Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
A recent study by Texas A&M researchers evaluated the results to male offspring of parental alcohol exposure. The exposure to the chemical diethylnitrosamine was found to be disruptive to mitochondrial,…
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Researchers Urge Awareness About the Risk to Children of Parental Alcohol
Due to the efforts of public health officials in the 1940s, Murine typhus was almost eradicated in the United States. However, there now appears to be a resurgence in the…
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The CDC Cautions that a Flea-Borne Disease Is on the Rise in California and Texas
Malaria remains responsible for 50,000 deaths annually. An ever-expanding population coupled with malaria gaining resistance to treatments are prominent roadblocks. As reported in Science Alert, the plan is radical. The…
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Its ‘Game Over’ When Mosquitos Siphon Human Blood Laced with a Poisonous Drug
Prader-Willi syndrome is a leading cause of obesity in children. The rare disease was discovered over seventy years ago, yet this is the first therapy to be approved by the…
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Soleno Therapeutics Receives FDA Approval for Prader-Willi Syndrome
National Cancer Center researchers have discovered a mechanism for liver regeneration in animal models triggered almost immediately after episodes of severe liver damage. The study, reported in MedicalXpress, explains that…
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Scientists Discover Mechanism for Liver Regeneration
Professor Sophia Padilla, lead author of a new study on antibiotic resistance describes the cycle in an article published in UC Irvine’s American Chemical Society Journal. Scientists develop drugs to…
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Scientists are in a Race to End the Antibiotic Resistance Cycle
Scientists have earnestly delved into a new study to test a drug for individuals who have genetically inherited a type of early-onset Alzheimer’s disease known as “dominantly inherited Alzheimer’s disease”.…
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Alzheimer’s: A Well-Earned Glimmer of Hope
One Million People: That is an estimate of the number of individuals who die from infections that resist drugs such as antibiotics according to a report in BBC News. Yet,…
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Scientists Have Discovered a Goldmine of Potential Antibiotics in the Immune System
Inflammatory bowel disease (IBD) affects approximately 1.6 million people in the U.S. According to a report in Healio, this equates to about 1.3% of the adult population. IBD can be…
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Inflammatory bowel disease (IBD) affects approximately 1.3% of the U.S. adult population
Sixty-six-year-old Tim Andrews, a resident of New Hampshire, is the fourth patient worldwide to undergo a pig kidney transplantation. As reported recently in a Mass General News Release, Tim is…
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The Second Successful Genetically Edited Pig Transplant Performed by Harvard Surgeons at Mass General
As reported in a recent edition of the Harvard Gazette, AI is commonly used to analyze X-rays and scans. AI has begun to outperform physicians in prognostic and diagnostic assessments.…
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Should AI Make Diagnostic and Prognostic Assessments for End-of-Life Decisions?
In June 2023 Jenny Decker took time out from her job as a trauma nurse and sailed out of Kona, Hawaii, beginning her solo voyage around the globe. Jenny’s mission…
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Nurse JENNY DECKER is Sailing Around the Globe to Raise Awareness for Charcot-Marie-Tooth Disease – UPDATE
This article is written by Enrico Orzes and originally published on Osservatorio Malattie Rare (OMaR). It has been translated from Italian. Patient Worthy is grateful to the team at OMaR…
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The story of Laura and Martina and a rare disease called GACI with two very different outcomes.
Mesoblast Biotechnology Company has received FDA approval for its Ryoncil therapy as the first of its kind to be approved in the United States. The therapy has been developed to…
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FDA Approves the first Mesenchymal Stromal Cell Therapy to Treat the Graft Versus Host Disease in Adults and Children
Sickle Cell, an inherited disease, involves crescent shaped red blood cells that are the “vehicles” containing hemoglobin, a protein responsible for carrying oxygen throughout the body. For almost a year…
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Sickle Cell Disease: Two Drugs are An Arm’s Length from a Potential Cure
Roche has been developing an experimental drug for Parkinson’s disease for over ten years. According to BioPharma Dive, the latest statements from the company are that the drug, prasinezumab, failed…
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Parkinson’s: Roche Will Continue Activity with Prasinezumab After Second Failure
According to the data that was presented at the 2024 ACR Convergence, a considerable number of patients are hospitalized when it could have been avoided. As reported in Healio News,…
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Rheumatoid Arthritis Patients Can Avoid Hospitalization by Seeking Early Treatment
Approximately one and one half million people are affected by ulcerative colitis (UC) worldwide. It is an inflammatory bowel disorder with, as of yet, no known cause. There are, however,…
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Ulcerative Colitis: Over One Million People are Waiting for Dosing to Begin in First-in Human Trial
The FDA’s recent approval of AbbVie’s new combination therapy provides patients with longer-lasting control of movements. As described recently in Biopharmadive, Parkinson’s disease is characterized by uncontrolled muscle movements or…
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Parkinson’s: Newly Approved Drug Gives Advanced-Stage Patients Longer Periods of Relief
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The use of the gene therapy elivaldogene autotemcel (Skysona), has been approved due to its success in the treatment of patients diagnosed with the neurological disease cerebral adrenoleukodystrophy (CALD). The…
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Gene Therapy Promising for Cerebral Adrenoleukodystrophy but Carries Risk of Blood Cancer
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According to a recent report in Healio News, the GLP-1 agonists are medications developed primarily to control blood sugar levels for type two diabetes. About the FLOW Clinical Trial The…
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The Newest Medications to Treat Chronic Kidney Disease in Type Two Diabetes
Spinal muscular atrophy (SMA) is a rare disease causing progressive muscular weakness. Severe forms of the disease can be fatal to infants. Apitegromab is an experimental therapy that was successful…
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Positive Trial Data is Welcomed News for Spinal Muscular Atrophy Patients
Healio Gastroenterology Source: Concomitant use of common medications does not significantly affect UC induction therapy
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Concomitant use of common medications does not significantly affect UC induction therapy
Healio Cardiology Source: Immune checkpoint inhibitors for advanced lung cancer linked to higher blood clot risk
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WHATNEXT: Immune checkpoint inhibitors for advanced lung cancer linked to higher blood clot risk
Eighty-five-year-old Frank Meuers considers his 500th immunoglobulin infusion to be a cause for celebration. Frank has logged details of his doctor’s visits since his first dose of replacement therapy with…
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It Took Almost 60 Years for the Correct Diagnosis and Treatment for Primary Immunodeficiency