Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.
According to FirstWord Pharma, patients with paroxysmal nocturnal hemoglobinuria (PNH) in the United Kingdom (UK) may soon have a more effective and efficient, and less invasive, treatment option. Currently, the…
In 2009, the FDA approved Tyvaso (treprostinil) Inhalation Solution to reduce symptoms associated with Group 1 pulmonary hypertension (PH), also known as pulmonary arterial hypertension (PAH). Beyond symptom reduction, the…
Growing up, I was always told that oral health related directly to regular health. But now, a study from researchers at the NYU College of Dentistry and Weill Cornell Medicine…
In mid-April, Kantar Health and the International Gaucher Alliance (IGA) shared the launch of a rare disease registry developed by the partnership. The registry, known as GARDIAN, will explore Gaucher…
Earlier this year, WP1066, a p-STAT3 inhibitor, received three separate Rare Pediatric Disease designations for the treatment of medulloblastoma, atypical teratoid rhabdoid tumor, and diffuse intrinsic pontine glioma. Now,…
Clinical trials can be beneficial in many ways. For one, these trials show researchers whether a treatment’s impact is durable and sustained. Determining this often requires some follow-up period. According…
According to Drug Target Reviews, there may be an emerging vaccination effective against preventing Zika virus infection. Though many cases are mild, the infection can cause severe birth defects and…
On April 1, 2021, biopharmaceutical company AbbVie shared that new data is available from the Phase 3 SELECT-PsA 1 clinical trial. The 24-week results follow the impact of RINVOQ (upadacitinib)…
In late March 2021, the FDA gave Fast Track designation to annamycin. The treatment, initially developed for patients with acute myeloid leukemia (AML), is now being explored for patients with…
#KnowThyNuts. While the hashtag, on its surface, sounds a bit funny, it is actually a call to action. According to a news release from Movember Canada, testicular cancer, though…
Could repurposing certain drugs help treat other conditions? Well, according to Technology Networks, yes. Recently, researchers from the UCL Great Ormond Institute of Child Health and the Great Ormond Street…
What if we could harness a naturally occurring compound to starve and kill serious brain tumors? According to Medical XPress, researchers from Queen Mary University of London are working to…
A variety of gene mutations cause retinitis pigmentosa (RP) - but how do those genes affect the degeneration of rod and cone photoreceptors in the eyes? According to Medical XPress,…
In a recent press release, immuno-oncology and biopharmaceutical company GT Biopharma, Inc. ("GT") shared the release of new data and results from the Phase 1/2 GTB-3550 TriKE clinical trial. Through…
As many patients within the rare disease community know, the diagnostic odyssey can be long and arduous. But what if burgeoning technologies, like artificial intelligence (AI) and its branches (machine…
From April 5 - 30, the American Chemical Society meets to hold ACS Spring 2021, where chemistry professionals meet to discuss new research and knowledge in their field. During the…
In a recent news release, biopharmaceutical company FibroGen, Inc. ("FibroGen") shared that its therapeutic candidate, pamrevlumab, received Fast Track designation from the FDA. The anti-CTGF antibody is designed to treat…
Over one year ago, the news became saturated with information on COVID-19, a novel coronavirus pandemic that has since swept the globe. At the time of this article, there are…
During clinical trials, Independent Data Safety Monitoring Boards (DSMBs) sometimes assess trial safety, trial integrity, and how well the trials are upholding patient needs. According to Business Insider, the DSMB…
Every autumn, VTE Dublin is held to discuss treatment, care, and research centered around venous thromboembolism (VTE). The conference consists of clinicians and experts who are passionate about improving the…
With genetic disorders, there is always a big question: do specific gene mutations respond differently to treatment? How can treatment be targeted to best suit the needs of patients? According…
In a news release from California Polytechnic State University ("Cal Poly"), the University shares how a joint study between itself and the University of South Florida ("USF") has garnered new…
Did you know that zebrafish are often used in genetic research? Not only do they have the same major organs and tissues as humans do, but zebrafish also share a…
From March 19-22,the Society of Gynecological Oncology (SGO) held its 2021 Annual Meeting on Women's Cancer. Because of COVID-19, the event was held virtually. During the meeting, researchers presented…
Could it be beneficial to harness a potentially devastating virus, such as Zika virus, for use in medical treatment? At first glance, this seems somewhat counterintuitive. Yet a news release…
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