One-time treatment provides a new option for pediatric patients with a rare, progressive genetic disorder As announced in a recent press release, the U.S. Food and Drug Administration has approved…
I want to share this to give some ideas I have found that help me move through difficult days with more steadiness and self compassion, especially when things are flaring…
As reported on Radiology Business, the American Society for Radiation Oncology (ASTRO) has released its inaugural clinical practice guideline dedicated to the use of radiation therapy in bladder cancer, highlighting…
As reported on Healio, the U.S. Food and Drug Administration has approved finerenone (Kerendia; Bayer) for adults with chronic kidney disease (CKD) associated with type 1 diabetes, marking the first…
To start, a few words about the immune system: The immune system is comprised of cells, molecules, and biochemicals, and works to maintain human health. It can be defined as…
Editor's Note: Patient Worthy is honored to share this article, originally written by Linda Chase of Able Hire. Accessible travel planning means building a trip around a traveler’s actual mobility,…
For new caregivers supporting a parent, partner, or relative at home, the days can turn into an unbroken string of decisions, vigilance, and worry. The caregiving challenges often arrive faster…
When I was 39 years old, my life changed in an instant. I was a father of two young children, my daughter was six and my son almost six months…
As reported on News-Medical, an experimental treatment for idiopathic pulmonary fibrosis (IPF), rentosertib, was associated with shifts toward younger biological age profiles across multiple protein-based aging measures in a phase…
As reported on PharmaBiz, the U.S. Food and Drug Administration has accepted Takeda’s New Drug Application for the investigational oral therapy zasocitinib (TAK-279) and assigned the filing Priority Review status…
My name is Terri, and I live in the small town of Searcy, Arkansas, where I’ve proudly connected with countless people and their families over the years, especially while working…
As reported on Fierce Biotech, the U.S. Food and Drug Administration (FDA) has launched a new pilot program designed to streamline the investigational new drug (IND) application process and reduce…
Editor's Note: This story was originally written and submitted to us by Anthony Clark. "Okay, Michael, hold the ball up to your ear, then throw it! Just like this: ear,…
The condition Dupuytren disease, also called Dupuytren contracture, is a chronic disorder of connective tissue in the palm. Tissue gradually becomes thickened and tight, forming cords that can pull one…
As reported on PharmaBiz, the US Food and Drug Administration (FDA) has authorized Acepodia to proceed with clinical testing of ACE723, an investigational antibody-drug conjugate (ADC) designed for patients with…
As reported on Fierce BioTech, a phase 3 study conducted by MediLink has delivered positive results for Roche-partnered antibody-drug conjugate (ADC) tambotatug pelitecan (tam-peli), also known as YL201, in patients…
What's the Good News? Researchers have successfully completed initial testing of an experimental Parkinson's medication called TT-P34. The early results are very encouraging and suggest the drug is safe, works…
The history of cystinosis is one of the most successful examples of rare disease research leading to meaningful treatments. In a recent interview with the European Medical Journal, William Gahl—a…
This is my son Nikolai. Nikolai was recently diagnosed with Mucopolysaccharidosis type 2, or "Hunter Syndrome." A rare genetic form of childhood dementia, it's caused by a mutation in the…
As reported on PharmaBiz, a combination of Imfinzi (durvalumab) and Imdelltra (tarlatamab) has delivered significant improvements in survival outcomes for patients with extensive-stage small cell lung cancer (ES-SCLC), according to…
At the age of 18, I was diagnosed with a rare swallowing disorder called Achalasia. At the time of this video, I had undergone several surgeries, procedures, and countless appointments,…
In honor of World Duchenne Awareness Day on September 7th, Mal Duffin has invited us to share this app designed for parents whose children are living with Duchenne Muscular Dystrophy. Mal's…
As reported on World Pharma News, the U.S. Food and Drug Administration has granted approval to daraxonrasib, an oral RAS-targeting therapy, for adults with metastatic pancreatic adenocarcinoma who have previously…
A novel investigational Ebola vaccine has shown encouraging safety and immunogenicity results in a first-in-human clinical trial, supporting further development of an alternative vaccination strategy against Ebola virus disease, as…
Editor's Note: Patient Worthy is honored to share this article, originally written by David St. Denis, President & Director at Anteris Technologies. Transcatheter aortic valve replacement (TAVR) was originally developed…
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