Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
Iowa University researchers at its Children’s Hospital led the effort that found a new target. According to the Iowa Carver College of Medicine, to date, efforts by researchers focused on…
A rare and life-threatening kidney disease affecting young adults and children finally has an effective and approved therapy due to the pioneering and leadership of researchers at the Iowa University’s…
A team of doctors at NYU Langone transplanted a pig kidney into a brain-dead patient and reversed its rejection twice during the 61-day study. Currently, estimates of the number of…
There may be several reasons that HCC cancer of the liver cannot be removed. It may be due to the size of the tumor, or location proximity to major blood…
Breaking a system into small independent and interchangeable modules that can perform certain functions is called modularity. For many years the KRAS oncogene proved to be a classic example of…
Light chain amyloidosis (AL) is a progressive and rare disease whereby abnormal plasma cells found in the blood and urine over-produce light chain proteins. These proteins misfold into amyloid fibrils…
The findings were recently published in Nature Immunology and reported by Precision Medicine suggesting that a factor called Interferon Regulatory Factor 4 (IRF4) takes responsibility as a driver of transplant…
A gene-editing protein, small enough to fit into adeno-associated viruses (AAVs) that infect humans has been identified. As reported by Precision Medicine, these compact AAVs can be modified so that…
The developer of the Promega OncoMate MSI Dx Analysis System recently announced the FDA’s approval of the system identifying patients who may benefit from the combination of Lenvatinib (Lenvima) and…
Please go HERE to read Part 1 of this article The company, GEMMABIO, will pursue a number of rare, large indications. A new spinout, RareTx, will be dedicated to Orphan…
Professor Zdeněk Sofer of the University of Prague and his team developed and validated a "Lab-on-a-Scalpel" concept which is a surgical tool incorporating an integrated diagnostic sensor. Their findings were…
As noted in a recent article published in Inside Precision Medicine, in 1992 gene therapy was often discussed but seldom practiced. When Jim Wilson MD, PhD attended Penn State, gene…
Xspray Pharma, the developer of the drug dasatinib, was recently issued a Complete Response Letter (CRL) by the FDA while waiting for corrective actions, according to Cancer Network. Based on…
According to a press release from Syndax Pharmaceuticals, the developer of Revumenib, the drug met its primary endpoint resulting in complete remission (CR) or CR with partial recovery. Relapsed or…
A recently published study in The Lancet reports that over 54,600 children living in Gaza are severely malnourished. In addition, as of August 2025, there are few therapeutic options available…
Over 9,300 individuals living in the United States are currently waiting for a liver transplant. There is a serious need for liver donors. This message was recently sent out by…
Immuneering’s midstage pancreatic deep cyclic MEK protein inhibitor, (DCI), almost doubled the standard overall survival. It is a deep cycle inhibitor that targets key pathways in a pulsed manner. Results…
A recent study by UCLA researchers of in-home murders of children twelve and under revealed that according to the National Violent Death Reporting System and other agencies, nearly one quarter…
Medetoidine is an animal sedative increasingly being found in human opioid deaths according to published reports in the journal “The Conversation” and shared on MedicalXpress. Synthetic opioids claim thousands of lives…
In a recent study, deficiency in Vitamin D was associated with an elevated risk of developing Alzheimer’s disease. Yet there were no indications that it is the direct cause of…
After the death of six patients, the FDA has announced that it will require earlier and more frequent monitoring of the monoclonal antibody Leqembi, the brand name for the Alzheimer’s…
Researchers at UC Berkeley, DTU, and OptoCeutics in Denmark have created a non-medical light-based technology that improved cognitive function for Alzheimer’s patients who have participated in previous clinical trials. The…
A new study recently published in the European journal of Preventive Cardiology and reported by Medical News Today, noted that individuals who added extra steps plus reasonable speed to their…
Studies by highly accredited Mayo Clinic and Barrow Neurological researchers report finding an association between living in close proximity to a golf course and an increased risk of Parkinson’s disease…
Shebli Atrash, MD, Levine Cancer Institute medical oncologist and associate professor of medicine at the University of Wake Forest interviewed with Medical Express following his presentation at the 2025 Conference in…
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