Perpetually Healing
Editor's Note: Patient Worthy is proud to share the following story from our friends at Elephants & Tea, originally written by Dillon Groover, a brain cancer survivor. To see the…
Continue Reading
Perpetually Healing
One Mom’s Fight to Change the Language Around Microvillus Inclusion Disease (MVID)
Editor's Note: Patient Worthy is honored to share this article from our friends at Rareative. To see the article in its original format, please click here. When Jen brought Callie…
Continue Reading
One Mom’s Fight to Change the Language Around Microvillus Inclusion Disease (MVID)
FDA Grants Priority Review to Imfinzi-Enfortumab Vedotin Regimen for Muscle-Invasive Bladder Cancer
As reported on PharmaBiz, the FDA has accepted AstraZeneca’s supplemental Biologics License Application for durvalumab plus neoadjuvant enfortumab vedotin in patients with muscle-invasive bladder cancer who cannot receive or have…
Continue Reading
FDA Grants Priority Review to Imfinzi-Enfortumab Vedotin Regimen for Muscle-Invasive Bladder Cancer
Selcodebart Shows Hematologic Activity in Myelofibrosis-Associated Anemia
As reported on ONC Live, early findings from the phase 1/2 RALLY-MF trial suggest selcodebart may improve hemoglobin levels and reduce dependence on red blood cell transfusions in patients with…
Continue Reading
Selcodebart Shows Hematologic Activity in Myelofibrosis-Associated Anemia
Dengue Fever: If Half the World Is at Risk, Why Has No One Prevented It?
Once concentrated largely in tropical and subtropical regions, dengue is posing an expanding public health challenge as climate conditions, urbanization and population movement increase the number of people at risk.…
Continue Reading
Dengue Fever: If Half the World Is at Risk, Why Has No One Prevented It?
Investigational Drug Could Help Against Diabetic Retinopathy
Diabetic retinopathy affects approximately 30% of adults with diabetes and stands as one of the leading causes of vision loss among working-age individuals worldwide. The condition damages the delicate blood…
Continue Reading
Investigational Drug Could Help Against Diabetic Retinopathy
Barb’s Fight Against Stage 4 Lymphoma
In June 2024, I went to the emergency room because the “flu” I’d been diagnosed with a week earlier had turned into abdominal pain that didn’t feel right. After a…
Continue Reading
Barb’s Fight Against Stage 4 Lymphoma
Rare Inherited EGFR Mutation Greatly Raises Lung Cancer Risk
People who inherit a rare change in the EGFR gene may be much more likely to develop lung cancer. Their risk is about 25 times higher than that of people…
Continue Reading
Rare Inherited EGFR Mutation Greatly Raises Lung Cancer Risk
Singapore Approves Wegovy for MASH With Moderate to Advanced Liver Fibrosis
Semaglutide 2.4 mg becomes Singapore’s first approved therapy for adults with noncirrhotic metabolic dysfunction-associated steatohepatitis and F2-F3 fibrosis. As reported on the Manila Times, Singapore’s Health Sciences Authority (HSA) has…
Continue Reading
Singapore Approves Wegovy for MASH With Moderate to Advanced Liver Fibrosis
Ebola – Lessons Learned
The Ebola Outbreak: DR Congo The Ebola outbreak in DR Congo was declared in May 2026. As reported by the BBC, it is now the second worst on record with…
Continue Reading
Ebola – Lessons Learned
Synapticure: A Nationwide Neurology Network Developed by Utilizing Telehealth
Patients in the United States wait an average of 34 to 50 days (roughly 1 to 1.5 months) for an initial neurology appointment, with wait times stretching up to 4…
Continue Reading
Synapticure: A Nationwide Neurology Network Developed by Utilizing Telehealth
FDA Expands Welireg Use in Kidney Cancer With Lenvima Combination
As reported on FiercePharma, Merck & Co.’s Welireg has secured an expanded FDA approval that moves the drug earlier in the treatment of advanced kidney cancer, adding a new option…
Continue Reading
FDA Expands Welireg Use in Kidney Cancer With Lenvima Combination
A Routine Colonoscopy at 44 Revealed Cancer – Now She’s Raising Awareness
I thought I wanted a second baby. My son was an adult, and despite having an adorable Frenchie, I was ready to take steps to get to the baby smell.…
