According to a story from Cure Today, a recent study has found that identifying mutations in patients with myeloproliferative neoplasms may be the key in predicting outcomes, such as disease…
Patients as Partners When you're diagnosed with an illness such as metastatic breast cancer, pancreatic cancer, or another rare disease that has limited treatment options, it's very easy to lose…
New data has been released about the effects of lenabasum, an experimental drug, on patients with systemic sclerosis and dermatomyositis. Corbus, who are developing lenabasum, are planning to present the…
According to a story from Multiple Sclerosis News Today, Dr. Robert Fox and Dr. Robert Bermel, both of the Cleveland Clinic, recently spoke about new treatment improvements that are needed…
According to a story from pm360online.com, the specialty pharmaceutical company Santhera Pharmaceuticals has recently announced of its Phase Ib/IIa clinical trial that will test its experimental product POL6014. This therapy…
According to a story from Inside Philanthropy, a recent case study was conducted in order to determine the main sources of funding for rare disease research. This broad ranging study…
According to a story from globenewswire.com, Galapagos NV and Gilead Sciences, Inc., recently announced that two clinical trials which were recently published in The Lancet demonstrated that the experimental treatment filgotinib could…
According to a story from EurekAlert!, a Phase I trial is being developed that will test a unique, three part combination treatment for children with neuroblastoma, a rare form of…
According to a story from BioPortfolio, the biopharmaceutical company Deciphera Pharmaceuticals, Inc., recently announced the release of preliminary data from the company's Phase I clinical trial, which is still in…
According to a report by MedCityNews, gene therapies have been catching increasing interest. They’ve been popular in the news and hot talk among medical professionals, but it seems like the…
An ambitious project called the Human Cell Atlas is attempting to study all the cells in the human body – of which there are more than 37 trillion. Researchers hope…
According to a recent press release, patients living with ankylosing spondylitis may soon have another treatment option. The researchers studying the new treatment, known as ixekizumab, recently posted results from…
According to a story from crainsnewyork.com, the biotechnology company Gotham Therapeutics has received financing to the tune of $54 million so that it can begin developing drugs to treat rare…
According to a story from pm360online.com, the biopharmaceutical company Principia Biopharma recently announced that they had achieved $10 million in milestones that are related to the development of its experimental…
According to a story from Medical Xpress, a recent study involving over 400 children has revealed the distinct characteristics of the gut microbiome in ulcerative colitis. Ulcerative colitis is considered…
According to a story from BioSpace, EUSA Pharma and AVEO Oncology recently announced the release of updated interim results from the second Phase of a Phase Ib/2 clinical trial which…
If drugs were measured by the quantity of approvals, orphan drugs would make quite a splash. Measured in more financial terms, however, they make up a much smaller portion of…
According to a story from BioSpace, the pharmaceutical company Advicenne has been granted clearance from Health Canada's Office of Clinical Trial to extend its Phase III clinical trial, which is…
According to a recent press release by Anavex, the United States Food and Drug Administration has approved an investigational new drug application for a study of the drug Anavex®2-73 in…
According to a story from BioSpace, the biotechnology company Cellenkos, Inc., recently announced that the US Food and Drug Administration (FDA) has given the company the go ahead to begin…
According to a story from Ottawa Citizen, the Pan-Canadian Research Network on Lyme Disease recently received a boost of $4 million from the Canadian government and The Canadian Institutes of…
According to a story from businesses.com.au, a new blood test that is currently in clinical trials could more accurately determine which patients will need chemotherapy to cure their cancer after…
According to a story from markets.businessinsider.com, the drug development company Pharming Group N.V. recently announced results from a Phase II trial testing its medication RUCONEST. This drug was tested as…
Genomic testing is becoming increasingly common, but more work still needs to be done into understanding which gene variants are linked to health and disease. To address this, the National Institutes…
The companies Genentech and Roche are working together to carry out a program of studies involving patients with Huntington’s disease (the huntingtin-lowering trial ASO program). One is a natural history…
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