Regeneron Pharmaceuticals recently announced that it is testing a medicine for the treatment and/or prevention of Covid-19. According to an article by CNN, the testing of its anti-SARS-CoV-2 antibody combination…
June 19th is recognized as World Sickle Cell Day. This day is set aside to help spread awareness about sickle cell disease and its variants among the general public and…
Parkinson's News Today recently published an article featuring a study in Italy showing the benefits of deep brain stimulation in patients with late-stage Parkinson’s disease. The history of the subthalamic…
According to a story from PR Newswire, the US Food and Drug Administration (FDA) has just approved a treatment for rare adult-onset Still's disease for the first time ever. The…
This year, thanks to COVID-19, the European Hematology Association (EHA) took their annual conference online - but that didn't prevent some intriguing new insights and ideas. In a press release,…
At this year's EULAR 2020 E-Congress, Dr. Suzanne Verstappen, MD, presented on how lifestyle changes could benefit patients with rheumatic and musculoskeletal diseases (RMDs). Her interest in the impact of…
According to a recent article in PubMed, immune checkpoint inhibitors (ICIs) are the most commonly used type of cancer immunotherapy. ICIs have brought about a substantial improvement in the prognosis…
According to a recent article in Fiercepharma, vaccines based on new technology are being developed by AstraZeneca, Moderna, and Johnson & Johnson. The trials will be funded and conducted by…
High dose-intensive chemotherapy regimens have been shown as effective for children with Burkitt lymphoma. However, the intensity often leads to discomfort, adverse reactions, and poor outcomes in adult patients, particularly…
According to an article in the Washington Post, a recent comment by a WHO official caused a furious debate and criticism of the organization. Maria Van Kerkhove, the head of…
According to a story from Renal & Neurology News, a recent study has found that rituximab is superior to azathioprine therapy in preventing symptoms relapse in patients living with ANCA…
by Danielle Bradshaw, In the Cloud Copy A common occurrence among children that have rapid-onset obesity with hypothalamic dysfunction, hypoventilation, and autonomic dysregulation or ROHHAD syndrome is that they’re also…
According to a story from Medpage Today, the US Food and Drug Administration has approved the drug lurbinectedin (marketed as Zepzelca), developed by Jazz Pharmaceuticals, as a treatment for metastatic…
By Lauren Thayer from In The Cloud Copy Latent autoimmune diabetes in adults or LADA is a slow progressing form of autoimmune diabetes. Similar to type 1 diabetes, also an…
Over 2018 and 2019, BioCryst Pharmaceuticals conducted two surveys to better understand the needs and expectations of hereditary angioedema (HAE) patients. Overall, they found that despite progress in HAE therapies,…
According to a story from Buzzfeed News, the results of a recent trial held in the UK may have finally revealed a medication that can have a major positive impact…
Recently, a team of Yale researchers wanted to understand how genetic mutations in patients with Rett syndrome resulted in neurological issues. Using a unique type of genetic testing, researchers were…
This week, UbiVac and Bristol Myers Squibb announced their clinical trial collaboration in a Biospace press release. The two companies, in a Phase 1b trial, look to study whether combining…
In the geographically small island nation of New Zealand, there are estimated to be as many as 300,000 people who live with various rare diseases or disorders. Unfortunately, like in…
According to the ASCO Post, researchers have discovered genomic characteristics of smoldering multiple myeloma that can tell one's risk of progression to multiple myeloma. Dr. Mark Bustoros and his team…
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Summer is approaching, and Lyme disease is coming with it. Ticks and wildlife are more active in the warmer months, leading to an increase in tick-spread diseases. But because we…
According to a story from BioPharma Dive, the drug company Sarepta Therapeutics is pushing forward with its plans to develop a gene therapy for limb-girdle muscular dystrophy (LGMD). The company…
Myositis Myositis is an autoimmune disease that leads to muscle damage. Patients live with chronic disability due to the symptoms of this rare condition. These include skin rashes, pain, weakness, fatigue,…
June 17th is recognized as World CDKL5 Awareness Day and the month of June is considered CDKL5 Awareness Month. First organized by the International Foundation for CDKL5 Research (IFCR), the…
It is crazy to think back to a few months ago and see how much has changed. In March, SARS-CoV-2, which you probably know as COVID-19, was declared a global…
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