Over 55,000 people are diagnosed with pancreatic cancer every year. And about 95 percent of people who are diagnosed with pancreatic cancer will lose their lives from it. Pancreatic…
The United States government has awarded a grant of over $4 million to fund research into genetic mitochondrial diseases. The three-year grant was given to the Children’s Hospital of Philadelphia…
According to a story from uk.news.yahoo.com, Sammy Basso is 22 years old, and for him, it is a miracle. That is because Sammy is living with the rare genetic disorder…
According to a story from Hematology Times, a recent phase 2 study found that a three-part combination treatment could be a valuable treatment option for patients with chronic lymphocytic leukemia.…
TMI Alert! Pooping, or lack thereof, deserves its own book. Constipation. Hemorrhoids. Ugh! Nothing helped. Over the counter remedies, enemas, plenty of fluids, a diet high in fiber. I tried…
A recent study, carried out by researchers from the National Cancer Institute (part of the NIH) and several other universities, outlines a potential new method of predicting whether immune checkpoint…
According to a story from Multiple Sclerosis News Today, a recent case report suggests that switching from the immunotherapy drug Gilenya to another immunotherapy called Lemtrada could cause a severe…
Despite my misfortune, I still live life to the fullest I can. At three years of age, I was diagnosed with a rare disease, which initially had little impact on…
Pfizer has released the primary results from the Phase 3 clinical trial of tafamidis, an investigational drug being researched as a potential treatment for transthyretin amyloid cardiomyopathy. For more…
According to a story from Newswise, the results of a phase 3 clinical trial suggest that the medication tafamidis could substantially reduce the risk of hospitalization or death for patients…
A report on newsmedical.net details a major grant awarded for the research of idiopathic pulmonary fibrosis (IPF). The grant totals $8.9 million, aiming to fund a program for several years.…
Scientists have discovered a link between the causes of rheumatoid arthritis and Huntington's disease through Epigenetics. Rheumatoid arthritis is an autoimmune disease that causes pain and swelling in the joints. …
September is Dystonia Awareness Month! Dystonia is a chronic movement disorder, existing in the same family as the more well-known Parkinson’s disease. Symptoms of dystonia are defined by involuntary muscle contractions which…
Happy Last Day of August! As we get ready for the autumn, we want to highlight four articles. We have an article about the Zebra Ball fundraising for EDS advocacy,…
Happy Last Day of August! As we get ready for the autumn, we want to highlight four articles. We have an article about the Zebra Ball fundraising for EDS advocacy,…
According to a story from journals.lww.com, a recent study investigates the beneficial impact of a thymectomy operation for patients with myasthenia gravis. This procedure has been a common approach for…
According to a story from BioSpace, the gene therapy company Reflection Biotechnologies Ltd. recently announced that the US Food and Drug Administration (FDA) has given Orphan Drug designation to its…
The Australian biopharmaceutical company Antisense Therapeutics has announced that the first patient has been dosed on a Phase 2 clinical trial of the investigational drug ATL1102, which is being developed…
According to a story from Medpage Today, a recent study found that the drug Avapro, which is commonly used to treat high blood pressure, could also slow down the dilation…
The United States Adopted Name Council, which selects simple, new, and informative generic drug names, has approved ‘Onvansertib’ as the generic name for PCM-075. PCM-075 is an investigational drug that…
According to CureToday.com, those who have been diagnosed with chronic lymphocytic leukemia, CLL, are now living longer than ever before. This feat can be attributed to the influx of…
Friday September 7th is World Duchenne Muscular Dystrophy Day! Duchenne muscular dystrophy (DMD) is one of nine forms of muscular dystrophy. Patients with DMD cannot make dystrophin in their muscles causing…
A research team, funded in part by grants from the NIH and the National Multiple Sclerosis Society, say that they have discovered a new subtype of multiple sclerosis. The…
Hello there! My name is Amy. My friends call me Miss Amy. I’m 42 years old and I have a 21-year-old son who also shares the same diagnosis as me.…
According to a story from hms.harvard.edu, a recent study is revealing new information about the connection between aging and neurodegenerative disorders, such as Parkinson's disease, dementia, and amyotrophic lateral sclerosis.…
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