The U.S. FDA just granted breakthrough therapy designation to a new mantle cell lymphoma treatment called acalabrutinib! This drug is specifically for people who have already gone through at least…
Pharma giant Novartis's new cancer drug tisagenlecleucel passed a critical test by winning the support of a federal advisory panel - setting it up for final FDA approval in September.…
Those who have received the diagnosis of trigeminal neuralgia can experience sudden pain in the jaw, cheeks, and forehead. This pain can last seconds to a few minutes. Some people with…
A report titled, “Association of Sarcoidosis With Increased Risk of VTE: A Population-Based Study, 1976 to 2013,” recently released information that patients with sarcoidosis have a 3-fold increased risk for…
For a while, researchers and scientists have known that the protein, TDP-43, is found in clumps in the brain cells of patients with amyotrophic lateral sclerosis (ALS). It has also…
Cancer has a pretty complicated history with statins, a class of drugs that are most commonly used to lower blood cholesterol levels. In the past, laboratory tests involving statins have…
CymaBay, Inc. recently announced positive provisional results from its low-dose Phase II seladelpar clinical trial for primary biliary cholangitis (PBC) patients. Once you get past the confusing part of that…
According to a recent study in Science Daily, scientists have found evidence that one treatment drug's effect on the cells for a specific condition could actually be applied to several…
Two lucky Lennox-Gastaut syndrome (LGS) researchers were awarded grants by the LGS Foundation last week on July 12. These two recipients are both doing fascinating work in LGS research and,…
Listen up, sun worshipers, there's yet another reason to slather on SPF 105. Researchers are now exploring the link between melanoma and Parkinson's Disease (PD). The root cause is not…
Great news for our friends in the the Gaucher community! The FDA and its counterpart across the pond, the European Medicines Agency (EMA), have outlined a new strategy to spur…
You heard that right, Starbucks lovers! According to two different studies - one from the US and one from Europe - drinking anywhere from one to three cups of coffee…
A recent Canadian study published in Seminars in Arthritis and Rheumatism announced findings that psoriatic arthritis disease activity showed trends of stabilizing and even improving during pregnancy. Psoriatic arthritis is…
Could crizanlizumab be the next treatment to prevent pain in those with sickle cell disease (SCD)? Is this the medicine you've been hoping for? Sickle cell disease (SCD) is an…
There's some new information available about Parkinson's disease, and researchers are really excited about it. Earlier this month, researchers found that visual system changes in recently diagnosed Parkinson's patients can…
A new study detailed in Nature, involving synthetically replicating certain cell activity has been hailed as a major breakthrough in developing therapies for many neurological disease – Parkinson’s chiefly among…
As reported in Nature (an international medical publication), research scientists have uncovered the atomic makeup of an important protein found in those with Alzheimer's Disease. This is being touted as a…
Has your healthcare provider ever talked to you about using an FDA-approved drug for an unapproved use (sometimes called an “off-label” use) to treat your disease or medical condition? It…
Have you ever tried to fit a square peg into a round hole? Short of taking a mallet to the peg, you’re not going to be successful in pushing it…
Nope, we're not joking! US SWAT teams (Special Weapons And Tactics, military weapons-equipped law enforcement teams) have been asked to step in to help with backlogged FDA applications to get experimental treatments designated as orphan…
Oh the joys of a 17-month-old toddler… I remember some of the typical behaviors of those days—the throwing heaving of everything and anything, the opening of the fridge a million…
3:15 a.m.? Are you kidding? Why am I awake and staring at a digital clock that says it’s 3:15 a.m.? Ever have a night like that? The more you get…
Allergan and Paratek Pharmaceuticals Inc. recently tested a drug called sarecycline for treatment of severe acne. The medicine is a tetracycline-derived antibiotic that is taken orally, and the best part…
Status epilepticus is a rare and sometimes fatal condition. About 60 percent of those with this super-refractory status epilepticus (SRSE) die, making it the most dangerous type of seizure. This…
According to the Salk Institute for Biological Studies, scientists have had a breakthrough in past efforts to develop a technique that can determine which proteins in a cell interact with…
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