According to a story from PR Newswire, a new program called The Lantern Project is working to provide a free testing program that allow doctors to more quickly diagnose patients…
According to a story from news-medical.net, Verastem, Inc., recently announced that its drug COPIKTRA (duvelisib) was recently added to the National Comprehensive Cancer Network's (NCCN) guidelines for the treatment of…
According to a story from PMLive, Leadiant Biosciences of Italy recently announced that its drug Revcovi has officially received approval from the US Food and Drug Administration. Revcovi was approved…
According to a story from Endpoints News, the Chief Science Officer for Spark Therapeutics is close to finishing up his first year with the company. His name is Federico Mingozzi,…
According to a story from Charcot-Marie-Tooth News, the continuously escalating cost of drugs in the United States is still plaguing rare disease patients and chronically ill people across the country.…
When it comes to rare diseases often one of the biggest hurdles is finding the right diagnosis. Tailoring treatment, and adjusting lifestyles can be difficult, but both are impossible if…
Getting access to medication can be a difficult and demanding process for patients. There are often a number of hoops to jump through, papers to sign, tests to go through…
According to a story from Disability Today, Gary Campbell was just 30 years old, but his severe multiple sclerosis made him feel like someone who was three times older. His…
According to a story from Xcomony, the tech startup Glympse Bio has been developing a sensor technology that it claims will allow doctors to detect a variety of diseases earlier…
According to a story from prnewswire.co.uk, the biopharmaceutical company PTC Therapeutics recently announced the release of initial data from the first drug registry for its product Translarna (ataluren). This registry…
According to a story from the Toronto Sun, the Canadian Agency for Drug and Technologies in Health (CADTH) recently announced that it would not be recommending the funding of the…
According to a report by biopharmadive.com, Pfizer announced they will be dropping support for an experimental Duchenne muscular dystrophy treatment. The company intends to see if the treatment may be…
According to a report by CTV News, a number of clinics across Canada are offering an unproven treatment. These treatments focus on expensive and unverified stem cell therapies. The treatments…
According to a story from marketscreener.com, the drug development startup Endocyte has recently reached $1.5 billion in total value. This biopharmaceutical company has been focused on developing therapies for two…
According to a story from The Atlantic, the continual development of gene editing technologies like CRISPR have the potential to cure a substantial portion of rare diseases that are linked…
According to a story from Scoop Independent News, speech therapists from the Waikato District in New Zealand have been using telehealth technology to great effect in order to deliver speech…
A study carried out by researchers from the University of North Carolina at Chapel Hill suggests that doctors in the state may not be testing patients for Ehrlichia infection often enough.…
According to a recent press release from Bluebird Bio, the European Medicines Agency has accepted and will review their marketing authorization application (MAA) for the investigational gene therapy LentiGlobin™ as…
A new drug designed to treat MAC lung disease as part of a combination antibacterial drug regimen in adults with limited treatment options has been granted Accelerated Approval by the…
The United States Food and Drug Administration has approved Copiktra™ (duvelisib). The drug is now approved as a treatment for adult patients diagnosed with refractory or relapsed chronic lymphocytic leukaemia…
The clinical research process is a thorough and time consuming method in which new drugs, therapies, and medical devices are rigorously tested before being made available to the public. Through…
According to a story from MedCity News, a recent study revealed a potential weakness of CAR-T cell immunotherapies that reveals the need for precision and caution in the extraction process.…
A past, current, and future problem – underrepresentation in clinical trials, particularly for rare diseases. Why does representation matter? Besides, you know, the basics of equality, drugs can react differently…
A Texas company, which opened in 2015, promised a new treatment for a number of conditions. Simply coming in and subscribing to a routine of IV treatments could treat cancer,…
According to a story from BioSpace, the biopharmaceutical company Orphazyme recently announced the results from its Phase 2/3 clinical trial of its investigational drug arimoclomol. This therapy is in development…
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