Dr. Lindsay Wilde, an oncologist at the Hematologic Malignancies Division of Jefferson University, recently contributed to an article in the Oncology Times outlining her research team’s new study and…
Last month, at the American Academy of Dermatology (AAD) Virtual Annual Meeting, Dr. Dedee F. Murrell, MD, explained the efficacy of rilzabrutinib for treating pemphigus. According to MDedge, many…
By Lauren Thayer from In The Cloud Copy Sickle cell disease (SCD) is group of inherited red blood cell disorders. In a typical, healthy red blood cell, the cell is…
INO-3107, a treatment for recurrent respiratory papillomatosis (RRP), has recently received the Orphan Drug Designation from the FDA. This treatment is currently being evaluate in a Phase 1/2 trial by…
According to a story from PR Newswire, the biotechnology company INOVIO has just announced that the company's investigational product candidate INO-3107 has earned Orphan Drug designation from the US Food…
According to GlobeNewswire, BridgeBio Pharmaceuticals and the Ivy Brain Tumor Center have recently began their Phase 0/2 trial of infigratinib. This treatment is meant for those with recurrent glioblastoma that…
As reported in Medical Xpress, researchers are studying how patients using bisphosophonates as part of a treatment regime to avoid fractures associated from osteoporosis are affected by "drug holidays" when…
By Danielle Bradshaw from In The Cloud Copy In a six-month long early rheumatoid arthritis (RA) trial - which was called NORD-STAR - researchers reported at the European League Against…
Just last month, the FDA approved MYCAPSSA for patients with acromegaly who have previously been treated with octreotide or lanreotide. As the first FDA-approved oral somatostatin analog, developer Chiasma…
Last month, according to an article in the Washington Post, the FDA allowed marketing of a video game as potentially beneficial to children who have been diagnosed with attention-deficit hyperactivity…
By Lauren Thayer from In The Cloud Copy Parkinson’s disease is a neurodegenerative disorder that is progressive, resulting in the patient having problems with movement. The symptoms of Parkinson’s disease…
By Lauren Thayer from In The Cloud Copy Systemic sclerosis is a rare autoimmune disease that is characterized by vascular abnormalities and fibrosis of various parts of the body, including…
By Danielle Bradshaw from In The Cloud Copy A research team has found a connection that ties disease-linked alpha-synuclein proteins and their tendency to loosely combine (or to aggregate) and…
A recent article in BioSpace reported that Blueprint Medicines Corp. has submitted a New Drug Application (NDA) to the FDA for the investigational drug pralsetinib with an action date…
According to data from the STOMP trial involving thirty-four patients, a triple regimen has been proven to induce durable responses in pretreated patients with relapsed/refractory multiple myeloma. A recent…
BioMarin has recently submitted a Marketing Authorization Application to the European Medicines Agency for their achondroplasia treatment, vosoritide. As of now, the review of the application will begin in August.…
According to a story from Medscape, the US Food and Drug Administration (FDA) has recently approved a new oral solution as a treatment for symptoms associated with narcolepsy, a rare…
According to a story from Globe Newswire, the biopharmaceutical company Ovid Therapeutics and the University of Connecticut School of Medicine (UConn) have announced a new license agreement and research collaboration…
According to a story from Markets Insider, the biotechnology company NMD Pharma A/S has recently announced that the Dutch ethics committee has approved the company's plan for a combined phase…
According to a story from msn.com, two women who were impacted by the rare disease familial chylomicronemia syndrome (FCS) have lead the charge in changing the procedures used by the…
According to a story from BioSpace, the biopharmaceutical company Bioniz Therapeutics, Inc., has recently announced the release of interim results from its phase 1/2 clinical trial. This trial is investigating…
According to Parkinson's News Today, an intestinal gel comprised of levodopa and carbidopa (LCIG) is able to lower the amount of time that Parkinson's patients spend in off episodes. These…
Orphazyme has recently submitted their New Drug Application to the FDA for their Niemann-Pick disease type C (NPC) treatment, arimoclomol. This application comes after the biopharmaceutical company was already granted…
According to a story from Parkinson's News Today, a recent study describes the development of a new technology called computational mapping algorithms for neural drug delivery (COMMAND), which was designed…
A recent article in Cure Today describes the impact of a new class of injectable radiation therapy on Barbara Davis’ metastatic breast cancer and Dr. Howard Schiff’s metastatic prostate…
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