FDA Accepts New Drug Application for Vascular Ehlers-Danlos Drug
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FDA Accepts New Drug Application for Vascular Ehlers-Danlos Drug

According to a story by MarketScreener, pharmaceutical company Acer Therapeutics Inc. has submitted a New Drug Application (NDA) for its vascular Ehlers-Danlos syndrome (vEDS) drug Edsivo. The NDA was granted…

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Fibrodysplasia Ossificans Progressiva Patient Files Lawsuit against County DDS
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Fibrodysplasia Ossificans Progressiva Patient Files Lawsuit against County DDS

According to an article originally from WCPO Cincinnati, a woman with fibrodysplasia ossificans progressiva is filing a lawsuit against officials of Ohio's Hamilton County. Jessica Scully, 57, alleges that the…

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Scientists Hopeful About Potential Sarcoidosis Treatment
For most people, sarcoidosis is not fatal, but beware of pulmonary hypertension

Scientists Hopeful About Potential Sarcoidosis Treatment

According to the Shillong Times, a study published in the New England Journal of Medicine has reported intriguing results when treating sarcoidosis with an already-approved rheumatoid arthritis medication. What is…

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Vybion Wins Orphan Drug Designation for Experimental Huntington’s Drug
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Vybion Wins Orphan Drug Designation for Experimental Huntington’s Drug

According to an article published on BioPortfolio, earlier this week, biotechnology company Vybion Incorporated secured orphan drug designation for its highly experimental Huntington's disease drug INT41. About Huntington's Disease Huntington's…

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X4 Pharmaceuticals Reports Positive Phase 2 Results for WHIM Syndrome Drug

According to an article published by Biospace, X4 Pharmaceuticals, based in Cambridge, Massachusetts, has recently announced successful phase two results in clinical trials for their experimental drug X4P-001. The drug…

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