The United States Food and Drug Administration has awarded Fast Track Designation to the investigational drug miransertib (ARQ 092), which is being researched as a potential treatment for PIK3CA-related overgrowth…
According to a story from pm360online.com, the biopharmaceutical company Insmed Incorporated recently announced that the data from its Phase 3 clinical trial of amikacin liposome inhalation suspension (ALIS). ALIS was…
The first US patient has been dosed with the drug MIN-102 as part of a clinical trial into its effects in patients with adrenomyeloneuropathy. For more information about this, you…
Top-line data from a Phase 3 study of an experimental method of visualising prostate cancer has been announced. While it met the primary endpoint for specificity, it did not meet…
Azathioprine is a drug used in the treatment of a variety of conditions. Inflammatory bowel disease, arthritis, and vasculitis may all include azathioprine as part of their respective therapies. It…
A recent study published in the journal Cell has investigated the process behind the genetic condition Glut1 deficiency syndrome. Many genetic disorders are thought to be caused by genetic alterations that…
According to a story from Parkinson's Disease Today, a recent review highlights the potential benefits and limitations of telemedicine in treating Parkinson's disease. However, the authors also say that more…
A recent study carried out by scientists from the University of Utah Health has highlighted the role of a protein called Staufen1 in spinocerebellar ataxia type 2 and amyotrophic lateral…
Cancer treatment is a delicate process to say the least. Radiation and chemotherapy, though often effective, are not easy on patients. This is especially true for children. According to a…
According to a story from aawsat.com, a recent analysis suggests that nutrition therapy is an effective tool for slowing the progression of chronic kidney disease and delaying the need for…
Some estimates place the rate of preterm birth as high as 15 million babies each year. This describes a serious global health concern. Many of these babies experience neurological disorders…
According to a story from bioportfolio.com, the biopharmaceutical company Eureka Therapeutics recently released the results of the proof of concept trial for its experimental T-cell therapy ET140202 as a treatment…
According to a story from cnbc.com, a group of volunteers in a clinical study drank a concentrated brew that was filled with bacteria. This may sound unpleasant or even dangerous,…
The United States Food and Drug Administration has granted an Investigational New Drug application for AP101. AP101 is a drug that is being researched as a potential treatment for epidermolysis…
According to a story from Medical Xpress, a team of researchers has discovered a naturally occurring plant compound that exploits a particular weakness found in uveal melanoma, a rare type…
According to a story from BioSpace, the biopharmaceutical company Soleno Therapeutics recently announced that it will be updating the minimum age for participating patients in its Phase III clinical trial…
Linda Ramsey had a son named Kevin. In the beginning everything was okay, and Kevin grew normally for a short time. After a few months, his experienced difficulty swallowing. He…
According to a report by the New York Times, a group of researchers tested the health benefits of bacteria this summer. Specifically, researchers aimed to determine if they were able…
The non-profit organisation CureDuchenne has announced that they have made a $500,000 investment in the company 4D Molecular Therapeutics in order to support the development of gene therapy research. For…
According to a story from EurekAlert!, a collaborative team of researchers from the University of Florida and The Salk Institute are using cryo-electron microscopy in order to more closely examine…
A study of an investigational drug called ZX008 in patients who have refractory Lennox-Gastaut syndrome has produced promising results, according to Zogenix. For more detailed information, you can view…
The speciality pharmaceutical company Advicenne has announced that the US FDA has cleared the Investigational New Drug (IND) application submitted on behalf of ADV7103. ADV7103 is an investigational treatment for…
McMaster University researchers investigating the factors underlying patient relapse in acute myeloid leukaemia believe that they may have found a type of cell that plays an important role. The researchers…
According to a story from BioPortfolio, the drug development company Dicerna Pharmaceuticals recently announced the release of proof of concept data in its Phase I trial testing the company's experimental…
The companies BeiGene Ltd. and SpringWorks Therapeutics have announced that they will collaborate to research the safety and preliminary efficacy of a combination of two drugs: BeiGene’s investigational drug lifirafenib…
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