An article by the Evening Standard announces new research towards a cure for cases of genetic blindness. The doctors pursuing this research are able to develop specific parts of the…
The drug minocycline is a tetracycline antibiotic. Previous research using mouse models has indicated that it may have anti-inflammatory and antiapoptotic (prevents cell death) properties and may benefit some neurological…
According to Digital Health Age, a wearable eye technology may be revolutionary in the lives of those who have Locked-In Syndrome, which is often associated with ALS and other motor…
Two companies, Tolero Pharmaceuticals Inc. and AbbieVie, have agreed to collaborate to clinically research a potential combination therapy for relapsed or refractory acute myeloid leukaemia. The potential therapy is comprised…
The investigational drug AT132 has been awarded Regenerative Medicine Advanced Therapy designation for the treatment of X-linked Myotubular Myopathy by the United States FDA. You can read the source press…
Two studies have looked into the long-term effects of subthalamic deep brain stimulation as a treatment for Parkinson’s disease. For more detailed information on this topic, you can find the…
According to Newswise, new findings indicate that electrical stimulation of the spinal cord and brain may be effective in treating symptoms of a group of rare neurological movement disorders, neurodegenerative ataxias.…
August is Stevens-Johnson Syndrome (SJS) Awareness Month! In honor of the SJS community, Friday August 31st has been designated an awareness day. What is Stevens-Johnson Syndrome? SJS is a rare, serious…
Unknown origins of birth. Overcoming enormous personal obstacles at an early age. A mysterious medical diagnosis. Making a drastic new change in life. This could - and is! - a…
The speciality pharmaceutical company Tikomed has announced that the UK Medicines and Healthcare Products Regulatory Agency has granted the company permission to go ahead with a Phase 2 clinical study.…
I came into the hospital about four days ago at 6 am in extreme abdominal pain. I remember writhing on the emergency room bed and breathing so frantically that my…
According to a story from BioSpace, the US Food and Drug Administration (FDA) recently approved the drug Oxervate (cenegermin). This treatment is the first FDA approved therapy for the rare…
According to a story from medicalxpress.com, a team of scientists at the University of Massachusetts Medical School have successfully developed a strategy for editing genes that could be used to…
According to a press release from Eisai Inc. and Merck (also known as MSD), Lenvima®(lenvatinib) has been approved by the United States FDA as a first-line treatment for patients…
A team of researchers led by Constantinos Koshiaris from the University of Oxford have recently published a study that investigated the best way to identify multiple myeloma through blood tests.…
Living with PKD has been a constant struggle for me but for you to better understand my story, I’m going to start from the beginning when I was first diagnosed.…
According to a story from mirror.co.uk, Vanessa Riddle, who had the rare cancer neuroblastoma, recently died after defying her cancer for almost a decade. She passed on June 1st, with…
According to a story from abc.net.au, a team of Australian scientists have developed a technique for delivering radiation therapy that could enhance both the potency and safety of treatment. This…
According to a story from the St. Helens Star, Amanda Sackville-Wiggins was diagnosed with hepatocellular carcinoma, a rare type of liver cancer, just after her 21st birthday. The cancer was…
According to a story from BioPortfolio, the U.S. Food and Drug Administration (FDA) has recently approved a new combination therapy for the treating small lymphocytic lymphoma and chronic lymphocytic leukemia…
According to a story from the San Francisco Chronicle, Isabel Bueso's parents were told when she was born that she would not live more than seven years. However, she continued…
Senator John McCain passed away on Saturday, August 25th after his year-long battle with glioblastoma, a rare form of brain cancer. He was four days short of his 82nd birthday.…
Happy Back 2 School Time! As the week comes to a close, we want to spotlight four articles. We have an honest piece from PW contributors Denise Crompton and Tom…
According to a story from Tablet Magazine, Emily Kramer-Golinkoff is a 33 year old woman who is living with cystic fibrosis, a rare disorder that primarily affects the lungs. Emily…
According to a story from sciencemag.org, Huntington's disease can often feel like a curse. That's how it felt for Michelle Dardengo as she watched the disease consume her father. At…
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