As reported on Fierce Biotech, Silence Therapeutics reported positive phase 2 findings for divesiran, an investigational small interfering RNA (siRNA) treatment for polycythemia vera (PV), a rare blood cancer marked…
As reported on Drugs, Scholar Rock says the US Food and Drug Administration’s review of its biologics license application for apitegromab, an investigational treatment for spinal muscular atrophy (SMA), remains…
Last year, I came down with a severe autoimmune disorder. It came out of nowhere. And it was bad. I was hospitalized three times over the course of a few…
Editor's Note: We are honored to share this story from our friends at CURE SYNGAP. To see this article in its original format, please click here. Porter is one of Jansen’s…
It was 2013, I was 21 years old, studying abroad in Italy, living the semester every college student dreams about. Then I woke up one morning and my body was…
New research presented by Teva Pharmaceuticals at Psych Congress Elevate 2026, and reported on PharmaBiz, adds to the growing body of evidence supporting the use of Austedo (deutetrabenazine) and Austedo…
Living with dystonia, or any chronic condition, places the nervous system under continuous pressure and strain. When symptoms are unpredictable or uncomfortable, the brain learns to stay on high alert, anticipating…
New Treatment Strategy May Eliminate Need for Immediate Organ Removal As reported on Bioengineer, groundbreaking clinical investigation led by researchers at Mayo Clinic suggests that an innovative intravesical immunological agent…
Editor's Note: The following recipe was written and shared with us by our friend Julie, the Cancer Dietitian. I cannot tell you how many people express their amazement and surprise…
New Research Reveals Protective Link Between Routine Immunizations and Uveitis Prevention A comprehensive analysis of patient health records reported on Medscape has uncovered a promising connection: individuals who receive standard…
Editor's Note: The following patient story was submitted to us by Daniel S.—an animal lover, sports fan, and former IIH patient. When you think about shunts, where do you imagine…
As reported on MedScape, gradually extending the interval between belimumab doses may allow carefully selected patients with systemic lupus erythematosus (SLE) in long-term remission to reduce treatment exposure (and in…
As reported on PR Newswire, the US Food and Drug Administration has granted Breakthrough Therapy designation to Kowa’s investigational therapy K-808 (pemafibrate) for primary biliary cholangitis (PBC), the company announced.…
As reported on The ASCO Post, perioperative treatment with enfortumab vedotin-ejfv plus pembrolizumab resulted in superior event-free survival, overall survival, and pathologic response rates compared with neoadjuvant cisplatin/gemcitabine in cisplatin-eligible…
As reported by the BBC, the Ebola outbreak in DR Congo was declared in May 2026 and is now the second worst on record with officials estimating that the death…
Editor's Note: The following article was originally written by Dr. Linda Bluestein. Linda Bluestein, MD, is a board-certified anesthesiologist and internationally recognized expert in hypermobility disorders, integrative pain medicine, and…
As reported on Gizmodo, Samsung has announced that its Galaxy Ring will soon support an FDA-cleared sleep apnea risk detection feature, making it the first smart ring to offer a…
Editor's Note: The following patient story was submitted to us by Christoph Muth, a 52-year-old German man currently residing in Thailand. I am living with a very rare, highly complex,…
As reported by The Manila Times, Axsome Therapeutics has announced the initiation of its Phase 3 CLARITY clinical trial evaluating solriamfetol as a potential treatment for adults with major depressive…
According to a press release from Texas A &M, researchers are using artificial intelligence to narrow drug choices and make shared data easier to use. Tuberculosis drug discovery speeds up with new…
A team from Minnesota University has created a synthetic cell that includes lifeless chemicals and created a synthetic cell that will grow, reproduce, and even compete for food along with…
Editor's Note: Patient Worthy is honored to share this article from our friends at Elephants & Tea, originally written by Kiki Khan, a leukemia survivor. To see the article in…
Editor's Note: This post was written and submitted to us by Jon Scheinman, and originally shared on LinkedIn. To see the article in its original format, please click here. I…
As reported on Drugs, Eli Lilly has reported positive topline findings from two additional Phase 3 trials of retatrutide, its investigational triple hormone receptor agonist designed to target GIP, GLP-1,…
As reported on PharmaBiz, AstraZeneca has reached an important regulatory milestone in Europe after the European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) recommended approval of Trixeo…
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