Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
In a recent press release, biopharmaceutical company Regulus Therapeutics, Inc. announced that their drug candidate, RGLS4326, received Orphan Drug Designation for the treatment of autosomal dominant polycystic kidney disease…
Excited, nervous, worried: a lot of varied emotions go into being pregnant and giving birth. But during COVID-19, a global pandemic? It's understandable that those feelings are amplified. Currently,…
While medications and surgery can both improve gastroparesis symptoms, many patients still struggle with finding the right treatment. However, a new medication might soon help: tradipitant. In a study published…
Biopharmaceutical company Theratechnologies Inc. recently announced that its therapy candidate tesamorelin is effective in the treatment of HIV-associated nonalcoholic steatohepatitis (NASH). According to new data, published in JCI Insight, tesamorelin…
There's no misunderstanding this fact: renal-replacement therapy is effective for patients with severe acute kidney injuries (AKI). However, states Kenny Walter in MD Magazine, the efficacy of this treatment can depend…
Thanks to the rampant spread of COVID-19, many events, symposiums, and clinics moved online. One was the 2020 ACR State-of-the-Art Clinical Symposium, in which participants discuss diagnostic information, treatments,…
During EHA25 Virtual, researchers presented on hematological concepts and the future of diagnosis, treatment, and research. One such presentation discussed results from the InHIBIT-Bleed study, which examined the efficacy…
Thanks to COVID-19, many annual meetings and other events have been held online this year. One such event was the American Society of Retina Specialists (ASRS) Virtual Annual Meeting,…
When Emilia Galarneau grows up, she'll have quite an exciting story to tell about her birth. According to the Connecticut Children's Medical Center, Emilia was born on March 6th,…
It's no secret that stress, anxiety, and depression can negatively affect us physically. But according to Myasthenia Gravis News, researchers also linked stress and depression to increased relapses for…
As society progresses, certain diseases or conditions become more and more prevalent. For example, chronic conditions like osteoporosis or diabetes have rapidly risen over the past decade. Now, according…
Experimental and innovative new technologies play a crucial role in advancing the medical sphere. Although nanomedicine is uniquely poised to treat diseases through nanotechnology, it typically comes with a…
In order to better understand rare conditions and diseases, researchers sometimes create registries and biobanks full of resources. Recently, the Solve ME/CFS Initiative (Solve M.E.) announced the launch of…
Sick of being locked inside with nothing to do? Well, this is just your luck! On July 22, you can celebrate the 6th annual World Brain Day from the…
If you're part of the rare disease community, then you probably are not a stranger to explaining your condition to others. But think about it. Has this ever been…
In a recent press release, Knopp Biosciences announced that their drug therapy KB-3061 was granted Rare Pediatric Disease Designation to treat patients with KCNQ2 epileptic encephalopathy (KCNQ2-EE), a rare…
Although we may feel like the world is stopped, thanks to COVID-19, many companies consistently push for technological advances. According to Myeloma Research News, GNS Healthcare is one of those…
According to CLL Pharmacist, results from the Phase 3 GENUINE trial show that, when taken in conjunction, ibrutinib and ublituximab lead to better patient outcomes than either drug alone.…
According to SeekingAlpha, biotechnology company QED Therapeutics recently announced that the first pediatric patient was dosed in the PROPEL 2 trial. The mid-stage trial, which is testing the investigational…
Recently, pharmaceutical company RIBOMIC announced that the first patient was dosed in their Phase 1 clinical trial. Ultimately, the trial is meant to determine whether RBM-007 could be an effective…
At the start of 2020, we had no idea what this year would bring: COVID-19, a novel coronavirus declared a pandemic in March. As of the morning of July 17,…
It's no secret to anybody that knows me: I struggle with anxiety, and have for as long as I can remember. I was first medicated for anxiety and depression…
This past week, biopharmaceutical company Kiniksa Pharmaceuticals announced that their drug, rilonacept, received Orphan Drug Designation from the FDA. Following positive data from the RHAPSODY Phase 3 clinical trial,…
In the GRAPPA 2020 Annual Meeting, held virtually this year, Dr. Philip Helliwell acknowledged that he, like many rheumatologists, struggled to understand a certain condition: SAPHO syndrome. According to…
According to a recent press release from Albireo Pharma, the first participant has enrolled in the BOLD trial. The BOLD trial, which stands for Biliary atresia and the use…
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