The ongoing coronavirus/COVID-19 pandemic has caused widespread uncertainty across the globe, and a lot of us have questions about what to do or what to expect. The rare disease community…
Uncertain times may be the understatement of the year so far. When the news of COVID-19 (coronavirus) caught our attention, there were a lot of people frozen in disbelief and…
Según una historia de CureDuchenne, la compañía de biotecnología Dyne Therapeutics anunció recientemente que CureDuchenne Ventures ha realizado una inversión de capital que respaldará el desarrollo de todas las nuevas…
According to a news release, researchers have found that cysteinase, a compound designed to treat a rare kidney stone disease, may also be effective in treating patients with pancreatic cancer.…
April is Sjögren's Syndrome Awareness Month. This is held annually in an effort to spread awareness about this syndrome, and has been held since 1998. Unfortunately, this disease receives little…
As reported in CCAKids Blog, 2020's contagion has imposed a strange new set of rules and precautions for leaving the house. The latest CDC recommendation has told all of America…
"An apple a day keeps the doctor away." Growing up, this sing-song refrain stood as nothing more than a reminder from my parents to eat my fruits and veggies. But it…
According to CNBC, there is a shortage across the country of a very important medication: hydroxychloroquine. This is somewhat unsurprising. After all, the Trump administration has been vocal about the…
According to Business Insider, cases of COVID-19 and deaths attributed to it are rising rapidly. The pandemic was officially declared on March 10th, just about one month ago. At the…
Seneca Biopharma, Germantown, Md., issued a press release announcing its recent meeting with the FDA to discuss elements of a final design and protocol for a Phase 3 trial investigating…
According to a story from Porphyria News, Lucia Monaco, PhD, is the chair of the International Rare Diseases Research Consortium (IRDiRC). Despite the ongoing disruptions caused by the coronavirus/COVID-19 pandemic,…
According to a story from Spectrum News, the Andrews family has been dealing with a rare disease called Niemann-Pick disease type C for years. Parents Pam and Chris knew early…
According to an article in The Asahi Shimbun, Japanese scientists have developed a new vaccine to mitigate neuronal degeneration caused by Alzheimer's disease. The vaccine, delivered nasally, had promising results…
Hi everyone, We hope everyone's doing okay-- whatever that means for you right now. Today we have an article about how rationing systems during COVID-19 pandemic is affecting people who…
De acuerdo a una historia de Fierce Biotech, recientemente ha habido algunos avances impresionantes en el tratamiento de la fibrosis quística. El último hito fue desarrollar y aprobar el medicamento…
Ornithine transcarbamylase (OTC) deficiency is a disorder that can cause comas, seizures, and death, making it necessary for those affected to seek treatment. Arcturus Therapeutics aims to give those with…
According to a report by ABC News, Virtua Health, one of the largest healthcare providers in New Jersey, claimed to have a forty-year history of organ transplant completions. Nonetheless, a…
According to Parkinson's News Today, Dutch neurologist Bastiaan Bloem, MD, believes that the development of Parkinson's disease can be attributed to chemical exposure. About Parkinson's Disease Parkinson's disease is…
According to an article in Healio, the immunosuppressing drug voclosporin was found to be effective in stimulating renal responses in patients with lupus nephritis. About Lupus Nephritis Lupus nephritis…
According to Healio, a recent study has found that patients with ovaries who have asthma or chronic obstructive pulmonary disease (COPD) are at a higher risk of developing rheumatoid…
According to an article in Science Daily, Professor David Nicewicz and a team of researchers at the UNC Department of Chemistry, discovered a method of creating tracers used in…
As reported in Biospace, a new gene therapy has made notable progress towards curing x-linked retinitis pigmentosa, a disease responsible for sight loss in men. Until now, the disease irreversibly…
According to Oren Goldshtein, CEO of Vectorious Medical Technologies, remote patient monitoring is needed now more important than ever. Nobody knows how long the COVID-19 pandemic will last or…
The Health Medicine Network has shared that researchers found a potential early biomarker that could help track the development of non-alcoholic fatty liver disease. With up to 80% of…
A person with diabetes is not able to properly make or use insulin well. Advancements in science are now seriously looking at updating and perfecting ways to help people…
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