotherapeutics announced it has obtained approval from the Medicines and Healthcare products Regulatory Agency (MHRA) for two Phase 2 clinical trials to analyze its…
According to a recent article, a study shows that patients with epithelial ovarian cancer do present with at least one symptom the majority (72%) of the time. Ovarian Cancer Ovarian…
Research by three doctors provided a basis for tyrosine kinase inhibitors (TKI) and offered advancements in treatment for renal cell carcinoma (RCC) patients. Two such TKIs, sunitinib and sorafenib, remain…
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…
In a February 8, 2022 news release, late-stage clinical company Synthetic Biologics, Inc. shared that the FDA granted Orphan Drug designation to the therapeutic candidate VCN-01. VCN-01 is a therapeutic…
The Memorial Sloan Kettering Cancer Center has recently released skincare guidelines and tips for those living with cutaneous T-cell lymphoma (CTCL). It's important that impacted individuals take good care of…
The week of February 7-14, 2022 is being recognized as Congenital Heart Defect Awareness Week, a time to help spread awareness about congenital heart defects. While individual heart defect conditions…
Rare Disease Day, which is recognized each year on the last day of February, is probably the biggest day for rare disease patient advocacy annually. There are always a wealth…
People with epidermolysis bullosa (EB) often experience symptoms such as intense itching or severe pain. Unfortunately, these symptoms can be debilitating and may greatly affect overall quality-of-life. However, some burgeoning…
There are many inequities in our society, and many of these exist within the healthcare sphere. In this article, we're specifically going to look at the inequity that Black women…
According to a recent article, the European Commission (EC) has approved Merck’s KEYTRUDA as an adjuvant treatment for type renal cell carcinoma (RCC), a type of kidney cancer. Renal Cell…
According to a recent article, patients with recurring kidney cancer who would most likely need to get their kidney removed can now possibly keep their organ thanks to a new…
According to a study published in PLOS Medicine, only around half of pragmatic or 'real-world' trials collect data as reported by patients or involve patients as partners in research. This…
Positive results were announced today by Anavex Life Sciences, which is based in New York, for its Phase 3 clinical trial of Anavex 2-73. Participants in the trial were female…
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