According to a story from Chemical & Engineering News, many drug research and development startups are beginning to turn to gene expression data in order to find new uses for…
A new study has found that 80 percent of people who have an identifiable genetic risk for cancer due to a mutated BRCA1/2 gene don’t know they're at risk. The…
Nightstar Therapeutics has released preliminary data from a Phase 1/2 study of an experimental gene therapy designed to treat X-linked retinitis pigmentosa. For more detailed information you can view the…
A study carried out by researchers from Harvard Medical School and Brigham and Women’s Hospital has explored the link between dopamine neurones, Parkinson’s disease, and psychiatric disorders. To read about…
According to a story from Medical Xpress, an international group of scientists from the US, France, and Spain may have discovered that an antifungal agent commonly used to treat skin…
The United States Food and Drug Administration has awarded Orphan Drug Designation to an experimental PLX cell therapy (called PLX-R18) as a treatment for graft failure and incomplete haematopoietic recovery…
According to a story from PR Newswire, the drug developer Protagonist Therapeutics recently announced that its investigational therapy PTG-300 has earned Fast Track designation from the US Food and Drug…
The United States Food and Drug Administration has awarded twelve research grants worth a total of over $18 million for research into rare diseases. For more information about this news,…
According to a story from BioSpace, the biotechnology company BioElectron recently announced that the results from its Phase 2a clinical trial of its experimental product EPI-589 are looking positive. EPI-589…
According to a story from UPI, gene editing technology could be a potential treatment for mitochondrial diseases, a rare, genetic illness that is usually fatal. In a proof-of-concept experiment, researchers…
According to a story from Angioedema News, an investigational product from BioCryst Pharmaceuticals called BCX7353 was able to quickly subdue swelling attacks in hereditary angioedema in clinical trials. In addition,…
Sangamo Therapeutics has shared details of their preliminary data from a clinical trial of the investigational drug SB-525 in patients with Haemophilia A. For more detailed information, you can read…
According to a story from statnews.com, the drug developer Sarepta has recently announced the its clinical trial testing an experimental gene therapy has resumed after the FDA lifted the hold.…
A study carried out by a research team at Yale University and mainly funded by the National Institutes of Health has identified a cell in the spinal fluid of patients…
According to a report by medicalexpress.com, researchers recently discovered a new genetic condition. Though researchers previously described the condition in animals, no human evidence had yet been found. Michigan State…
Researchers at the University of Pennsylvania have studied the genetics of a class of neurological disorders that includes Huntington’s disease and Fragile X Syndrome. They found that there were similarities…
According to a story from Business Wire, the biotechnology company Abivax recently released the results from its Phase 2a clinical trial. This trial was testing its investigational product ABX464 as…
According to a story from healthnewsdigest.com, teams of researchers from around the world have successfully revealed a new biomarker that can help predict treatment outcomes in ovarian cancer. The activity…
According to medicalexpress.com, the United States government recently approved the import of marijuana extracts from Canada. Though an uncommon occurrence, the US government approved the import for a clinical trial…
According to a story from Mother Jones, patients of black or Native American backgrounds are consistently underrepresented in clinical trials. This occurs even when the trials are for diseases that…
According to a story from EurekAlert! a cell culture platform developed by scientists associated with Hokkaido University will allow researchers to record and observe the natural behaviors of cancer cells.…
Scientists working in a lab have successfully managed to grow a miniature human esophagus (esophageal organoid). They hope that this could be used in the future to study conditions…
A new study explored the mechanisms underlying narcolepsy, a rare sleep disorder. The condition has previously been linked to reduced levels of a neurotransmitter called hypocretin, and the recent study…
According to a story from Research & Development, increasing collaboration between a variety of different organizations is helping to propel and improve the develop of new drugs for the treatment…
According to a story from cacm.acm.org, researchers have been slowly developing an AI software that can diagnose diseases simply by watching the way in which a person types on a…
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