Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
According to the Cambridge Network, Cambridge University Hospitals NHS Foundation Trust (CUH) is starting a new clinical trial to test two experimental treatments for COVID-19. The trial, called TACTIC-E,…
In a recent press release, biotechnology company Sarepta Therapeutics announced positive findings from their clinical trial studying SRP-9003 as a treatment for limb-girdle muscular dystrophy (LGMD) type 2E. This…
You have a number of different cells throughout your body, all of which perform different functions or provide support. One extremely interesting type are astrocytes, star-shaped glial cells that…
Over the last few years, I've heard the refrain that my health - oddly - starts in my gut. So whenever I got sick, someone would advise me to…
Plakous Therapeutics released a press release to announce that Protego-PD™, their therapy for infants with necrotizing enterocolitis (NEC), received both the Orphan Drug and Rare Pediatric Disease designations from the FDA. There are…
According to Parkinson's News Today, the FDA is reviewing Gocovri as a potential treatment for "off episodes" in patients with Parkinson's disease who are already taking levodopa. "Off episodes"…
The medical field has seen many advancements over the past few decades. In particular, treatment for rheumatic diseases has greatly improved. However, states Healio, this is not reflected in patient…
This year, thanks to COVID-19, the European Hematology Association (EHA) took their annual conference online - but that didn't prevent some intriguing new insights and ideas. In a press release,…
At this year's EULAR 2020 E-Congress, Dr. Suzanne Verstappen, MD, presented on how lifestyle changes could benefit patients with rheumatic and musculoskeletal diseases (RMDs). Her interest in the impact of…
High dose-intensive chemotherapy regimens have been shown as effective for children with Burkitt lymphoma. However, the intensity often leads to discomfort, adverse reactions, and poor outcomes in adult patients, particularly…
Recently, a team of Yale researchers wanted to understand how genetic mutations in patients with Rett syndrome resulted in neurological issues. Using a unique type of genetic testing, researchers were…
This week, UbiVac and Bristol Myers Squibb announced their clinical trial collaboration in a Biospace press release. The two companies, in a Phase 1b trial, look to study whether combining…
It is crazy to think back to a few months ago and see how much has changed. In March, SARS-CoV-2, which you probably know as COVID-19, was declared a global…
Every day, the world becomes increasingly technological. With this comes advances in many realms, from healthcare to education. Recently, says Parkinson's News, medical technology company Manus Neurodynamica received £750,000 (approx. $950,000)…
What better way to study Parkinson's disease than...to not study it? Well, according to Parkinson's News Today, researchers are hoping to learn more about the disorder by doing just that.…
According to a recent press release, biopharmaceutical company CASI Pharmaceuticals filed a Clinical Trial Application (CTA) (IND) in the United Kingdom. CASI Pharmaceuticals is hoping to test the safety…
Currently, up to 5% of American citizens have nonalcoholic steatohepatitis (NASH), a liver disease resulting in damage and inflammation. But there's no approved treatments, presenting an unmet need in…
In the past, there have been few effective treatments for patients with primary hyperoxaluria type 1 (PH1), a genetic disorder causing kidney damage and failure. But, according to News Medical,…
When the 19-year-old French woman first visited the hospital, she was extremely lethargic. She displayed neurological symptoms. Upon kidney failure, the patient was admitted into the ICU. But soon, doctors…
Five years ago, Leah Gaitan-Diaz's life changed when she was diagnosed with myasthenia gravis. But with this condition comes a lack of understanding or confusion over what it entails. In…
In Spain, a young child showed signs of muscle atrophy and difficulty walking; she wasn't quite stable on her feet and struggled with balance and coordination. But it wasn't until…
An estimated 25-30 million Americans are part of the rare disease community. If you're one of them, you share a common (yet uncommon) experience: public scrutiny, difficulties in diagnoses, treatment…
Education, research, support, and patient advocacy: these are just four of the amazing things that rare disease or disorder foundations offer. Many foundations seek to offer programs and resources to…
Have you ever heard a sound that makes you want to clamp your hands over your ears? Well, for people with misophonia, this aversion to certain noises can be…
According to a Town News press release, Sound Pharmaceuticals, a biopharmaceutical company based in Seattle, received FDA approval for their Phase 3 clinical trial on SPI-1005. The trial, STOPMD-3,…
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