According to a story from PBS, the FDA has been approving new treatments at a noticeably faster rate than it has in the past. As a result, it appears that…
According to a story from EurekAlert!, researchers have found that the drug Diamox, which is used to treat a variety of illnesses and conditions such as altitude sickness, glaucoma, epilepsy,…
According to a story from bioportfolio.com, two companies, Ionis Pharmaceuticals, Inc., and its affiliate Akcea Pharmaceuticals, recently announced that its product inotersen (to be marketed as TEGSEDI) has gained approval…
According to a story from BioSpace, the biopharmaceutical company Acceleron Pharma, which develops TGF-beta based treatments for rare and serious illnesses, recently announced that the U.S. Food and Drug Administration…
According to Medical Xpress, gene therapy may become the next treatment option for those with chronic kidney disease, CKD. Researchers at Washington University School of Medicine in St. Louis have…
According to a story from the Deccan Chronicle, researchers may have discovered a new treatment for Dupuytren's contracture that could offer substantial benefits over currently available treatment options. The scientists…
According to a story from pm360online.com, a new study of Prader-Willi syndrome will soon be under way thanks to a recent collaboration between the biopharmaceutical company Zafgen and the Foundation…
According to a story from Psychology Today, a study from 2017 titled Cognitive behavioral therapy is effective in misophonia: An open trial concluded that cognitive behavioral therapy could play a significant role in…
According to BioPortfolio, the company UniQure has recently announced that the first hemophilia B patient has been enrolled in their Phase III study of the treatment AMT-061, which is an…
According to a story from sciencedaily.com, recent research has revealed the mechanism that causes hypokalemic periodic paralysis, a rare condition that causes patients to experience sudden, severe muscle weakness. The…
A researcher from the University of Alabama at Birmingham is working on how to improve treatment for patients with status epilepticus. The original article can be read here, at UAB…
According to PRNewswire, Beverly Hills, and Frankfurt based INFUSIO donated $5000 each of their patient’s Lyme disease treatment in May. Interest in the program was high. As a result, INFUSIO…
The experimental drug olinciguat (IW-1701) has been granted Orphan Drug Designation by the U.S. Food and Drug Administration (FDA) for the treatment of sickle cell disease. The full article can…
The Orphan Drug Designation awarded to the drug dovitinib for treating adenoid cystic carcinoma has been transferred from Novartis to Oncology Venture. The full article can be found here, at…
According to a June 29th report by Business Wire, ACADIA Pharmaceuticals Inc. received a new FDA approval for a form of Parkinson’s treatment. The approval specifically allows ACADIA to produce…
According to a story from the Vancouver Sun, the College of Physicians and Surgeons of B.C. recently issued new requirements in regards to the usage of opioids for treating patients…
According to a report from the University of Toledo, researchers developed a new molecule that could stop cancer in its tracks. The molecule, known as Sweet-P, works by targeting a…
What could make a family in Lebanon travel all the way to UCLA? The answer is a unique stem cell gene therapy designed to combat SCID. The El Kerdi family…
According to Business Wire, a pharmaceutical company, Aurinia Pharmaceuticals Inc., recently announced that they have enrolled the first lupus nephritis patients in the AURORA 2 extension study. Not only this, but Aurinia…
Mepsevii (vestronidase alfa) is a treatment for Mucopolysaccharidosis VII (MPS VII). The Committee for Medicinal Products for Human Use (CHMP) has given a positive recommendation for the marketing authorisation of…
A new treatment for schizophrenia has been approved by the US Food and Drug Administration (FDA). Aristada Initio (aripiprazole lauroxil) for the initiation of Aristada (aripiprazole lauroxil) is now expected…
According to a story from toweroncology.com, a recent study has revealed that a more aggressive chemotherapy could be significantly more effective for patients with pancreatic cancer after surgery in comparison…
According to a report by the Syndney Morning Herald, Australia may soon approve an in vitro fertilization technique known colloquially as the three-parent technique. This would allow families to greatly…
The US Food and Drug Administration (FDA) is reviewing a supplemental New Drug Application (sNDA) for the drug Imbruvica (ibrutinib) in combination with rituximab (Rituxan) for treating Waldenström macroglobulinemia. The…
According to a report by NBC news, despite seemingly endless advancements in cancer treatment, many experts agree that chemotherapy is still a powerful and valid tool. In fact, many see…
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