According to a story from BioSpace, Martin Pharmaceuticals' Livantra appears to be on something of a roll. Earlier in the year, the drug received Orphan Drug designation for the treating…
According to a story from kentlive.news, Lucy Frost of Tumbridge Wells is doing everything she can in an attempt to get the NHS to provide her son with the medication he…
The United States FDA has awarded Fast Track Designation to the investigational drug AVB-S6-500 for the potential treatment of platinum-resistant recurrent ovarian cancer. You can find out more detailed information…
Just this morning, the family of American hero and political icon John McCain announced via a statement he will cease treatment for the aggressive and rare form of brain cancer,…
No one likes to be judged. However, during the many years that I've been involved with rare diseases families, I've learned that some people are very quick to judge parents…
According to a story from Nevada Public Radio, in the early 1980s, Lisa Iezzoni was a medical student at Harvard University. Around that time she received a diagnosis of multiple…
According to a story from healthnewsdigest.com, an important source of data related to brain cancer has just become widely available to global researchers. This dataset was supported by Georgetown University,…
If you suffer with anxiety, you know just how crippling it can be. Anxiety* is actually a natural response to our environment that is designed to protect us from danger.…
According to a story from Newsweek, when 25 year old Rebecca Griffiths first knew that her son Reggie, now aged two, was diagnosed with Sanfilippo syndrome, she had to face…
According to a story from thesun.co.uk, Jade Baldwin, 35 had been dealing with mysterious itchiness for years before she sought medical attention for it. While her legs were itchy, there…
According to a story from Newswise, a team of scientists from the St. Jude's Children's Research Hospital have been hard a work conducting an in-depth analysis of a pediatric solid…
According to a story from Financial Buzz, the drug development company Eisai and Merck recently announced that their cancer drug lenvatinib, marketed as LENVIMA,® has gained marketing approval from the…
According to a story from hemophilia.org, the drug developer uniQure recently announced that the first patient had been dosed in the company's Phase IIb clinical trial. This trial is testing…
According to Science Blog, a therapeutics company is on its way to creating an implantable, insulin-producing device that may give injections a run for their money. Therapies similar to…
According to a story from the Newham Recorder, a three year old girl named Isla Caton's neuroblastoma has relapsed for the second time. Despite the bad news, her mother Nicola…
According to a story reported by The New York Times, on Christmas Day, a physician and mom of two became too weak and fatigued to do much of anything. Her…
This article contains a summary of the first episode of Afflicted A new series on Netflix called Afflicted explores chronic illness. It follows seven people as they talk about their…
According to a report by Newswise, a new form of gene therapy has been developed which may slow or prevent retinitis pigmentosa. Researchers funded by the National Eye Institute (NEI)…
Melody Alsaker is a researcher at Gonzaga with a passion for math. Not just any math though. The numbers and concepts Alsaker works with could be the kind that develops…
According to the Tampa Bay Times, Aaron McQ did not want to die. He knew, however, with his disease he would inevitably have to. The 50-year-old man from Seattle…
According to a report by Scicasts, a research team in Copenhagen recently discovered a new method for detecting cancer. The new method has the ability to detect a diverse set…
According to UWHealth, the researchers at UW Carbone Cancer Center look behind the five-year survival rate for cancer and instead consult what they call their "core facility--Cancer Prevention and…
According to The Times of Israel, a group of researchers believe they have found the origin of what could lead to a treatment for amyotrophic lateral sclerosis. Given the debilitating effect…
Several organisations are collaborating to develop a gene therapy that targets cystic fibrosis. Boehringer Ingelheim, Imperial Innovations, Oxford BioMedica, and the UK Cystic Fibrosis Gene Therapy Consortium will work…
The healthcare technology company RDMD was founded by Onno Faber, who has himself been diagnosed with a rare disorder. RDMD, which describes itself as “dedicated to accelerating research” with…
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