Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
In a recent news release on Morningstar, biopharmaceutical company Albireo Pharma, Inc. ("Albireo") shared that its investigational drug candidate Bylvay (odevixibat) earned a positive opinion from the European Medicines…
Sometimes, medical studies just don't go the way that companies want them to. According to MedCity News, this is what biotechnology company Larimar Therapeutics ("Larimar") was faced with during…
In 2019, generic pharmaceuticals and biosimilars leader Sandoz launched intravenous treprostinil for patients with pulmonary arterial hypertension (PAH). But according to a new media release, generic treprostinil is now…
When Gwen Dillon's son, Aaron, was just 1.5 years old, he was diagnosed with craniosynostosis, a birth defect in which the bones of a baby's skull close early. According to…
In a recent company update, via AccessWire, biotechnology company Aptevo Therapeutics Inc. ("Aptevo") shared positive results from a Phase 1 dose-escalation trial. During the trial, Aptevo evaluated APVO436 for patients…
From May 11 to 14, 2021, the American Society of Gene & Cell Therapy (ASGCT) Virtual Annual Meeting took place. During the 24th annual meeting, a variety of stakeholders met…
If you could use a genetic test to determine your risk of developing a specific condition, would you? Earlier identification and diagnosis is crucial in improving patient outcomes, as well…
Normally, amyotrophic lateral sclerosis (ALS), a progressive neurodegenerative disorder, affects individuals between ages 50-60, with prevalence increasing with age. Once diagnosed, patients typically survive for another 3-5 years. However,…
According to a recent news release, the Lennox-Gastaut Syndrome (LGS) Foundation shared that its 6th Annual Walk 'n' Wheel event will take place on June 5th, 2021. The event…
On May 24, 2021, biopharmaceutical company NeoImmuneTech, Inc. shared that the first patient was dosed in a pilot study centered around NT-I7 (efineptakin alfa). Altogether, the study is designed…
In a press release from late May 2021, AAV gene therapy company and Bayer AG subsidiary Asklepios BioPharmaceutical, Inc. ("AskBio") shared that the FDA approved its Investigational New Drug (IND)…
Over 50 years ago, levodopa was approved to treat patients with Parkinson's disease. To this day, levodopa, administered via pills or intravenously, remains the standard-of-care. But according to Parkinson's News…
A majority of individuals who have strokes are over the age of 60. But what happens when younger individuals have unexplained strokes? What causes these to happen? According to a…
In early May 2021, pharmaceutical company GlaxoSmithKline shared that its therapy Benlysta (belimumab) was approved by the European Commission (EC) for expanded use in adult patients with lupus nephritis…
During the American Society of Gene & Cell Therapy (ASGCT) 24th Annual Meeting, which took place virtually from May 11-14, 2021, biotechnology company M6P Therapeutics ("M6P") presented preclinical data…
Head and neck squamous cell carcinoma (SCC) is considered both aggressive and difficult to treat. In fact, doctors estimate that nearly 50% of all patients will eventually see the recurrence…
Recently, the FDA granted Priority Review status to a supplemental New Drug Application (sNDA) for zanubrutinib, MPR reports. While the treatment, under the brand name Brukinsa, is currently indicated for…
To this day, Colleen Sosinski still isn't quite sure how her journey with necrotizing fasciitis began. During summer 2020, she was relaxing and enjoying the sun. Then, as reported by…
The CDC notes that in 2019, an estimated 409,000 people globally died of malaria - but a majority of those who died were children in sub-Saharan Africa. In fact, 94%…
For patients and families, finding a supportive community can be extremely helpful. These communities spur research, offer a sense of understanding, and build awareness. This is exactly what Susan G.…
From May 11-14, 2021, the American Society of Gene and Cell Therapy (ASGCT) held its 24th Annual Meeting. Due to COVID-19, the meeting was held virtually - but that didn't…
There are multiple gene mutations associated with severe combined immunodeficiency (SCID), a rare genetic disorder which severely inhibits - or stops - immune function. But according to New Atlas, an…
While some therapies offer potential benefits to patients, not all therapies show efficacy within the clinical trial environment. Recently, shares MedCityNews, this occurred with biotechnology company Biogen Inc.'s ("Biogen") gene…
From April 23-25, 2021, the American Academy of Dermatology (AAD) held its Virtual Meeting Experience (AAD VMX 2021). During the event, over 75 meetings discussed various research and other insights…
The U.S. Food and Drug Administration (FDA) runs a number of programs designed to facilitate research and drug development for serious conditions. One such program is the Fast Track program;…
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