What do bitcoin and healthcare have in common? Not much until recently. Now an established healthcare provider is launching a system based on patient empowerment. The platform focuses primarily on…
A gene therapy being developed as a treatment for Sanfilippo syndrome has just been awarded Regenerative Medicine Advanced Therapy (RMAT) status in the US, reports GlobalGenes. Sanfilippo syndrome is a…
He was billed as "The 8th Wonder of the World," and this month a new documentary on the legendary WWE wrestler, André the Giant, premiered on cable outlet HBO. According…
A clinical trial that gave children with progeria an experimental drug that was initially intended for cancer patients has produced promising results, reports The Washington Times. The study found that children…
Let's get moving in May! First off, for all you pop culture/Internet meme lovers, it's that time of year... May means we're on the eve of summertime, knee-deep in springtime,…
The inaugural Homocystinuria Network America Conference was held April 21st-22nd in Westford, MA. The families in attendance traveled from all across the US for the event. They all have different…
According to a story from PR Newswire, The Marfan Foundation and Backpack Health are partnering so that the foundation can begin the creation of a patient registry for people affected…
The Australian government will subsidize a new treatment for Hodgkin lymphoma, bringing its price down from $200,000 per course to $39.50 for most people, and $6.40 for concession patients, reports…
To read part one of this story, click here. Morgan is a young woman in her early twenties who has been living with symptoms of extreme pain on a daily…
According to a story from biotechprism.com, ten-year-old boy Jed Kagan of South Africa was crippled by debilitating pain when he first appeared at the Red Cross War Memorial Children's Hospital in…
According to a story from People, a little girl from Ohio has faced major health challenges since her birth. Grace Rosian, who was born with Down syndrome, was diagnosed with…
A new study reported on by Hematology Times has found that being taught art can significantly decrease pain and anxiety, and promote a positive mood in patients with hematologic malignancies.…
The US Food and Drug Administration (FDA) has just awarded Breakthrough Therapy Designation to a drug (OMS721) being developed to treat thrombotic microangiopathy that has developed as a result of haematopoietic stem…
Terrence Merrill shares the challenging emotional realities of raising a child with Sanfilippo syndrome. You can read more background about the Merrill's battle against this rare disease in our article here.…
At the age of 28, Suzy remembers medical students feeling her puffy hands and feet. Her feet were so expanded she had to wear wide shoe sizes. Her fingers were…
When I was diagnosed with Parkinson's Disease (PD) in 2000, I first thought of my three children and how my diagnosis would impact them. How would I tell them? Would I…
12-year-old Cezy Fosca lives in Kilkenny City and suffers from Morquio syndrome. Her family waited for months on approval for her treatment, after she lost access to it. Finally, the…
When people are faced with cancer, their main concerns are understandably treatment and survival. However, many are shocked to discover that when they survive cancer, another sinister blow on their…
A gene therapy called ABO-202 that is being developed to treat Batten disease has just been granted Orphan Drug Designation by the European Medicines Agency (EMA), reports BioPortfolio. This follows…
The phrase “it takes a village” gets tossed around a lot. But in Codicote, that’s what’s happening. Fundraising events and challenges are being held left and right. All of them…
The US Food and Drug Administration (FDA) has just approved the drug Vonvendi for use in adult patients with von Willebrand disease who are undergoing surgery. This is an extension…
Imagine not being able to eat because you cannot swallow your food. Add to that intolerable pain and the inability to sleep at night. These are some of the symptoms…
In order to honor Cystinosis Awareness Day, which takes place on May 7th each year, a man will attempt to walk 57 miles in a single day in order to…
What if paranoia could be genetically located? A study of Prader-Willi syndrome gave scientists a chance to find out. Keep reading to learn more about this development, or follow the…
In St. Louis, Missouri, a local start-up is using novel research to make a big difference. The start-up, known as Unleash seeks to develop a unique cure for cancer. Keep…
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