First Patient with Alzheimer’s Dosed in Bryostatin-1 Clinical Trial
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First Patient with Alzheimer’s Dosed in Bryostatin-1 Clinical Trial

  Last week, clinical stage biopharmaceutical company Neurotrope announced that the first patient was dosed in a Phase 2 clinical trial to test the safety, efficacy, and tolerability of bryostatin-1…

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Phase 3 Study Results Bring Hope for Children with Primary Hyperoxaluria Type 1  
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Phase 3 Study Results Bring Hope for Children with Primary Hyperoxaluria Type 1  

  According to a recent article in BioSpace, young children and infants who have been diagnosed with primary hyperoxaluria type 1 (PH1) are often faced with the use of gastrostomy…

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The Glanzmann’s Research Foundation: Dedicated to Finding a Cure
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The Glanzmann’s Research Foundation: Dedicated to Finding a Cure

Patient Worthy has recently begun a partnership with the Glanzmann's Research Foundation, a nonprofit patient organization dedicated to spreading awareness about Glanzmann's thrombasthenia and finding a cure. We spoke with…

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Experimental WHIM Syndrome Treatment Gets FDA Fast Track Designation
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Experimental WHIM Syndrome Treatment Gets FDA Fast Track Designation

According to a story from GlobeNewswire, the biopharmaceutical company X4 Pharmaceuticals, Inc. has just announced that the US Food and Drug Administration (FDA) has granted its investigational product candidate mavorixafor…

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