Continue Reading
A Routine Colonoscopy at 44 Revealed Cancer – Now She’s Raising Awareness
Boundaries, Securities, and Safety: The Unexpected Challenges of Kevin’s PKU Advocacy
15 years ago I released my first PKU project. I never imagined the day would come when I would need to assert my boundaries this firmly. As I write this,…
Continue Reading
Boundaries, Securities, and Safety: The Unexpected Challenges of Kevin’s PKU Advocacy
Lung Health Starts Early and Needs Protecting Throughout Life
World Lung Day 2026 puts a spotlight on lung health across the life course Lung health begins early in life and needs to remain a priority throughout life, says the…
Continue Reading
Lung Health Starts Early and Needs Protecting Throughout Life
Organoid Advances Could Open New Paths for Spinal Cord and Peripheral Nerve Repair
As reported on News Medical, researchers are increasingly exploring laboratory-grown organoids as potential tools for repairing damage caused by spinal cord and peripheral nerve injuries. A review published in Engineering…
Continue Reading
Organoid Advances Could Open New Paths for Spinal Cord and Peripheral Nerve Repair
Novel Therapies and the FDA
Twenty-six Novel Therapies have been FDA-approved so far this year. Medical journals, including "The Lancet", see this as a difficult task. The Agency must maintain strict safety rules while simultaneously…
Continue Reading
Novel Therapies and the FDA
FDA Approves Lilly’s Once-Weekly Onswik Insulin for Adults With Type 2 Diabetes
As reported on PR Newswire, the U.S. Food and Drug Administration has approved Eli Lilly and Company’s Onswik (insulin efsitora alfa-gobe), introducing a once-weekly basal insulin option for adults living…
Continue Reading
FDA Approves Lilly’s Once-Weekly Onswik Insulin for Adults With Type 2 Diabetes
The Invisible Kingdom: Reimagining Chronic Illness
Chronic diseases perplex doctors, while leaving patients mysteriously ill Meghan O’Rourke, the author of the best-selling book Invisible Kingdom, recently released an excerpt from this compelling story to Elle Magazine.…
Continue Reading
The Invisible Kingdom: Reimagining Chronic Illness
Investigational Immunotherapy Improved Survival in Advanced Squamous NSCLC
As reported on MedPage Today, an experimental immunotherapy called gotistobart helped patients with advanced squamous non-small cell lung cancer (NSCLC) live longer than standard chemotherapy in the phase III PRESERVE-003…
Continue Reading
Investigational Immunotherapy Improved Survival in Advanced Squamous NSCLC
Sharing Our Stories Is a Gift, and It Costs Us Every Time
Editor's Note: Patient Worthy is honored to share this essay from Carrie Ostrea. I have been fortunate to share my rare disease daughter's story for seventeen years. I have shared…
Continue Reading
Sharing Our Stories Is a Gift, and It Costs Us Every Time
Nearly Seven Years Later: Why Are So Many Long COVID Patients Still Going Untreated?
A Q&A with Robert Groysman, MD, on why standard tests can miss long COVID—and how individualized care may help patients break the cycle When the first wave of COVID-19 patients…
Continue Reading
Nearly Seven Years Later: Why Are So Many Long COVID Patients Still Going Untreated?
Liquid Biopsy and Cancer
The Wall Street Journal opinion editors recently published an article a liquid biopsy test called Galleri, prior to an upcoming FDA review. Key Trial Results Driving the Enthusiasm The article…
Continue Reading
Liquid Biopsy and Cancer
The Willem Family’s Medical Challenges
For most of my life, I knew something was wrong with my body. I just never had a name for it. When I was around 18, I had what I…
Continue Reading
The Willem Family’s Medical Challenges
The Speak Foundation Lobbies in Washington: BridgeBio’s Development Hopeful
“For people living with a progressive rare disease, time is measured differently. Research and clinical trials can take years while patients continue to lose strength and function,” said Kathryn Bryant…
Continue Reading
The Speak Foundation Lobbies in Washington: BridgeBio’s Development Hopeful
- 1
- 2
- 3
- 4
- …
- 27
- Go to the next page
