Anna is from England and recently finished her undergraduate degree. She has an interest in medicine and enjoys writing. In her spare time she likes to cook, hike, and hang out with cats.
The political party the Scottish Liberal Democrats has voted in support of a motion about myalgic encephalomyelitis (ME). This motion calls for several changes, including stopping graded exercise therapy…
The United States Food and Drug Administration has awarded Fast Track Designation to an experimental gene therapy for the treatment of wet age-related macular degeneration. For more detailed information, you…
An international study led by researchers at the University of Alabama Birmingham has investigated the link between a specific genetic mutation underlying neurofibromatosis type 1, and the symptoms patients with…
Corbus Pharmaceuticals have announced that they will go ahead with a Phase 3 study investigating the drug lenabasum as a potential treatment for dermatomyositis. For more information, you can view…
A recently published study has highlighted the role of a sub-group of astrocytes (a type of brain cell) in brain inflammation, which can be a feature of multiple serious diseases,…
A bill (H.R. 6801) has been introduced that is designed to support the development of rare disease therapeutics. Known as the Rare Disease Fund Act, it was introduced by Congressmen…
A report recently published by the American Association for Cancer Research has highlighted the progress made in fighting cancer but emphasises that continued investment by the government in healthcare research…
The United States Food and Drug Administration has awarded Rare Paediatric Disease Designation to an experimental drug for the treatment of Stargardt disease. For more information, you can find the…
Bone Therapeutics, who are developing an allogeneic bone cell therapy as a treatment for delayed-union fractures of long bones, has announced the results of a Phase 1/11A study. They have…
Novartis has carried out a survey to find out what elements of a treatment are most important to patients with psoriasis. The survey found that patients value clear skin the…
The United States FDA has awarded Breakthrough Therapy Designation to a drug called LOXO-292 for the treatment of RET-altered non-small cell lung cancer and thyroid cancer, in patients who meet…
The United States Food and Drug Administration has granted Breakthrough Device Designation to a medical device that is designed to screen for hyperkalaemia (high blood potassium levels) without taking a…
The first US patient has been dosed with the drug MIN-102 as part of a clinical trial into its effects in patients with adrenomyeloneuropathy. For more information about this, you…
Top-line data from a Phase 3 study of an experimental method of visualising prostate cancer has been announced. While it met the primary endpoint for specificity, it did not meet…
Recent medical developments have led to new drugs designed to treat rare genetic disorders. However, the high cost of many of these drugs limits the number of patients who have…
The pop-punk singer Avril Lavigne has announced her return to music with a new album that she made while fighting chronic Lyme disease. In a letter to her fans, she…
A recent study published in the journal Cell has investigated the process behind the genetic condition Glut1 deficiency syndrome. Many genetic disorders are thought to be caused by genetic alterations that…
The National Organisation for Rare Disorders has announced the addition of ten new rare disease registries. For more detailed information about this news, you can view NORD’s source press release…
A recent study carried out by scientists from the University of Utah Health has highlighted the role of a protein called Staufen1 in spinocerebellar ataxia type 2 and amyotrophic lateral…
The United States Food and Drug Administration has granted an Investigational New Drug application for AP101. AP101 is a drug that is being researched as a potential treatment for epidermolysis…
The non-profit organisation CureDuchenne has announced that they have made a $500,000 investment in the company 4D Molecular Therapeutics in order to support the development of gene therapy research. For…
A study of an investigational drug called ZX008 in patients who have refractory Lennox-Gastaut syndrome has produced promising results, according to Zogenix. For more detailed information, you can view…
The speciality pharmaceutical company Advicenne has announced that the US FDA has cleared the Investigational New Drug (IND) application submitted on behalf of ADV7103. ADV7103 is an investigational treatment for…
The companies BeiGene Ltd. and SpringWorks Therapeutics have announced that they will collaborate to research the safety and preliminary efficacy of a combination of two drugs: BeiGene’s investigational drug lifirafenib…
The George Washington (GW) University School of Medicine and Health Sciences has announced that they and twelve other research centers are collaborating with the Scleroderma Research Foundation to launch the…
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