According to a story from EParent, the pharmaceutical company Ultragenyx released a statement confirming that the company's product MEPSEVII had received approval for public use by the Food and Drug…
According to a story from CBC News, Jillian Lanthier's son Landen Alexa was diagnosed with a severe and rare form of juvenile idiopathic arthritis at six years old. Although he…
According to a story from Syosset Jericho Tribune, the charity basketball fundraiser called Hoops for Harrison is back again this year. The tournament was named after Harrison Gillman, who now…
According to a story from ANCA Vasculitis News, The European Medicines Agency just approved the pharmaceutical company ChemoCentryx's application for the marketing of avacopan as a potential treatment for anti-neutrophil…
At only six years old, Simeon Augustus Peterson, also referred to as "Mr. Pete," was diagnosed with Hansen's disease. From then on, he lived the rest of his life cut…
According to a story at medpagetoday.com, a recent study showed that stem cell transplant could be a viable new method for treating scleroderma, and could be more effective than previous…
According to an article from Financial Buzz, the pharmaceutical company CymaBay Therapeutics has announced that the first of its patients have begun to enroll in a long term seladelpar clinical…
New research is helping experts understand the underlying causes of idiopathic pulmonary fibrosis on the molecular scale. When solving any problem, disease included, it is best to start by understanding…
According to a story from the National Hemophilia Foundation, the Swedish pharmaceutical company Orphan Biovitrum announced that its first patient was registered for a new phase 4 clinical trial. The…
Margarita Matias could not believe her eyes when she walked into the newly renovated bathroom. Her old bathroom was far from ideal, and often leaked. The new arrangement is optimized…
According to a recent article from indiatoday, a new study has revealed information about how osteosarcoma and other cancer cells manage to survive in the body. The new research suggests…
According to an article from businesswire.com, the pharmaceutical company Odonate Therapeutics announced the beginning of CONTESSA, a phase three study of the treatment tesetaxel and its function in patients with…
At three months old, Emily's mouth hurt. Her first tooth started coming in. Her parents immediately knew that something was wrong. Three months later, the family received dire news about…
According to a story from philly.com, many people with severe forms of brain cancer are not receiving sufficient hospice treatment, according to a recent assessment. The study took data from…
According to a story from financialbuzz.com, the pharmaceutical company AveXis, Inc., is planning to begin preparations to submit a Biologics License Application (BLA) to the Food and Drug Administration for…
According to a story from the Chicago Tribune, Ben Barres, a widely renowned neurobiologist and researcher, passed away at age sixty-three after fighting pancreatic cancer. Mr. Barres was credited with…
According to a story from prnewswire.com, the experimental treatment SPR001 was just granted orphan drug status by the Food and Drug Administration (FDA). The new treatment is currently being developed…
A recent study has revealed a possible mechanism for the repair of nerves damaged by multiple sclerosis. Research at the University of California has found that gene expression in certain…
Organovo Holdings recently stated that its 3D bioprinted therapeutic liver tissue was granted orphan drug status by the Food and Drug Administration (FDA). Taylor Crouch, the company CEO, was excited…
Poor mental focus may be a contributing to the paralysis that commonly occurs after a stroke, according to a new study. A person who has had a stroke, when the…
Baseball pitcher Tyson Ross recently signed to a Minor League contract with the San Diego Padres. In the past, Ross pitched for the Padres from 2013-2016. Now thirty years old,…
Batu Biologics just raised $1.3 million in order to continue funding the development of ValloVax, an immunotherapy treatment for cancer tumors. The crowdfunding project was started in May 2017. Initially,…
The Cystinosis Research Network (CRN) is offering scholarships to prospective college students who have been impacted by the condition. The organization offers two different scholarships, one for a student that…
The pharmaceutical company Protalix Biotherapeutics, Inc. announced that a drug currently in development called PRX-102 has been granted orphan drug status by the European Commission. The treatment is being developed…
DelMar Pharmaceuticals announced that its flagship cancer treatment drug, called VAL-083, was given "Fast Track" status by the Food and Drug Administration. VAL-083 is a possible treatment for a type…
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