According to a story from financialbuzz.com, the biotechnology company BIOPHYTIS has submitted documentation for orphan drug designation from the European Medicines Agency (EMA). This designation will be for Sarconeos, a…
According to a story from globenewswire.com, the pharmaceutical company Amicus Therapeutics recently announced that its drug Galafold had received official approval for public use in Japan. Galafold is the first…
According to a story from pressreleasepoint.com, a group of scientists at the University of Birmingham have a received funding to the tune of £3 million in order to conduct research on…
According to a story from Digital Trends, Google has recently added an option for wheelchair-accessible routes on its widely popular navigation tool, Google Maps. This option will make the app…
According to a story from medscape.com, the 2018 budget recently signed by the president is going to feature some spending increases for health-related services. These changes have the potential to…
According to a story from the National Institutes of Health, the innovative new CRISPR gene editing technology is being used in order to identify specific genes that could play a…
According to a story from biospace.com, a research team from the National Cancer Institute was able to successfully deliver an experimental nanomedicine to mice that had rare cancers such as…
According to a story from Medical Xpress, two new treatments were able to slow down the worsening of symptoms associated with muscular dystrophy in a mouse model study. Tamoxifen and…
According to a story from Walcha News, Felicity Nivison first began feeling paralysis and pain in her feet and hands. Soon, the symptoms spread to her legs and she was…
According to a story from webmd.com, diesel exhaust could increase the risk of developing amyotrophic lateral sclerosis, also known as Lou Gehrig disease. People who are exposed to diesel exhaust…
According to a story from pharmiweb.com, the pharmaceutical company Ovid Therapeutics announced recently that the U.S. Food and Drug Administration (FDA) has given its drug candidate OV101 Fast Track designation…
According to a story from aninews.in, mother Shashi Mishra and her daughter Anamika Mishra have staged a hunger strike in a desperate move to receive treatment for their muscular dystrophy.…
According to a story from engadget.com, the tech company AliveCor, known for its KardiaBand device for Apple Watch, is currently developing new capabilities for its innovative watch strap. Currently, the…
According to a story from sciencedaily.com, new and improved standards of treatment are allowing patients with Duchenne muscular dystrophy to have longer lifespans than in the past. By all accounts,…
According to a story from the Herald Sun, Matilda Mahon, an eighteen month old girl from Australia, will need to travel to the United States in order to receive treatment…
According to a story from Xconomy National, some patient advocacy organizations are beginning to speak out about exorbitantly high drug prices despite the fact that many of them receive funding…
According to a story from The European Society For Medical Oncology, a recent study shows that young adults and teenagers are less likely to adhere to follow-up guidelines following treatment…
According to a story from guttmacher.org, the U.S. Department of Health and Human Services proposed a host of new regulations purported to enforce over 20 federal provisions related to "conscience…
According to a story from PR Newswire, the pharmaceutical companies Sanofi and and Regeneron Pharmaceuticals are implementing a plan to make Praluent injections more accessible and affordable for patients with…
According to a story from news-medical.net, researchers from The Scripps Research Institute have successfully outlined a new path for the treatment of Charcot-Marie-Tooth disease subtype 2D (CMT2D). The scientists hope…
According to a story from pharmpro.com, the pharmaceutical company Abeona Therapeutics announced that it has been given Rare Pediatric Disease Designation for its ABO-202 program by the U.S. Food and…
According to a story from Financial Buzz, the pharmaceutical company Proteostasis Therapeutics recently announced that the company's experimental treatment PTI-428 was granted Orphan Drug Designation by the FDA. PTI-428 is…
According to a story from pm360online.com, some recent studies from Scandinavia are serving to highlight the lack of advances in treatment for psoriatic arthritis. While other types of arthritis have…
According to a story from the Clarion Ledger, surgeons at the University of Mississippi Medical Center are now trained to conduct a minimally invasive procedure to relieve the symptoms of…
According to a story from pharmavoice.com, the pharmaceutical company Cadent Therapeutics has announced the beginning of the Phase I clinical study for its drug candidate CAD-1883. The therapy is a…
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