An Experimental Treatment for Primary Hyperoxaluria has Earned Rare Pediatric Disease Designation
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An Experimental Treatment for Primary Hyperoxaluria has Earned Rare Pediatric Disease Designation

According to a story from BioSpace, the biopharmaceutical company Dicerna Therapeutics, Inc. has announced recently that the US Food and Drug Administration (FDA) has granted Rare Pediatric Disease designation to…

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Dr. Eunice Wang Discusses Newly Approved Treatments for Acute Myeloid Leukemia
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Dr. Eunice Wang Discusses Newly Approved Treatments for Acute Myeloid Leukemia

  Earlier this year, The Leukemia & Lymphoma Society hosted a presentation by Dr. Eunice Wang, Clinical Leukemia Service, Professor of Oncology, Roswell Park Comprehensive Cancer Center. Dr. Wang’s presentation…

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New Treatment Approved in Canada for Gastrointestinal Stromal Tumor
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New Treatment Approved in Canada for Gastrointestinal Stromal Tumor

According to a story from Biotech 365, the biopharmaceutical company Deciphera Pharmaceuticals has recently announced that the company's drug ripretinib (marketed as QINLOCK™) has been approved by Health Canada. The…

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Study: Nuplazid Demonstrates its Impact in Parkinson’s Disease Patients
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Study: Nuplazid Demonstrates its Impact in Parkinson’s Disease Patients

  According to a recent article in Parkinson’s News Today, results of an extension study confirm that FDA approved Nuplazid (pimavanserin) reduces the severity of delusions and hallucinations in Parkinson’s disease…

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Protego-PD, for Necrotizing Enterocolitis, Receives Orphan Drug and Rare Pediatric Disease Designations
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Protego-PD, for Necrotizing Enterocolitis, Receives Orphan Drug and Rare Pediatric Disease Designations

  Plakous Therapeutics released a press release to announce that Protego-PD™, their therapy for infants with necrotizing enterocolitis (NEC), received both the Orphan Drug and Rare Pediatric Disease designations from the FDA. There are…

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A New Phase 2 Trial Begins for Experimental Nonalcoholic Steatohepatitis Treatment
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A New Phase 2 Trial Begins for Experimental Nonalcoholic Steatohepatitis Treatment

According to a story from globenewswire.com, the biotechnology company CytoDyn Inc. has recently announced the initiation of a phase 2 clinical trial. This clinical trial will be testing the company's…

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A Study Confirms Significant Benefits from Deep Brain Stimulation for Late-stage Parkinson’s Patients

Parkinson's News Today recently published an article featuring a study in Italy showing the benefits of deep brain stimulation in patients with late-stage Parkinson’s disease. The history of the subthalamic…

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The First Treatment for Adult-Onset Still’s Disease Just Got FDA Approved
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The First Treatment for Adult-Onset Still’s Disease Just Got FDA Approved

According to a story from PR Newswire, the US Food and Drug Administration (FDA) has just approved a treatment for rare adult-onset Still's disease for the first time ever. The…

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Portuguese Authorities Approve Treatment for HATTR Amyloidosis Polyneuropathy
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Portuguese Authorities Approve Treatment for HATTR Amyloidosis Polyneuropathy

According to a story from PR Newswire, Akcea Therapeutics, Inc. recently announced that the Portuguese Medicine Regulatory Authority (INFARMED) has announced its approval of reimbursement for inotersen (marketed as TEGSEDI®)…

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