Just because we are staying home to avoid COVID-19 doesn't mean the medical field has stopped! In fact, many doctors are more determined than ever to improve patient outcomes.…
Metformin is a popular drug used by type 2 diabetes patients. According to recent interviews conducted by reporters for Medical Xpress, a team of researchers conducted parallel rodent and…
A blood test that gives a more accurate diagnosis of Alzheimer’s disease was announced at the July 2020 International Conference of the Alzheimer’s Association. The Association estimates that approximately…
According to a story from GlobeNewswire, the biopharmaceutical company Ovid Therapeutics Inc. and Columbia University have recently entered a collaborative partnership that will be focused on developing gene-based treatments for…
According to a story from Charcot-Marie-Tooth News, an all new protocol first described in the journal Brain Sciences could mark a significant advance in Charcot-Marie-Tooth disease research. The protocol allows for the…
According to a story from Parkinson's News Today, a recent study may have discovered the origins of chronic pain and damage to the sensory nerves as found in some cases…
As reported in Parkinson's News Today; Daniel Vesely had a hunch. He had been using mannitol, an easy to access over-the-counter sweetener and supplement often used by people with diabetes,…
Metformin is a popular drug used by type 2 diabetes patients. According to recent interviews conducted by reporters for Medical Xpress, a team of researchers conducted parallel rodent and…
Dr. Lindsay Wilde, an oncologist at the Hematologic Malignancies Division of Jefferson University, recently contributed to an article in the Oncology Times outlining her research team’s new study and…
By Lauren Thayer from In The Cloud Copy Sickle cell disease (SCD) is group of inherited red blood cell disorders. In a typical, healthy red blood cell, the cell is…
By Caitlin Seida from In The Cloud Copy Researchers in Russia completed a study measuring certain biomarkers among those with alcohol use disorder (AUD) and depression. The study sought to…
Chronic pain affects about two-thirds of those with Parkinson's, making it the major non-motor symptom of the disease. A study published in Movements Disorders has found that anandamide and glucocerebroside…
Rare Pediatric Disease Designation has just been granted by the FDA for an investigative therapy for lymphatic malformations (LMs). This therapy is called TARA-002 and was developed by Protara Therapeutics.…
An investigative therapy for hemolytic disease of the fetus and newborn (HDFN) has just received the FDA's Rare Pediatric Disease and Orphan Drug Designations. This therapy is called nipocalimab and…
In a recent webinar hosted by the National Organization for Rare Disorders (NORD), a number of speakers discussed an up and coming project spearheaded by the organization: the Rare Disease…
Moebius Syndrome Moebius syndrome is a rare condition that causes an inability to move the eyes laterally and facial paralysis. A similar type of paralysis can also occur as a…
According to GlobeNewswire, BridgeBio Pharmaceuticals and the Ivy Brain Tumor Center have recently began their Phase 0/2 trial of infigratinib. This treatment is meant for those with recurrent glioblastoma that…
By Lauren Thayer from In The Cloud Copy Systemic mastocytosis (SM) is a complicated condition of the blood in which excessive numbers of mast cells (a type of white blood…
By Danielle Bradshaw from In The Cloud Copy In a six-month long early rheumatoid arthritis (RA) trial - which was called NORD-STAR - researchers reported at the European League Against…
Last month, according to an article in the Washington Post, the FDA allowed marketing of a video game as potentially beneficial to children who have been diagnosed with attention-deficit hyperactivity…
By Lauren Thayer from In The Cloud Copy Parkinson’s disease is a neurodegenerative disorder that is progressive, resulting in the patient having problems with movement. The symptoms of Parkinson’s disease…
By Danielle Bradshaw from In The Cloud Copy A research team has found a connection that ties disease-linked alpha-synuclein proteins and their tendency to loosely combine (or to aggregate) and…
A recent article in BioSpace reported that Blueprint Medicines Corp. has submitted a New Drug Application (NDA) to the FDA for the investigational drug pralsetinib with an action date…
According to data from the STOMP trial involving thirty-four patients, a triple regimen has been proven to induce durable responses in pretreated patients with relapsed/refractory multiple myeloma. A recent…
Chemotherapy-induced peripheral neuropathy, or CIPN, is a common side effect of chemotherapy. A recent study aimed to uncover whether or not oxaliplatin chemotherapy increased risk of CIPN for those with…
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
