According to an article from Parkinson's News Today, a recent analysis testing transcranial magnetic stimulation demonstrated that the procedure was not effective in treating the depression that is a common…
According to a story from the Irish Mirror, eleven year old Cezy Fosca, who has a rare condition called Morquio syndrome, has lost access to the only drug available that…
According to a story from the Vancouver Sun, five rare disease drugs just received coverage in British Columbia. The funding comes from savings accumulated thanks to a recent agreement that…
According to a story from news-medical.net, a recent study that the reduced expression of miR-125a-5p results in an increase in the concentration of the protein TIMP-1. Prior research has associated…
According to an article from globenewswire.com, the pharmaceutical company Amicus Therapeutics announced that the Food and Drug Administration (FDA) has the company's New Drug Application for migalastat with filing for…
According to an article from news-medical.net, a group of researchers from the Telomere and Telomerase Group at the Spanish National Cancer Research Centre have been able to pin down the…
According to an article from Newswise, another recent study is providing further support to the connection between severe gum disease and the development of certain types of cancer. Periodontitis is…
According to a story from biomedcentral.com, doctors have begun screening infants for tyrosinemia type 1. However, it is still unclear how accurate the screening process for this genetic disorder is.…
According to a story from Specialty Pharmacy Times, medical professions are starting to recognize the need for a new standardized treatment plan for pediatric rheumatic diseases. Pediatric diseases are illnesses…
Dangerous forms of brain cancer such as glioblastoma are almost impossible to treat. However, new research by Dr. Roel Verhaak could change that. Glioblastoma is the most aggressive form for…
According to a story from EurekAlert, a recent study published in the journal Pediatric Research reveals new protein biomarkers that researchers can use to evaluate how patients with progeria have reacted…
According to a story from biospace.com, a treatment developed by the pharmaceutical company Pfizer was given Breakthrough Therapy designation by the Food and Drug Administration (FDA). The drug is a…
According to an article from news-medical.net, researchers are beginning to delve into the causes of a rare lung disease called primary ciliary dyskinesia. This research is revealing previously unknown information…
The biotech company Myonexus Therapeutics may soon begin clinical trials for muscular dystrophy gene therapy treatment after obtaining nearly $2.5 million of investments. The research behind the new treatment was…
According to an announcement from ema.europa.eu, the European Medicines Agency (EMA) recently granted market authorization for a new treatment for alpha-mannosidosis. The new drug is an enzyme replacement therapy called…
According to an article from BBC News, Jackie Harrison had a daunting choice to make. There was a fifty percent chance that she would contract Huntington's disease, a rare condition…
According to a story from the National Hemophilia Foundation, the pharmaceutical company Novo Nordisk announced that its product REBINYN was now available for hemophilia B patients. The treatment is intended…
According to a story from CBS News, Hazel Hammersley was diagnosed with neuroblastoma at age two. As a result, she was forced to fight for her life at a very…
According to a story from Bronchiectasis News Today, the results of a new study suggests that bronchiectasis may trigger autoimmune inflammatory disease. The study found that the condition was frequently…
The Orphan Disease Center in association with the University of Pennsylvania and the Loulou Foundation just announced their 2018 Pilot Grant Program for CDKL5 Deficiency Disorder. CDKL5 deficiency disorder (CDD)…
According to a story from CTV Vancouver Island News, a charming young child known affectionately as 'bus boy' died in his sleep on Saturday, January 27th. Dominic Orr was only…
According to a story from Independent, cumbersome delays and possible funding cuts are severely hampering England's National Health Service (NHS). These delays are proving very costly for patients with long…
According to an article from Newswise, a team of researchers are studying tissue engineering for the repair of knee injuries such as a torn meniscus. The meniscus is the section…
According to a recent article from BioSpace, a study of Accuray's CyberKnife radiosurgical system showed good results with the new technology. The CyberKnife system projects radiation beams from multiple angles…
According to a story from Newswise, The University of Adelaide in Australia received a $1.19 million grant in order to spearhead an international research project. The project's aim is to…
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