Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
source: pixabay.com
According to a report in Myeloma Research News, the European Commission has recently granted authorization to market bortezomib, dexamethasone and thalidomide (collectively known as VTd) plus daratumumab to treat…
Continue Reading
Four Drug Combination to Treat Multiple Myeloma Performs Well in Trial
source: pixabay.com
The Halcyon machine holds an imaging mechanism that produces a high-quality CAT scan plus it houses a treatment unit that delivers radiation. According to a recent news release, approximately twenty-four…
Continue Reading
The Halycon Machine Could Mark a Major Improvement in Radiation Treatment
source: pixabay.com
A recent press release by the global biopharmaceutical research company, AbbVie, reported a positive opinion by CHMP granted to VENCLYXTO® combined with obinutuzumab to treat chronic lymphocytic leukemia (CLL). A positive opinion by…
Continue Reading
Venclyxto® Plus Obinutuzumab Offers Previously Untreated CLL Patients Chemotherapy-Free Treatment
The gleaming new Dutch headquarters of the European Medicines Agency (EMA), fronting Domenico Scarlattilaan in Amsterdam’s suburban Zuidas business district, finally opened for business last month — just over two…
Continue Reading
With Post-Brexit Move to Amsterdam Complete, EMA Renews Rare Disease Focus
source: pixabay.com
According to an article in the Alzheimer’s publication Being Patient, participants who had been enrolled in the discontinued phase three trials of aducanumab will start receiving the drug as…
Continue Reading
Biogen to Relaunch its Alzheimer’s Drug with FDA Clearance in New Study
source: pixabay.com
According to a January 2020 release by Business Wire, the USFDA has awarded accelerated approval of Epizyme’s TAZVERIK™ in the treatment of advanced epithelioid sarcoma (ES). The approval was…
Continue Reading
TAZVERIK™ Has Received FDA Accelerated Approval for Epithelioid Sarcoma
source: pixabay.com
Janssen R&D, a division of Johnson & Johnson (J&J), has partnered with the UK Biobank and others according to a recent news release by 3BL Media. It is noteworthy…
Continue Reading
ICYMI: Johnson & Johnson and the UK Government: Genomics For Disease Prevention
source: pixabay.com
Although ‘precision medicine’ has been mentioned in medical circles since 1999, according to a recent article in Pharmafile, technological advancements have now made it feasible. For years physicians have…
Continue Reading
Precision Medicine: Are We There Yet?
source: pixabay.com
Researchers at the Medical Center of Hackensack University conducted a study of three drugs now proven to be safe and effective for the treatment of severe seizures. According to…
Continue Reading
Three Drugs Proven Safe for the Treatment of Status Epilepticus
source: pixabay.com
According to a recent article in the MalayMail, it occurred to Abdullah’s doctor that the 67-year-old would be an inspiration for others who have kidney failure. His nephrologist, Dr.…
Continue Reading
This Glomerulonephritis Patient has Been Receiving Dialysis Treatment for Over 30 Years. Now he Shares his Discipline with Other Patients
source: pixabay.com
According to a recent article in MedPage Today’s 2019 year-end review, the number of life-threatening lung diseases in systemic juvenile idiopathic arthritis (sJIA) patients has been increasing. sJIA is…
Continue Reading
Searching for the Cause of Lung Disease in Systemic Juvenile Idiopathic Arthritis
source: pixabay.com
Genentech (Roche Group) announced positive results of its FIREFISH trial in a recent Business Wire news release. The second part of the study evaluated risdiplam’s efficacy on infants ages one…
Continue Reading
Risdiplam Delivers An Improvement to Infants with Spinal Muscular Atrophy Type 1
source: pixabay.com
It has been evident to scientists for years that Alzheimer’s disease, which affects about five million people in the U.S., is caused by an accumulation of two proteins within…
Continue Reading
A New University of Alabama Study Finds That Norepinephrine is the Missing Piece in the Alzheimer’s Puzzle
source: pixabay.com
According to a recent article in the UK Newcastle Chronicle, when doctors gave Leanne Buckley an opportunity to terminate both her pregnancies, Leanne and her husband Michael were emphatic…
Continue Reading
ICYMI: Newcastle Scientists Identify a Gene that Plays a role in Joubert Syndrome
source: pixabay.com
Surgery has been found to often be the best option towards a cure for a cancerous tumor (resectable) but there are many other tumors that are diagnosed as unresectable…
Continue Reading
FDA’s Acceptance of AYVAKIT’s New Drug Application Offers Hope to Metastatic GIST Patients
source: pixabay.com
According to a recent article in PsychCentral, a rare genetic disorder called 22q11.2 deletion syndrome (22q) is very often misdiagnosed. A study shows that social impairment is the most…
Continue Reading
22q11.2 Deletion Syndrome Often Misdiagnosed as Autism
The biopharmaceutical company Cellectar Biosciences recently announced that the FDA granted its lead phospholipid drug conjugate, CLR 131, Orphan Drug Designation(ODD) for treatment of lymphoplasmacytic lymphoma. ODD is granted by…
Continue Reading
FDA Grants Orphan Drug Designation to Cellectar’s CLR 131 for the Sixth Time
source: pixabay.com
The American Journal of Managed Care (AJMC) published excerpts from a presentation by Dr. Andrew Wei at the 61st American Society of Hematology (ASH) Annual Meeting. The article stated…
Continue Reading
Phase III Study for Acute Myeloid Leukemia Hailed as Landmark Trial
source: pixabay.com
According to a recent article in Pharma Tutor, researchers at NHGRI, a division of the National Institute of Health, identified the biological cause of a newly-discovered autoinflammatory disease they named…
Continue Reading
ICYMI: A New Year, a New Autoinflammatory Disease, and a Promising New Drug
source: pixabay.com
According to a recent article in Yahoo News, Johan’s mother’s seven-year-old brother died years ago of chronic granulomatous disease (CGD). The mother, Maren, was told that she also had…
Continue Reading
A Bone Marrow Transplant From His Six-Year-Old Brother Saved This CGD Patient’s Life
Ty Eschenbaum’s world of high school football and working on his family’s ranch and farm changed suddenly after his freshman year when he was diagnosed with leukemia. Ty, who…
Continue Reading
Leukemia Survivor Arranges Make-a-Wish Trip for a Young Caroli Disease Patient
source: pixabay.com
According to an article in BioSpace, the FDA recently approved the PARP inhibitor Lynparza that was developed by Merck and AstraZeneca to be used as maintenance therapy for pancreatic…
Continue Reading
2020 Brings Hope to Patients with Pancreatic Cancer Thanks to Newly Approved Lynparza
source: pixabay.com
Susan Winn’s family history of ovarian and breast cancer can be traced back to the 1860s. Susan’s adult daughters, Kathryn, Bridget and Maureen, were recently interviewed with CURE® (Cancer Updates Research…
Continue Reading
A Family With the Most Significant History of Breast and Ovarian Cancer in the US
source: pixabay.com
An article published earlier this year by Fierce Biotech outlines an approach that was developed by researchers at the Fred Hutchinson Cancer Research Center. Using CRISPR-Cas9’s gene-editing method the researchers were…
Continue Reading
New Approach Uses CRISPR-Cas9 to Boost Fetal Hemoglobin Production to Treat Blood Disorders
According to a recent article in Euronews, this year one hundred children who were diagnosed with spinal muscular atrophy (SMA) will receive Zolgensma, the world’s highest-priced drug, at no cost.…
Continue Reading
Parents React to Novartis’ International “Baby Lottery” for Zolgensma with Hope But Also With Outrage