Possible New Treatment for Facioscapulohumeral Muscular Dystrophy
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Possible New Treatment for Facioscapulohumeral Muscular Dystrophy

A team of researchers from the University of Alberta have created a possible treatment for facioscapulohumeral muscular dystrophy (FSHD). Their work has been published in the Proceedings of the National Academy…

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Simponi Works for Patients with AS, RA, and PsA – Even with Prior TNF Inhibitor Treatment
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Simponi Works for Patients with AS, RA, and PsA – Even with Prior TNF Inhibitor Treatment

  In some cases, people have a medical condition that doesn't respond well to treatments. The journey to finding an effective treatment can be long and difficult. But for patients…

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New Meniere’s Disease Treatment Has FDA Approval to Advance to a Phase III Trial

Sound Pharmaceuticals announced the first-ever Phase III clinical trial protocol for Meniere’s disease to be approved by the FDA. Meniere’s disease (MD) is a neurotologic disorder that involves tinnitus (ringing…

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Positive Results from Trial of Sotatercept, a Treatment for Pulmonary Arterial Hypertension
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Positive Results from Trial of Sotatercept, a Treatment for Pulmonary Arterial Hypertension

Acceleron Pharma has released the results from Phase 2 of their PULSAR trial, which studied sotatercept as a treatment for pulmonary arterial hypertension. Researchers are very excited by the positive…

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FDA Approves CRYSVITA for Tumor-Induced Osteomalacia
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FDA Approves CRYSVITA for Tumor-Induced Osteomalacia

Ultragenyx Pharmaceutical's therapy, CRYSVITA, has recently been approved by the FDA for the treatment of FGF23-related hypophosphatemia in tumor-induced osteomalacia (TIO) associated with phosphaturic mesenchymal tumors. This approval comes after…

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Company Receives Clearance to Conduct Trial for Propionic and Methylmalonic Acidemia
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Company Receives Clearance to Conduct Trial for Propionic and Methylmalonic Acidemia

According to a press release from HemoShear Therapeutics, the company has recently received official clearance from the US Food and Drug Administration (FDA) in regards to its Investigational New Drug…

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